Disease

Psychiatry·MeSH: Disease

Prevalence

0.7 / 100K

Incidence

0.1 / 100K/yr

1401 drugs in development·452 companies·2 clinical trials

Drug Pipeline by Phase

Approved(223)
DrugCompany
ABRAXANEImmunityBio, Inc. (IBRX)
abriladaPFIZER INC (PFE)
aBSI (Automated Bone Scan Index)Lantheus Holdings, Inc. (LNTH)
acam2000Emergent BioSolutions Inc. (EBS)
adcircaELI LILLY & Co (LLY)
afinitorNovartis AG (NVS)
alendronateMylan II B.V. (MYL)
Alginic Sodium Diester InjectionCHINA PHARMA HOLDINGS, INC. (CPHI)
Alimta®ELI LILLY & Co (LLY)
Alinity® familyABBOTT LABORATORIES (ABT)
ambrisentanMylan II B.V. (MYL)
amlodipineOXFORD IMMUNOTEC GLOBAL PLC (OXFD)
amoxicillinMiromatrix Medical Inc. (MIRO)
ANORO ELLIPTAInnoviva, Inc. (INVA)
APOKYNSUPERNUS PHARMACEUTICALS, INC. (SUPN)
ASCENIVADMA BIOLOGICS, INC. (ADMA)
austedo xrTeva Pharmaceutical Industries Limited (TEVA)
avatrombopagGYRE THERAPEUTICS, INC. (GYRE)
avsolaAMGEN INC (AMGN)
azilectTeva Pharmaceutical Industries Limited (TEVA)
azithromycinSUNSET ISLAND GROUP (SUN)
baclofenANI PHARMACEUTICALS INC (ANIP)
baclofenImpax Laboratories, LLC (IPXL)
bexaroteneAmneal Pharmaceuticals, Inc. (AMRX)
BinaxNOW®ABBOTT LABORATORIES (ABT)
BinaxNOW® / Panbio® rapid testing platformsABBOTT LABORATORIES (ABT)
breynaMylan II B.V. (MYL)
BRIUMVITG THERAPEUTICS, INC. (TGTX)
Bumetanide for InjectionCHINA PHARMA HOLDINGS, INC. (CPHI)
c6 lyme elisa kitOXFORD IMMUNOTEC GLOBAL PLC (OXFD)
calcitonin-salmonAmneal Pharmaceuticals, Inc. (AMRX)
CapvaxiveMerck & Co., Inc. (MRK)
CASGEVYCRISPR Therapeutics AG (CRSP)
CASGEVYEditas Medicine, Inc. (EDIT)
CASGEVY (exagamglogene autotemcel)Editas Medicine, Inc. (EDIT)
cerebroprotein hydroloysateCHINA PHARMA HOLDINGS, INC. (CPHI)
Cerebroprotein Hydroloysate InjectionCHINA PHARMA HOLDINGS, INC. (CPHI)
CerebroproteinHydroloysate InjectionCHINA PHARMA HOLDINGS, INC. (CPHI)
chenodiolOptec International, Inc. (GM)
cibinqoPFIZER INC (PFE)
cinacalcetDR REDDYS LABORATORIES LTD (RDY)
clarithromycinSUNSET ISLAND GROUP (SUN)
clonoSEQAdaptive Biotechnologies Corp (ADPT)
clopidogrel biTeva Pharmaceutical Industries Limited (TEVA)
contivaGYRE THERAPEUTICS, INC. (GYRE)
crexontImpax Laboratories, LLC (IPXL)
cutaquigKORU Medical Systems Inc. Common Stock (DE) (KRMD)
cuvitruKORU Medical Systems Inc. Common Stock (DE) (KRMD)
cyclophosphamideNEXUS BIOPHARMA INC (NEXS)
danyelzaY-mAbs Therapeutics, Inc. (YMAB)
dexlansoprazoleMylan II B.V. (MYL)
dimethylMylan II B.V. (MYL)
donepezilDR REDDYS LABORATORIES LTD (RDY)
dopteletAKORN INC (AKRX)
doxercalciferolAmneal Pharmaceuticals, Inc. (AMRX)
elelysoProtalix BioTherapeutics, Inc. (PLX)
elfabrioProtalix BioTherapeutics, Inc. (PLX)
eligen b12 rxEMISPHERE TECHNOLOGIES INC (EMIS)
endariEmmaus Life Sciences, Inc. (EMMA)
enflonsiaMerck & Co., Inc. (MRK)
Epidiolex / EpidyolexJazz Pharmaceuticals plc (JAZZ)
epoprostenolMylan II B.V. (MYL)
eribulinDR REDDYS LABORATORIES LTD (RDY)
ErveboMerck & Co., Inc. (MRK)
erythromycin lactobionateNEXUS BIOPHARMA INC (NEXS)
etorelGYRE THERAPEUTICS, INC. (GYRE)
EVRENZO (爱瑞卓®) / roxadustatKYNTRA BIO INC. (KYNB)
famotidineMersana Therapeutics, Inc. (MRSN)
famotidineSeagen Inc. (SGEN)
famotidineENGENE HOLDINGS INC. (ENGN)
famotidineAvita Medical Inc. (RCEL)
famotidineMiromatrix Medical Inc. (MIRO)
famotidineSUNSET ISLAND GROUP (SUN)
FILSPARI®Travere Therapeutics, Inc. (TVTX)
fingolimodDR REDDYS LABORATORIES LTD (RDY)
fingolimodMylan II B.V. (MYL)
fingolimodSUNSET ISLAND GROUP (SUN)
fingolimodICON plc (ICLR)
fingolimodTeva Pharmaceutical Industries Limited (TEVA)
fingolimodGT Biopharma, Inc. (GTBP)
fingolimodAptinyx Inc. (APTX)
fingolimodaTYR PHARMA INC (ATYR)
fosinoprilTeva Pharmaceutical Industries Limited (TEVA)
GalafoldAMICUS THERAPEUTICS, INC. (FOLD)
Galafold®AMICUS THERAPEUTICS, INC. (FOLD)
gammagard liquidKORU Medical Systems Inc. Common Stock (DE) (KRMD)
Ge Hong Beriberi WaterChina Health Industries Holdings, Inc. (CHHE)
gocovriAdamas Pharmaceuticals Inc (ADMS)
GOCOVRISUPERNUS PHARMACEUTICALS, INC. (SUPN)
Hadlima (SB5)Organon & Co. (OGN)
Hepatocyte Growth-promoting Factor for InjectionCHINA PHARMA HOLDINGS, INC. (CPHI)
hizentraKORU Medical Systems Inc. Common Stock (DE) (KRMD)
ibrancePFIZER INC (PFE)
ImbruvicaRoyalty Pharma plc (RPRX)
imuldosaAcorda Therapeutics, Inc. (ACOR)
inbrijaAcorda Therapeutics, Inc. (ACOR)
indocinZyla Life Sciences (ZCOR)
INDOCIN (suppositories and oral suspension)Assertio Holdings, Inc. (ASRT)
INDOCIN SuppositoriesAssertio Holdings, Inc. (ASRT)
indomethacinAmneal Pharmaceuticals, Inc. (AMRX)
indomethacinMylan II B.V. (MYL)
inFoods® (IBS)BIOMERICA INC (BMRA)
InluriyoELI LILLY & Co (LLY)
inpefaLEXICON PHARMACEUTICALS, INC. (LXRX)
IPX203Amneal Pharmaceuticals, Inc. (AMRX)
IPX203 (CREXONT)Amneal Pharmaceuticals, Inc. (AMRX)
isosorbide monoEXELIXIS, INC. (EXEL)
JardianceELI LILLY & Co (LLY)
Jardiance®ELI LILLY & Co (LLY)
KisunlaELI LILLY & Co (LLY)
Klacid™ (Claribid™, Klaricid™)ABBOTT LABORATORIES (ABT)
korsuva / kapruviaTvardi Therapeutics, Inc. (TVRD)
labelingACURA PHARMACEUTICALS, INC (ACUR)
LEQEMBIBIOGEN INC. (BIIB)
letairisGILEAD SCIENCES, INC. (GILD)
lodonalBiostax Corp. (BTAX)
LYFGENIAbluebird bio, Inc. (BLUE)
macitentanMylan II B.V. (MYL)
MARGENZAMACROGENICS INC (MGNX)
MIEBOBausch Health Companies Inc. (BHC)
miglustatANI PHARMACEUTICALS INC (ANIP)
miplyffaZEVRA THERAPEUTICS, INC. (ZVRA)
miplyffaXOMA Royalty Corporation (XOMA)
modeysoJazz Pharmaceuticals plc (JAZZ)
mRESVIAModerna, Inc. (MRNA)
nelarabineAmneal Pharmaceuticals, Inc. (AMRX)
nelarabineNEXUS BIOPHARMA INC (NEXS)
neuraceqLantheus Holdings, Inc. (LNTH)
nexobridMediWound Ltd. (MDWD)
NiktimvoSyndax Pharmaceuticals Inc (SNDX)
nintedanibX4 Pharmaceuticals, Inc (XFOR)
nintedanibAptinyx Inc. (APTX)
nintedanibEXELIXIS, INC. (EXEL)
nintedanibGYRE THERAPEUTICS, INC. (GYRE)
nintedanibDR REDDYS LABORATORIES LTD (RDY)
nintedanibNYMOX PHARMACEUTICAL CORP (NYMXF)
nitroglycerinDR REDDYS LABORATORIES LTD (RDY)
nu.q netsVOLITIONRX LTD (VNRX)
Ocular Immunoglobulin E (IgE)AXIM BIOTECHNOLOGIES, INC. (AXIM)
Ocular Lactoferrin (Lf)AXIM BIOTECHNOLOGIES, INC. (AXIM)
OhtuvayreVerona Pharma plc (VRNA)
OmvohELI LILLY & Co (LLY)
ONAPGOSUPERNUS PHARMACEUTICALS, INC. (SUPN)
ONGENTYSAmneal Pharmaceuticals, Inc. (AMRX)
osmolex erAdamas Pharmaceuticals Inc (ADMS)
oxbrytaGlobal Blood Therapeutics, Inc. (GBT)
ozempicNovo Nordisk A/S (NVO)
paclitaxelMylan II B.V. (MYL)
pantoprazoleSUNSET ISLAND GROUP (SUN)
pantoprazoleEXELIXIS, INC. (EXEL)
paxlovidPFIZER INC (PFE)
periopredictINTERLEUKIN GENETICS INC (ILIU)
plegridyBIOGEN INC. (BIIB)
pombilitiAMICUS THERAPEUTICS, INC. (FOLD)
Pombiliti + OpfoldaAMICUS THERAPEUTICS, INC. (FOLD)
Pombiliti™ + Opfolda™AMICUS THERAPEUTICS, INC. (FOLD)
ponvoryVanda Pharmaceuticals Inc. (VNDA)
pravastatinAptinyx Inc. (APTX)
prednisoneDR REDDYS LABORATORIES LTD (RDY)
PrevymisMerck & Co., Inc. (MRK)
propafenoneMylan II B.V. (MYL)
propylgallateCHINA PHARMA HOLDINGS, INC. (CPHI)
Propylgallate for InjectionCHINA PHARMA HOLDINGS, INC. (CPHI)
PYRUKYND®AGIOS PHARMACEUTICALS, INC. (AGIO)
quest ad-detectQuest Diagnostics Incorporated (DGX)
rayaldeeOPKO HEALTH, INC. (OPK)
rayaldeeREPLIGEN CORP (RGEN)
RELVAR/BREO ELLIPTAInnoviva, Inc. (INVA)
Renflexis (SB2)Organon & Co. (OGN)
ropiniroleELITE PHARMACEUTICALS INC /NV/ (ELTP)
ropiniroleDR REDDYS LABORATORIES LTD (RDY)
RYTARYAmneal Pharmaceuticals, Inc. (AMRX)
sevelamer carbonateImpax Laboratories, LLC (IPXL)
sevelamer carbonateDR REDDYS LABORATORIES LTD (RDY)
siberian ginseng seriesFuss Brands Corp. (FBDS)
tascenso odtBICYCLE THERAPEUTICS PLC (BCYC)
tembexaEmergent BioSolutions Inc. (EBS)
tepezzaHorizon Therapeutics Public Ltd Co (HZNP)
teriflunomideMersana Therapeutics, Inc. (MRSN)
teriflunomideAptinyx Inc. (APTX)
tetrabenazineDR REDDYS LABORATORIES LTD (RDY)
theophyllineAmneal Pharmaceuticals, Inc. (AMRX)
tobramycinAmneal Pharmaceuticals, Inc. (AMRX)
tofidenceBIOGEN INC. (BIIB)
TrelegyRoyalty Pharma plc (RPRX)
treprostinilTeva Pharmaceutical Industries Limited (TEVA)
triamcinolone acetonideTeva Pharmaceutical Industries Limited (TEVA)
trientineAmneal Pharmaceuticals, Inc. (AMRX)
trodelvyImmunome Inc. (IMNM)
TrulicityELI LILLY & Co (LLY)
Trulicity®ELI LILLY & Co (LLY)
tykerbNovartis AG (NVS)
tyrvayaViatris Inc (VTRS)
Tyvaso (nebulized)UNITED THERAPEUTICS Corp (UTHR)
tyvaso dpiMANNKIND CORP (MNKD)
Tyvaso DPIUNITED THERAPEUTICS Corp (UTHR)
ursodiolOptec International, Inc. (GM)
VafseoAkebia Therapeutics, Inc. (AKBA)
valbenazineGreenwich LifeSciences, Inc. (GLSI)
VASCEPA (VAZKEPA in EU)AMARIN CORP PLCUK (AMRN)
VASCEPA (VAZKEPA)AMARIN CORP PLCUK (AMRN)
vazalorePLX PHARMA INC. (DPRX)
vispa-cel based on fda interactions to dateCaribou Biosciences, Inc. (CRBU)
vizamylGE HealthCare Technologies Inc. (GEHC)
VOQUEZNAPhathom Pharmaceuticals, Inc. (PHAT)
vprivSHIRE PLC (SHPGF)
VUMERITYAlkermes plc. (ALKS)
vyalevAbbVie Inc. (ABBV)
WeliregMerck & Co., Inc. (MRK)
wezlanaAMGEN INC (AMGN)
wixela inhubMylan II B.V. (MYL)
XADAGOSUPERNUS PHARMACEUTICALS, INC. (SUPN)
xeljanz xrPFIZER INC (PFE)
xembifyKORU Medical Systems Inc. Common Stock (DE) (KRMD)
XIIDRABausch Health Companies Inc. (BHC)
XPHOZAHARDELYX, INC. (ARDX)
yesintekBone Biologics Corp (BBLG)
yupelriMylan II B.V. (MYL)
yupelriTheravance Biopharma, Inc. (TBPH)
YUTREPIALiquidia Corp (LQDA)
Zenocutuzumab (Zeno) / BIZENGRI® (zenocutuzumab-zbco)Merus N.V. (MRUS)
ZUNVEYL (formerly ALPHA-1062)Alpha Cognition Inc. (ACOG)
zycuboFortress Biotech Inc. (FBIO)
Phase 3(291)
DrugCompany
[14c]azd0780ASTRAZENECA PLC (AZN)
[14c]azd0780 solution for infusionASTRAZENECA PLC (AZN)
[18f]pi-2620Insight Molecular Diagnostics Inc. (IMDX)
0.003% ar-15512AERIE PHARMACEUTICALS INC (AERI)
100 mg resmetiromMADRIGAL PHARMACEUTICALS, INC. (MDGL)
20vpcvSanofi (SNY)
20vpcvSanofi (SNY)
AbataceptENANTA PHARMACEUTICALS INC (ENTA)
AbataceptCrinetics Pharmaceuticals, Inc. (CRNX)
ABBV-444AbbVie Inc. (ABBV)
abbv-951AbbVie Inc. (ABBV)
acellular tissue engineered vesselHumacyte Inc. (HUMA)
ACP-204ACADIA PHARMACEUTICALS INC (ACAD)
Adjuvant chemotherapyValneva SE (VALN)
advateTakeda Pharmaceutical Company Limited American Depositary Shares (each representing 1/2 of a share of Common Stock) (TAK)
advateTAKEDA PHARMACEUTICAL CO LTD (TKPHF)
akcea-apo-lrxAKCEA THERAPEUTICS, INC. (AKCA)
AL050Alector, Inc. (ALEC)
alemtuzumabGH Research PLC (GHRS)
Alglucosidase AlfaAMICUS THERAPEUTICS, INC. (FOLD)
Alglucosidase alfa or Avalglucosidase alfaAMICUS THERAPEUTICS, INC. (FOLD)
alvelestatMereo BioPharma Group plc (MREO)
alxn1840ALEXION PHARMACEUTICALS, INC. (ALXN)
alxn1840Monopar Therapeutics (MNPR)
ANAVEX®2-73ANAVEX LIFE SCIENCES CORP. (AVXL)
anti-thymocyte globulinFilana Therapeutics Inc. (FLNA)
antihemophilic factorSHIRE PLC (SHPGF)
ap-cd/ldINTEC PHARMA LTD. (NTEC)
ar-15512AERIE PHARMACEUTICALS INC (AERI)
ar-15512 vehicleAERIE PHARMACEUTICALS INC (AERI)
AT2221AMICUS THERAPEUTICS, INC. (FOLD)
ATB200AMICUS THERAPEUTICS, INC. (FOLD)
atrasentanCHINOOK THERAPEUTICS, INC. (KDNY)
AuryxiaAkebia Therapeutics, Inc. (AKBA)
avalglucosidase alfaSanofi (SNYNF)
AZ-3102Crinetics Pharmaceuticals, Inc. (CRNX)
AZD0780ASTRAZENECA PLC (AZN)
AZD4248ASTRAZENECA PLC (AZN)
AZD6793ASTRAZENECA PLC (AZN)
AZD7798ASTRAZENECA PLC (AZN)
bardoxoloneREATA PHARMACEUTICALS INC (RETA)
Base-edited hematopoietic stem and progenitor cellsENANTA PHARMACEUTICALS INC (ENTA)
BatoclimabImmunovant, Inc. (IMVT)
bcg tokyo-172 strain vaccineGH Research PLC (GHRS)
belumosudilSanofi (SNY)
BelumosudilSanofi (SNY)
BelzutifanMerck & Co., Inc. (MRK)
best available therapyIncyte Corp. (INCY)
bexobrutidegNurix Therapeutics, Inc. (NRIX)
bezisterim (NE3107)BIOVIE INC. (BIVI)
bgfASTRAZENECA PLC (AZN)
bgf mdi 320/14.4/9.6 μgASTRAZENECA PLC (AZN)
bhv-1300Biohaven Ltd. (BHVN)
BIIB080BIOGEN INC. (BIIB)
BIIB122BIOGEN INC. (BIIB)
bivv009Bioverativ Inc. (BIVV)
bms-986515Juno Therapeutics, Inc. (JUNO)
brazikumab induction doseASTRAZENECA PLC (AZN)
brazikumab maintenance doseASTRAZENECA PLC (AZN)
buntanetapAnnovis Bio, Inc. (ANVS)
Bypassing AgentsENANTA PHARMACEUTICALS INC (ENTA)
CabozantinibMerck & Co., Inc. (MRK)
Cipaglucosidase AlfaAMICUS THERAPEUTICS, INC. (FOLD)
clofazimine inhalationMANNKIND CORP (MNKD)
corplex donepezilCorium International, Inc. (CORI)
crizanlizumabNovartis AG (NVS)
CrizanlizumabNovartis AG (NVS)
crofelemer powder forJaguar Health, Inc. (JAGX)
ctap101OPKO HEALTH, INC. (OPK)
ctx001VERTEX PHARMACEUTICALS INC / MA (VRTX)
darvadstrocelTAKEDA PHARMACEUTICAL CO LTD (TKPHF)
darvadstrocelTakeda Pharmaceutical Company Limited American Depositary Shares (each representing 1/2 of a share of Common Stock) (TAK)
dc1 vaccineGH Research PLC (GHRS)
disc-3405Disc Medicine, Inc. (IRON)
DonanemabELI LILLY & Co (LLY)
DonepezilCrinetics Pharmaceuticals, Inc. (CRNX)
drugNOVARTIS AG (NVSEF)
drugNovartis AG (NVS)
DTX401Ultragenyx Pharmaceutical Inc. (RARE)
duvakitugSanofi (SNYNF)
duvakitugSanofi (SNY)
DuvoglustatAMICUS THERAPEUTICS, INC. (FOLD)
elegrobartViridian Therapeutics, Inc.\DE (VRDN)
eliglustat gz385660Sanofi (SNY)
EmpagliflozinValneva SE (VALN)
Ensifentrine (nebulized) - asthmaVerona Pharma plc (VRNA)
Ensifentrine (nebulized) - bronchiectasisVerona Pharma plc (VRNA)
Ensifentrine (nebulized) - cystic fibrosisVerona Pharma plc (VRNA)
Ensifentrine / glycopyrrolate fixed-dose combinationVerona Pharma plc (VRNA)
Ensifentrine 1.5 mgVerona Pharma plc (VRNA)
Ensifentrine 3 mgVerona Pharma plc (VRNA)
ERTAMICUS THERAPEUTICS, INC. (FOLD)
erythropoiesis stimulating agentGH Research PLC (GHRS)
Erythropoiesis-Stimulating AgentAkebia Therapeutics, Inc. (AKBA)
etavopivatNovo Nordisk A/S (NVO)
etavopivat aNovo Nordisk A/S (NVO)
etavopivat bNovo Nordisk A/S (NVO)
etavopivat cNovo Nordisk A/S (NVO)
exa-celVERTEX PHARMACEUTICALS INC / MA (VRTX)
expec9vGH Research PLC (GHRS)
extracorporeal photopheresisIncyte Corp. (INCY)
Factor IXENANTA PHARMACEUTICALS INC (ENTA)
Factor VIII ConcentratesENANTA PHARMACEUTICALS INC (ENTA)
FazirsiranARROWHEAD PHARMACEUTICALS, INC. (ARWR)
ferricKERYX BIOPHARMACEUTICALS INC (KERYX)
ferric citrateAkebia Therapeutics, Inc. (AKBA)
ferumoxytolAMAG PHARMACEUTICALS, INC. (AMAG)
fexofenadineSanofi (SNY)
FexofenadineSanofi (SNY)
generxGene Biotherapeutics, Inc. (CRXM)
gff mdi 14.4/9.6 μgASTRAZENECA PLC (AZN)
govorestatApplied Therapeutics, Inc. (APLT)
guselkumabGH Research PLC (GHRS)
Haematopoietic growth factorENANTA PHARMACEUTICALS INC (ENTA)
hec585 dose aSUNSHINE BIOPHARMA INC. (SBFM)
hec585 dose bSUNSHINE BIOPHARMA INC. (SBFM)
hexyon vaccineSanofi (SNY)
horse anti-thymocyte globulinFilana Therapeutics Inc. (FLNA)
icotrokinraGH Research PLC (GHRS)
imatinibIncyte Corp. (INCY)
immune globulinTAKEDA PHARMACEUTICAL CO LTD (TKPHF)
imu-381IMMUNIC, INC. (IMUX)
imu-856IMMUNIC, INC. (IMUX)
inclacumabGlobal Blood Therapeutics, Inc. (GBT)
inclisiran sodium 300 mg inNovartis AG (NVS)
infliximabIncyte Corp. (INCY)
itepekimabSanofi (SNY)
ItepekimabSanofi (SNY)
itepekimab sar440340Sanofi (SNY)
ITI-1284-ODT-SLIntra-Cellular Therapies, Inc. (ITCI)
itolizumabEquillium, Inc. (EQ)
IV TulisokibartMerck & Co., Inc. (MRK)
jnj-78934804GH Research PLC (GHRS)
KarX-ECBRISTOL MYERS SQUIBB CO (BMY)
karxtKaruna Therapeutics, Inc. (KRTX)
L606Liquidia Corp (LQDA)
latozinemabAlector, Inc. (ALEC)
LecanemabELI LILLY & Co (LLY)
LecanemabBIOGEN INC. (BIIB)
Lecanemab IVBIOGEN INC. (BIIB)
Lecanemab SCBIOGEN INC. (BIIB)
Lepodisiran SodiumELI LILLY & Co (LLY)
Levodopa carbidopa intestinal gelAbbVie Inc. (ABBV)
Levodopa-carbidopa intestinal gelAbbVie Inc. (ABBV)
lonvoguran ziclumeranIntellia Therapeutics, Inc. (NTLA)
m-m-rvaxpro vaccineSanofi (SNY)
maralixibatMirum Pharmaceuticals, Inc. (MIRM)
mechanistic target of rapamycin inhibitorsIncyte Corp. (INCY)
menac conjugate vaccineSanofi (SNY)
menacyw135 polysaccharide vaccineSanofi (SNY)
MesnaFilana Therapeutics Inc. (FLNA)
mezagitamabTAKEDA PHARMACEUTICAL CO LTD (TKPHF)
mezagitamabTakeda Pharmaceutical Company Limited American Depositary Shares (each representing 1/2 of a share of Common Stock) (TAK)
MezagitamabCrinetics Pharmaceuticals, Inc. (CRNX)
migalastatSanofi (SNY)
migalastatSanofi (SNYNF)
migalastatAMICUS THERAPEUTICS, INC. (FOLD)
migalastat HClAMICUS THERAPEUTICS, INC. (FOLD)
MiglustatAMICUS THERAPEUTICS, INC. (FOLD)
Mirasol-treated Fresh Whole BloodUNITED THERAPEUTICS Corp (UTHR)
MirikizumabELI LILLY & Co (LLY)
MirikizumabENANTA PHARMACEUTICALS INC (ENTA)
MK-2060Merck & Co., Inc. (MRK)
MolnupiravirMerck & Co., Inc. (MRK)
mycophenolate mofetilIncyte Corp. (INCY)
NerandomilastValneva SE (VALN)
nexiguran ziclumeranIntellia Therapeutics, Inc. (NTLA)
ngn-101Neurogene Inc. (NGNE)
nio752NOVARTIS AG (NVSEF)
nmra-511Neumora Therapeutics, Inc. (NMRA)
obexelimabZenas BioPharma, Inc. (ZBIO)
ObexelimabXencor Inc (XNCR)
OlpasiranARROWHEAD PHARMACEUTICALS, INC. (ARWR)
OmalizumabCidara Therapeutics, Inc. (CDTX)
Other Biologic TherapiesENANTA PHARMACEUTICALS INC (ENTA)
otl-104Orchard Therapeutics plc (ORTX)
ozanimodCELGENE CORP /DE/ (CELG)
pacritinibGH Research PLC (GHRS)
pcv21Sanofi (SNY)
pcv21Sanofi (SNY)
Pegozafermin89bio, Inc. (ETNB)
pelacarsenNovartis AG (NVS)
pelacarsenNovartis AG (NVS)
pentostatinIncyte Corp. (INCY)
Peripheral blood stem cellsFilana Therapeutics Inc. (FLNA)
pg4PFIZER INC (PFE)
pl9643PALATIN TECHNOLOGIES INC (PTN)
plx-300Polaryx Therapeutics Inc. (PLYX)
plx-padPluri Inc. (PLUR)
posoleucelKalaris Therapeutics, Inc. (KLRS)
PrasinezumabPROTHENA CORP PUBLIC LTD CO (PRTA)
prochymalMesoblast Limited (MESO)
prochymal adult human mesenchymal stem cellsMesoblast Limited (MESO)
prochymal adult human mesenchymal stem cellsMESOBLAST LTD (MEOBF)
rabbit anti-thymocyte globulinFilana Therapeutics Inc. (FLNA)
ravulizumabHepion Pharmaceuticals, Inc. (CTRVP)
REFRESH OPTIVE UDAbbVie Inc. (ABBV)
remestemcel-lMesoblast Limited (MESO)
remestemcel-l-rkndMesoblast Limited (MESO)
RemternetugELI LILLY & Co (LLY)
ResmetiromMADRIGAL PHARMACEUTICALS, INC. (MDGL)
rexlemestrocel-l + ha mixtureMesoblast Limited (MESO)
rfviiiSHIRE PLC (SHPGF)
RilzabrutinibSanofi (SNY)
rilzabrutinib sar444671Sanofi (SNY)
risankizumabGH Research PLC (GHRS)
RisankizumabAbbVie Inc. (ABBV)
risvodetinibInhibikase Therapeutics, Inc. (IKT)
Rivastigmine Transdermal SystemUNITED THERAPEUTICS Corp (UTHR)
rvwfSHIRE PLC (SHPGF)
sacituzumab govitecanPhoenix Life Sciences International Limited. (PLSI)
sars-cov-2 adjuvanted recombinant protein vaccineSanofi (SNY)
sb-01GT Biopharma, Inc. (GTBP)
SC TulisokibartMerck & Co., Inc. (MRK)
semagludtideNovo Nordisk A/S (NVO)
sham needleGT Biopharma, Inc. (GTBP)
simufilamFilana Therapeutics Inc. (FLNA)
SimufilamFilana Therapeutics Inc. (FLNA)
SirolimusFilana Therapeutics Inc. (FLNA)
solanezumabPDL BIOPHARMA, INC. (PDLI)
SolanezumabELI LILLY & Co (LLY)
Standard Fresh Whole BloodUNITED THERAPEUTICS Corp (UTHR)
Standard Medical TherapyMerus N.V. (MRUS)
stat-201Statera Biopharma, Inc. (CBLI)
sutimlimabSanofi (SNY)
Tab-cel (Ebvallo)Atara Biotherapeutics, Inc. (ATRA)
tabelecleucelAtara Biotherapeutics, Inc. (ATRA)
tacrolimusIncyte Corp. (INCY)
tak-062Takeda Pharmaceutical Company Limited American Depositary Shares (each representing 1/2 of a share of Common Stock) (TAK)
tak-101Takeda Pharmaceutical Company Limited American Depositary Shares (each representing 1/2 of a share of Common Stock) (TAK)
tak-279Takeda Pharmaceutical Company Limited American Depositary Shares (each representing 1/2 of a share of Common Stock) (TAK)
tak-577TAKEDA PHARMACEUTICAL CO LTD (TKPHF)
tak-577Takeda Pharmaceutical Company Limited American Depositary Shares (each representing 1/2 of a share of Common Stock) (TAK)
tak-771TAKEDA PHARMACEUTICAL CO LTD (TKPHF)
tak-771Takeda Pharmaceutical Company Limited American Depositary Shares (each representing 1/2 of a share of Common Stock) (TAK)
tak-881TAKEDA PHARMACEUTICAL CO LTD (TKPHF)
tak-881Takeda Pharmaceutical Company Limited American Depositary Shares (each representing 1/2 of a share of Common Stock) (TAK)
tak-881Takeda Pharmaceutical Company Limited American Depositary Shares (each representing 1/2 of a share of Common Stock) (TAK)
tavapadonCerevel Therapeutics Holdings, Inc. (CERE)
telitaciceptVor Biopharma Inc. (VOR)
TelmisartanUNITED THERAPEUTICS Corp (UTHR)
TemsirolimusFilana Therapeutics Inc. (FLNA)
TerazosinUNITED THERAPEUTICS Corp (UTHR)
tetravalent inactivated enterovirus vaccineSINOVAC BIOTECH LTD (SVA)
tev-48574Teva Pharmaceutical Industries Limited (TEVA)
tev-53408Teva Pharmaceutical Industries Limited (TEVA)
TezepelumabASTRAZENECA PLC (AZN)
TocilizumabCrinetics Pharmaceuticals, Inc. (CRNX)
TozorakimabASTRAZENECA PLC (AZN)
tozorakimab dose regimen 1ASTRAZENECA PLC (AZN)
tozorakimab dose regimen 2ASTRAZENECA PLC (AZN)
tqj230Novartis AG (NVS)
tqj230Novartis AG (NVS)
trappsol cycloRafael Holdings, Inc. (RFL)
trivalent recombinant influenza vaccineSanofi (SNY)
TrontinemabValneva SE (VALN)
ustekinumabAbbVie Inc. (ABBV)
UstekinumabCrinetics Pharmaceuticals, Inc. (CRNX)
UstekinumabENANTA PHARMACEUTICALS INC (ENTA)
VadadustatAkebia Therapeutics, Inc. (AKBA)
varivax vaccineSanofi (SNY)
VatiquinonePTC THERAPEUTICS, INC. (PTCT)
vaxneuvance vaccineSanofi (SNY)
VAY736Novartis AG (NVS)
vedolizumabTakeda Pharmaceutical Company Limited American Depositary Shares (each representing 1/2 of a share of Common Stock) (TAK)
vedolizumab ivTAKEDA PHARMACEUTICAL CO LTD (TKPHF)
velaglucerase alfaTAKEDA PHARMACEUTICAL CO LTD (TKPHF)
veligrotugViridian Therapeutics, Inc.\DE (VRDN)
venglustatSanofi (SNY)
venglustat gz402671Sanofi (SNY)
veverimerTricida, Inc. (TCDA)
virtue sabOrchestra BioMed Holdings Inc. (OBIO)
von Willebrand Factor ConcentratesENANTA PHARMACEUTICALS INC (ENTA)
vonicog alfaSHIRE PLC (SHPGF)
vonvendiTAKEDA PHARMACEUTICAL CO LTD (TKPHF)
vonvendiTakeda Pharmaceutical Company Limited American Depositary Shares (each representing 1/2 of a share of Common Stock) (TAK)
votoplamNovartis AG (NVS)
votoplamNOVARTIS AG (NVSEF)
VRDN-001Viridian Therapeutics, Inc.\DE (VRDN)
VRDN-003Viridian Therapeutics, Inc.\DE (VRDN)
VRDN-006Viridian Therapeutics, Inc.\DE (VRDN)
VRDN-008Viridian Therapeutics, Inc.\DE (VRDN)
xtr004SPRING PHARMACEUTICAL GROUP, INC. (CYIG)
yellow fever vaccineSanofi (SNY)
ZerlasiranSilence Therapeutics Plc (SLN)
zigakibartNovartis AG (NVS)
zigakibartNovartis AG (NVS)
zilganersenIONIS PHARMACEUTICALS INC (IONS)
ziltivekimabNovo Nordisk A/S (NVO)
zimuraIVERIC bio, Inc. (ISEE)
zl-1109Zai Lab Ltd (ZLAB)
Phase 2(261)
DrugCompany
0.9%GH Research PLC (GHRS)
0.9%GH Research PLC (GHRS)
2hpβcdZyVersa Therapeutics, Inc. (ZVSA)
4D-125 IVT InjectionReplimune Group, Inc. (REPL)
abataceptGH Research PLC (GHRS)
AbiprubartKiniksa Pharmaceuticals International, plc (KNSA)
AcetaminophenENANTA PHARMACEUTICALS INC (ENTA)
Active drugACADIA PHARMACEUTICALS INC (ACAD)
ADX-631Aldeyra Therapeutics, Inc. (ALDX)
AKB-097Akebia Therapeutics, Inc. (AKBA)
akcea-angptl3-lrxAKCEA THERAPEUTICS, INC. (AKCA)
AL002Alector, Inc. (ALEC)
AL101/GSK4527226Alector, Inc. (ALEC)
alglucosidase alfaSanofi (SNY)
ALN-6400ALNYLAM PHARMACEUTICALS, INC. (ALNY)
aln-ang3West Pharmaceutical Services Inc. (WST)
aln-ang3REGENERON PHARMACEUTICALS, INC. (REGN)
ALN-APPALNYLAM PHARMACEUTICALS, INC. (ALNY)
amlitelimabSanofi (SNY)
AmlitelimabSanofi (SNY)
amt-130uniQure N.V. (QURE)
amx0318Amylyx Pharmaceuticals, Inc. (AMLX)
ANAVEX® 2-73 (blarcamesine)ANAVEX LIFE SCIENCES CORP. (AVXL)
ANAVEX® 3-71 (AF710B)ANAVEX LIFE SCIENCES CORP. (AVXL)
ARO-MAPTARROWHEAD PHARMACEUTICALS, INC. (ARWR)
aroxxenPRF Technologies Ltd. (PRFX)
AroxxenCrinetics Pharmaceuticals, Inc. (CRNX)
ARV-102ARVINAS, INC. (ARVN)
ATI-052Aclaris Therapeutics, Inc. (ACRS)
axo-lenti-pdSio Gene Therapies Inc. (SIOX)
azelapragBioAge Labs, Inc. (BIOA)
BDTX-1535Black Diamond Therapeutics, Inc. (BDTX)
BelumosudilCrinetics Pharmaceuticals, Inc. (CRNX)
bepranemabGT Biopharma, Inc. (GTBP)
best available treatmentIncyte Corp. (INCY)
biib122Denali Therapeutics Inc. (DNLI)
biological/vaccineGH Research PLC (GHRS)
BMS-986446PROTHENA CORP PUBLIC LTD CO (PRTA)
bryostatin-1Neurotrope, Inc. (NTRP)
BusulfanFilana Therapeutics Inc. (FLNA)
BusulfanENANTA PHARMACEUTICALS INC (ENTA)
cagrilintide + semaglutideNovo Nordisk A/S (NVO)
canakinumabNovartis AG (NVS)
CelecoxibUNITED THERAPEUTICS Corp (UTHR)
cenplacel-lCelularity Inc. (CELU)
CholatesMirum Pharmaceuticals, Inc. (MIRM)
cin-107CinCor Pharma, Inc. (CINC)
ct1812COGNITION THERAPEUTICS INC (CGTX)
CTX611CRISPR Therapeutics AG (CRSP)
CytoxanENANTA PHARMACEUTICALS INC (ENTA)
CytoxanFilana Therapeutics Inc. (FLNA)
db-3qHCW Biologics Inc. (HCWB)
db-3qBone Biologics Corp (BBLG)
dfv890Novartis AG (NVS)
dfv890Novartis AG (NVS)
diphenhydramineSanofi (SNY)
DiphenhydramineENANTA PHARMACEUTICALS INC (ENTA)
DiphenhydramineCidara Therapeutics, Inc. (CDTX)
DiphenhydramineFilana Therapeutics Inc. (FLNA)
DiphenhydraminePROTHENA CORP PUBLIC LTD CO (PRTA)
disc-0974Disc Medicine, Inc. (IRON)
disc-0998Disc Medicine, Inc. (IRON)
dupilumabSanofi (SNY)
DupilumabSanofi (SNY)
dusquetideSOLIGENIX, INC. (SNGX)
E2814ELI LILLY & Co (LLY)
EDG-003Edgewise Therapeutics, Inc. (EWTX)
EDG-5506Edgewise Therapeutics, Inc. (EWTX)
eli-002Elicio Therapeutics, Inc. (ELTX)
emixustatKUBOTA PHARMACEUTICAL HOLDINGS CO LTD (ACUC)
energi-f705IMPACT BIOMEDICAL INC. (IBO)
erepoxenXenetic Biosciences, Inc. (XBIO)
etavopivatForma Therapeutics Holdings, Inc. (FMTX)
etokimabANAPTYSBIO, INC (ANAB)
etrasimodPFIZER INC (PFE)
evinacumabWest Pharmaceutical Services Inc. (WST)
evinacumabREGENERON PHARMACEUTICALS, INC. (REGN)
evolocumabNovo Nordisk A/S (NVO)
FamotidineUNITED THERAPEUTICS Corp (UTHR)
fb-102Forte Biosciences, Inc. (FBRX)
fb102Forte Biosciences, Inc. (FBRX)
fxr314VivoSim Labs, INC. (VIVS)
GantenerumabELI LILLY & Co (LLY)
glyceryl bromide/formoterol inhalation aerosolSPRING PHARMACEUTICAL GROUP, INC. (CYIG)
GlycopyrrolateVerona Pharma plc (VRNA)
Glycopyrrolate 21.25 mcgVerona Pharma plc (VRNA)
Glycopyrrolate 42.5 mcgVerona Pharma plc (VRNA)
grf312 5%Grifols S.A. (GRFS)
grf312 5%Grifols SA (GIKLY)
GSK-4532990ARROWHEAD PHARMACEUTICALS, INC. (ARWR)
high dose gt-02287Gain Therapeutics, Inc. (GANX)
hu - hydroxyureaNovo Nordisk A/S (NVO)
human acellular vesselHumacyte Inc. (HUMA)
igc-ad1IGC Pharma, Inc. (IGC)
igc-ad1-activeIGC Pharma, Inc. (IGC)
IGM-2644IGM Biosciences, Inc. (IGMS)
imvotamabIGM Biosciences, Inc. (IGMS)
IMVT-1401Immunovant, Inc. (IMVT)
IMVT-1402Immunovant, Inc. (IMVT)
inaxaplinVERTEX PHARMACEUTICALS INC / MA (VRTX)
inebilizumabViela Bio, Inc. (VIE)
inebilizumabAMGEN INC (AMGN)
inopulseBellerophon Therapeutics, Inc. (BLPH)
ins-gshGH Research PLC (GHRS)
INS1148INSMED Inc (INSM)
Interleukin-2ENANTA PHARMACEUTICALS INC (ENTA)
isomyosamineQ/C TECHNOLOGIES, INC. (QCLS)
iti-1284Intra-Cellular Therapies, Inc. (ITCI)
jan101ALT5 Sigma Corp (ALTS)
kds2010SCILEX HOLDING CO (SCLX)
kio-101Kiora Pharmaceuticals Inc. (KPRX)
KPI-014KALA BIO, Inc. (KALA)
KT-474/SAR444656Kymera Therapeutics, Inc. (KYMR)
L-mentholCrinetics Pharmaceuticals, Inc. (CRNX)
lenrispodunIntra-Cellular Therapies, Inc. (ITCI)
lenrispodun (ITI-214)Intra-Cellular Therapies, Inc. (ITCI)
LesigerceptARROWHEAD PHARMACEUTICALS, INC. (ARWR)
lorundrostat 25mg+sglt2i qdMineralys Therapeutics, Inc. (MLYS)
low dose gt-02287Gain Therapeutics, Inc. (GANX)
lunsekimigSanofi (SNY)
lxe408NOVARTIS AG (NVSEF)
lxe408Novartis AG (NVS)
ly3202626ELI LILLY & Co (LLY)
ly3372689ELI LILLY & Co (LLY)
LY3841136ELI LILLY & Co (LLY)
ly4395089ELI LILLY & Co (LLY)
m281MOMENTA PHARMACEUTICALS INC (MNTA)
mas825Novartis AG (NVS)
MAS825Novartis AG (NVS)
mevidalenELI LILLY & Co (LLY)
mirikizumab -ELI LILLY & Co (LLY)
MitapivatAGIOS PHARMACEUTICALS, INC. (AGIO)
mivelsiranALNYLAM PHARMACEUTICALS, INC. (ALNY)
mk-1167Neuphoria Therapeutics Inc. (NEUP)
MK-1167Merck & Co., Inc. (MRK)
MK-2214Merck & Co., Inc. (MRK)
ml-007c-maMapLight Therapeutics, Inc. (MPLT)
MLR-1019Adhera Therapeutics, Inc. (ATRX)
montelukast versafilmINTELGENX TECHNOLOGIES CORP. (IGXT)
morf-057Morphic Holding, Inc. (MORF)
MORF-057ELI LILLY & Co (LLY)
mosliciguatRoivant Sciences Ltd. (ROIV)
mze782Maze Therapeutics, Inc. (MAZE)
mze829Maze Therapeutics, Inc. (MAZE)
napazimoneDBV Technologies S.A. (DBVT)
NE3107BIOVIE INC. (BIVI)
NEU-411Crinetics Pharmaceuticals, Inc. (CRNX)
nivisnebart (formerly AL101/GSK4527226)Alector, Inc. (ALEC)
nnc0194-0499Novo Nordisk A/S (NVO)
nnc0385-0434 aNovo Nordisk A/S (NVO)
NurOwn®BRAINSTORM CELL THERAPEUTICS INC. (BCLI)
nyx-458Aptinyx Inc. (APTX)
obefazimodAbivax SA (ABVX)
ObefazimodAbivax SA (ABVX)
Obefazimod 50 mg CapsuleAbivax SA (ABVX)
obefazimod miniAbivax SA (ABVX)
obefazimod miniAbivax SA (ABVX)
ObinutuzumabFilana Therapeutics Inc. (FLNA)
ObinutuzumabPROTHENA CORP PUBLIC LTD CO (PRTA)
ObinutuzumabARROWHEAD PHARMACEUTICALS, INC. (ARWR)
ObinutuzumabCidara Therapeutics, Inc. (CDTX)
ObinutuzumabStructure Therapeutics Inc. (GPCR)
oc-02Oyster Point Pharma, Inc. (OYST)
ocs-02Apexigen, Inc. (APGN)
olipudase alfaSanofi (SNY)
olpasiranAMGEN INC (AMGN)
ordesekimabPROVENTION BIO, INC. (PBI)
pacibekitugTourmaline Bio, Inc. (TRML)
PDA-001Celularity Inc. (CELU)
PDA-002Celularity Inc. (CELU)
PegfilgrastimENANTA PHARMACEUTICALS INC (ENTA)
pemvidutideAltimmune, Inc. (ALT)
pemvidutide (ALT-801)Altimmune, Inc. (ALT)
pemvidutide (formerly ALT-801)Altimmune, Inc. (ALT)
pepinemabVACCINEX, INC. (VCNX)
Peripheral Blood Stem Cell InfusionFilana Therapeutics Inc. (FLNA)
pl8177PALATIN TECHNOLOGIES INC (PTN)
PlerixaforENANTA PHARMACEUTICALS INC (ENTA)
pociredirFulcrum Therapeutics, Inc. (FULC)
pps vaccineSanofi (SNY)
ppsv23HCW Biologics Inc. (HCWB)
primecNeuroSense Therapeutics Ltd. (NRSN)
prochymalMesoblast Limited (MESO)
prt2761PORTOLA PHARMACEUTICALS INC (PTLA)
prv-015PROVENTION BIO, INC. (PBI)
prv-015Sanofi (SNY)
ptc518Novartis AG (NVS)
PTC518PTC THERAPEUTICS, INC. (PTCT)
QuetiapineACADIA PHARMACEUTICALS INC (ACAD)
regn9933REGENERON PHARMACEUTICALS, INC. (REGN)
reinovax pcv24 formulation 1HCW Biologics Inc. (HCWB)
reinovax pcv24 formulation 2HCW Biologics Inc. (HCWB)
reinovax pcv24 formulation 3HCW Biologics Inc. (HCWB)
renal autologous cell therapyPROKIDNEY CORP. (PROK)
rencofilstat (formerly CRV431)Hepion Pharmaceuticals, Inc. (CTRVP)
rhGAAAMICUS THERAPEUTICS, INC. (FOLD)
rist4721ARENA PHARMACEUTICALS INC (ARNA)
RO7046015PROTHENA CORP PUBLIC LTD CO (PRTA)
RO7269162Crinetics Pharmaceuticals, Inc. (CRNX)
rp-a501Rocket Pharmaceuticals Inc. (RCKT)
rsv vaccine candidateSanofi (SNY)
S-606001Valneva SE (VALN)
sabirnetugAcumen Pharmaceuticals, Inc. (ABOS)
sabirnetug (ACU193)Acumen Pharmaceuticals, Inc. (ABOS)
sar441566Sanofi (SNY)
SAR441566Sanofi (SNY)
sar442970Sanofi (SNY)
SAR442970Sanofi (SNY)
selatogrelInnovation Pharmaceuticals Inc. (IPIX)
sepranoloneRELMADA THERAPEUTICS, INC. (RLMD)
SER-287Seres Therapeutics, Inc. (MCRB)
SGLT2 inhibitorsENANTA PHARMACEUTICALS INC (ENTA)
SirolimusCrinetics Pharmaceuticals, Inc. (CRNX)
SirolimusENANTA PHARMACEUTICALS INC (ENTA)
SirolimusMerus N.V. (MRUS)
sln360Silence Therapeutics Plc (SLN)
Sodium ChloridePROTHENA CORP PUBLIC LTD CO (PRTA)
spr720Spero Therapeutics, Inc. (SPRO)
SPY120Spyre Therapeutics, Inc. (SYRE)
SPY130Spyre Therapeutics, Inc. (SYRE)
SPY230Spyre Therapeutics, Inc. (SYRE)
SuvecaltamideJazz Pharmaceuticals plc (JAZZ)
tak-062TAKEDA PHARMACEUTICAL CO LTD (TKPHF)
tak-101TAKEDA PHARMACEUTICAL CO LTD (TKPHF)
tak-279TAKEDA PHARMACEUTICAL CO LTD (TKPHF)
TAK-279Crinetics Pharmaceuticals, Inc. (CRNX)
tdap vaccineSanofi (SNY)
TebapivatAGIOS PHARMACEUTICALS, INC. (AGIO)
TemsirolimusELI LILLY & Co (LLY)
TemsirolimusENANTA PHARMACEUTICALS INC (ENTA)
tesamorelinIO Biotech, Inc. (IOBT)
tev-48574 dose regimen aTeva Pharmaceutical Industries Limited (TEVA)
tev-48574 dose regiment bTeva Pharmaceutical Industries Limited (TEVA)
TEV-53408Crinetics Pharmaceuticals, Inc. (CRNX)
tour006Tourmaline Bio, Inc. (TRML)
tour006 -Tourmaline Bio, Inc. (TRML)
tqc3721SPRING PHARMACEUTICAL GROUP, INC. (CYIG)
tqc3927 inhalation aerosolSPRING PHARMACEUTICAL GROUP, INC. (CYIG)
Triamcinolone Hexacetonide Inj Susp 20 MG/MLRevance Therapeutics, Inc. (RVNC)
TrosunilimabAbbVie Inc. (ABBV)
tti-109Tvardi Therapeutics, Inc. (TVRD)
tvb-2640Sagimet Biosciences Inc. (SGMT)
tx45Tectonic Therapeutic, Inc. (TECX)
ub-311Vaxxinity, Inc. (VAXX)
ucb0599GT Biopharma, Inc. (GTBP)
vay736Novartis AG (NVS)
vay736 1ml pfsNovartis AG (NVS)
vay736 2 ml pfsNovartis AG (NVS)
vay736 2ml aiNovartis AG (NVS)
verekitugUpstream Bio, Inc. (UPB)
VerekitugCrinetics Pharmaceuticals, Inc. (CRNX)
vhb937Novartis AG (NVS)
vla15PFIZER INC (PFE)
votoplamPTC THERAPEUTICS, INC. (PTCT)
vtx3232Ventyx Biosciences, Inc. (VTYX)
vtx958Ventyx Biosciences, Inc. (VTYX)
wokvac vaccineGH Research PLC (GHRS)
xpro1595Inmune Bio, Inc. (INMB)
zaltenibartOMEROS CORP (OMER)
zervimesine (CT1812)COGNITION THERAPEUTICS INC (CGTX)
zumilokibartApogee Therapeutics, Inc. (APGE)
Phase 1(193)
DrugCompany
[11C]AZ14132516ASTRAZENECA PLC (AZN)
[14c] lpm3770164ASCENTAGE PHARMA GROUP INTERNATIONAL (AAPG)
2 mL SunButyrate-TGChina Foods Holdings Ltd. (CFOO)
20-valent pneumococcal conjugate vaccinePFIZER INC (PFE)
4 mL SunButyrate-TGChina Foods Holdings Ltd. (CFOO)
4D-3104D Molecular Therapeutics, Inc. (FDMT)
ABBV-8736AbbVie Inc. (ABBV)
ace-1334ACCELERON PHARMA INC (XLRN)
ACE1831Merus N.V. (MRUS)
ACE1831Filana Therapeutics Inc. (FLNA)
ach-5228ACHILLION PHARMACEUTICALS INC (ACHN)
aevi-002AEVI GENOMIC MEDICINE, INC. (GNMX)
aio-001Syneos Health, Inc. (SYNH)
AJ201AVENUE THERAPEUTICS, INC. (ATXI)
AlemtuzumabFilana Therapeutics Inc. (FLNA)
AlloStemSpine® (CELZ-201 ADAPT)CREATIVE MEDICAL TECHNOLOGY HOLDINGS, INC. (CELZ)
AlloStemSpine® Chronic Lower Back Pain (CELZ-201 ADAPT)CREATIVE MEDICAL TECHNOLOGY HOLDINGS, INC. (CELZ)
aln-5288REGENERON PHARMACEUTICALS, INC. (REGN)
ALN-5288ALNYLAM PHARMACEUTICALS, INC. (ALNY)
aln-cidebREGENERON PHARMACEUTICALS, INC. (REGN)
ALN-HTT02ALNYLAM PHARMACEUTICALS, INC. (ALNY)
aln-sncaREGENERON PHARMACEUTICALS, INC. (REGN)
alvr106Kalaris Therapeutics, Inc. (KLRS)
amg 513AMGEN INC (AMGN)
amt-126Applied Molecular Transport Inc. (AMTI)
an2-502998AN2 Therapeutics, Inc. (ANTX)
AN2-502998 (formerly AN15368)AN2 Therapeutics, Inc. (ANTX)
ANAVEX®3-71ANAVEX LIFE SCIENCES CORP. (AVXL)
ANB033ANAPTYSBIO, INC (ANAB)
ANB101ANAPTYSBIO, INC (ANAB)
anito-celArcellx, Inc. (ACLX)
Anti-STEAP1 CAR T-cellsFilana Therapeutics Inc. (FLNA)
anti-thymocyte globulinPROTHENA CORP PUBLIC LTD CO (PRTA)
anti-thymocyte globulinARROWHEAD PHARMACEUTICALS, INC. (ARWR)
anti-thymocyte globulinCidara Therapeutics, Inc. (CDTX)
ANVS301Annovis Bio, Inc. (ANVS)
ANX1502Annexon, Inc. (ANNX)
APG333Apogee Therapeutics, Inc. (APGE)
AUR200Aurinia Pharmaceuticals Inc. (AUPH)
axatilimabIncyte Corp. (INCY)
AxatilimabSyndax Pharmaceuticals Inc (SNDX)
azd1613 - part aASTRAZENECA PLC (AZN)
azd1613 - part bASTRAZENECA PLC (AZN)
BG-A3004BeOne Medicines Ltd. (ONC)
biib094IONIS PHARMACEUTICALS INC (IONS)
BIVV003SANGAMO THERAPEUTICS, INC (SGMO)
bms-986004GH Research PLC (GHRS)
bnc375Neuphoria Therapeutics Inc. (NEUP)
BP1001-ABIO-PATH HOLDINGS, INC. (BPTH)
BusulfanCrinetics Pharmaceuticals, Inc. (CRNX)
BusulfanSANGAMO THERAPEUTICS, INC (SGMO)
cd19 hd allo car tEditas Medicine, Inc. (EDIT)
cd19-car t-cellsGH Research PLC (GHRS)
corplex memantineCorium International, Inc. (CORI)
CTX320CRISPR Therapeutics AG (CRSP)
CUE-401Cue Biopharma, Inc. (CUE)
CUE-501Cue Biopharma, Inc. (CUE)
CytoxanStructure Therapeutics Inc. (GPCR)
CytoxanARROWHEAD PHARMACEUTICALS, INC. (ARWR)
CytoxanCidara Therapeutics, Inc. (CDTX)
CytoxanPROTHENA CORP PUBLIC LTD CO (PRTA)
dendritic cell vaccineGH Research PLC (GHRS)
DexmedetomidineApplied Therapeutics, Inc. (APLT)
Dexmedetomidine and MidodrineApplied Therapeutics, Inc. (APLT)
digoxinNovo Nordisk A/S (NVO)
DiphenhydramineStructure Therapeutics Inc. (GPCR)
DNL628Denali Therapeutics Inc. (DNLI)
DNL952Denali Therapeutics Inc. (DNLI)
donepezil tdsCorium International, Inc. (CORI)
Droxidopa Oral ProductENANTA PHARMACEUTICALS INC (ENTA)
drsp/eeVERTEX PHARMACEUTICALS INC / MA (VRTX)
DVX201 (Unmodified Natural Killer Cells)Coeptis Therapeutics Holdings Inc. (COEP)
edk060NOVARTIS AG (NVSEF)
edk060Novartis AG (NVS)
eli-002 2pElicio Therapeutics, Inc. (ELTX)
EltrombopagCrinetics Pharmaceuticals, Inc. (CRNX)
Exl-111ENANTA PHARMACEUTICALS INC (ENTA)
farabursenRegulus Therapeutics Inc. (RGLS)
FilgrastimCidara Therapeutics, Inc. (CDTX)
FilgrastimARROWHEAD PHARMACEUTICALS, INC. (ARWR)
FilgrastimPROTHENA CORP PUBLIC LTD CO (PRTA)
FilgrastimENANTA PHARMACEUTICALS INC (ENTA)
FludarabinePROTHENA CORP PUBLIC LTD CO (PRTA)
FludarabineCidara Therapeutics, Inc. (CDTX)
FludarabineARROWHEAD PHARMACEUTICALS, INC. (ARWR)
frtx-02Fresh Tracks Therapeutics, Inc. (FRTX)
ft839FATE THERAPEUTICS INC (FATE)
gbt601Global Blood Therapeutics, Inc. (GBT)
Glucose-dependent Insulinotropic PolypeptideENANTA PHARMACEUTICALS INC (ENTA)
Granulocyte Macrophage Colony Stimulating FactorENANTA PHARMACEUTICALS INC (ENTA)
gt-02287Gain Therapeutics, Inc. (GANX)
hemopurifierAethlon Medical Inc. (AEMD)
hyqviaTakeda Pharmaceutical Company Limited American Depositary Shares (each representing 1/2 of a share of Common Stock) (TAK)
hyqviaTAKEDA PHARMACEUTICAL CO LTD (TKPHF)
ibc-ab002Checkpoint Therapeutics, Inc. (CKPT)
ion269IONIS PHARMACEUTICALS INC (IONS)
ion356IONIS PHARMACEUTICALS INC (IONS)
ionis maptIONIS PHARMACEUTICALS INC (IONS)
ionis maptrxIONIS PHARMACEUTICALS INC (IONS)
ipaTelix Pharmaceuticals Limited (TLX)
isc-hpnscInternational Stem Cell CORP (ISCO)
itacitinibIncyte Corp. (INCY)
KER-065Keros Therapeutics, Inc. (KROS)
KYV-101Filana Therapeutics Inc. (FLNA)
lepodisiranELI LILLY & Co (LLY)
Levodopa-CarbidopaAbbVie Inc. (ABBV)
lng/eeVERTEX PHARMACEUTICALS INC / MA (VRTX)
LP659Longboard Pharmaceuticals, Inc. (LBPH)
LUCAR-G79 T cellsLegend Biotech Corp (LEGN)
LUNAR-H5N1Arcturus Therapeutics Holdings Inc. (ARCT)
ly3439539ELI LILLY & Co (LLY)
LY3884961ELI LILLY & Co (LLY)
ly3954068ELI LILLY & Co (LLY)
ly3962681Prevail Therapeutics Inc. (PRVL)
ly4006895ELI LILLY & Co (LLY)
LY4006896ELI LILLY & Co (LLY)
lymphocyte immune globulinARROWHEAD PHARMACEUTICALS, INC. (ARWR)
lymphocyte immune globulinCidara Therapeutics, Inc. (CDTX)
lymphocyte immune globulinFilana Therapeutics Inc. (FLNA)
lymphocyte immune globulinPROTHENA CORP PUBLIC LTD CO (PRTA)
Lymphodepleting chemotherapyFilana Therapeutics Inc. (FLNA)
m230MOMENTA PHARMACEUTICALS INC (MNTA)
mb-106MUSTANG BIO, INC. (MBIO)
Mebendazole (improved formulation)Bullfrog AI Holdings Inc. (BFRG)
memantine tdsCorium International, Inc. (CORI)
MesnaPROTHENA CORP PUBLIC LTD CO (PRTA)
MesnaARROWHEAD PHARMACEUTICALS, INC. (ARWR)
MesnaCidara Therapeutics, Inc. (CDTX)
MesnaStructure Therapeutics Inc. (GPCR)
MesnaENANTA PHARMACEUTICALS INC (ENTA)
mipomersenTG THERAPEUTICS, INC. (TGTX)
mk-4334Neuphoria Therapeutics Inc. (NEUP)
motixafortideGH Research PLC (GHRS)
mze001Maze Therapeutics, Inc. (MAZE)
net/eeVERTEX PHARMACEUTICALS INC / MA (VRTX)
ngm/eeVERTEX PHARMACEUTICALS INC / MA (VRTX)
nio752Novartis AG (NVS)
nmra-215Neumora Therapeutics, Inc. (NMRA)
nmra-266Neumora Therapeutics, Inc. (NMRA)
nmra-323511Neumora Therapeutics, Inc. (NMRA)
nmra-898Neumora Therapeutics, Inc. (NMRA)
nnc0519-0130Novo Nordisk A/S (NVO)
nnc0560-0004Novo Nordisk A/S (NVO)
nnc4005-001Novo Nordisk A/S (NVO)
ojr520Novartis AG (NVS)
ojr520NOVARTIS AG (NVSEF)
OrforglipronELI LILLY & Co (LLY)
ov350Ovid Therapeutics Inc. (OVID)
pali-2108PALISADE BIO, INC. (PALI)
PaliferminMerus N.V. (MRUS)
PaliferminENANTA PHARMACEUTICALS INC (ENTA)
Peripheral Blood Stem Cell InfusionPROTHENA CORP PUBLIC LTD CO (PRTA)
pf-08046044/sgn-35cPFIZER INC (PFE)
pitavastatinNovo Nordisk A/S (NVO)
PlerixaforSANGAMO THERAPEUTICS, INC (SGMO)
PlerixaforMerus N.V. (MRUS)
pmn310ProMIS Neurosciences Inc. (PMN)
PozelimabREGENERON PHARMACEUTICALS, INC. (REGN)
prn2246/sar442168Principia Biopharma Inc. (PRNB)
PRX019PROTHENA CORP PUBLIC LTD CO (PRTA)
pur1800Pulmatrix, Inc. (PULM)
reni-celEditas Medicine, Inc. (EDIT)
renizgamglogene autogedtemcel (reni-cel)Editas Medicine, Inc. (EDIT)
rgls8429Regulus Therapeutics Inc. (RGLS)
rlyb114Rallybio Corp (RLYB)
rlyb116Rallybio Corp (RLYB)
rosuvastatinNovo Nordisk A/S (NVO)
rVSV∆G-MARV-GPValneva SE (VALN)
selatogrelViatris Inc (VTRS)
SER-147Seres Therapeutics, Inc. (MCRB)
ser-252Serina Therapeutics, Inc. (SER)
SER-252SUPERNUS PHARMACEUTICALS, INC. (SUPN)
SER-301Seres Therapeutics, Inc. (MCRB)
SirolimusStructure Therapeutics Inc. (GPCR)
sl-425Shattuck Labs, Inc. (STTK)
spk-3006Spark Therapeutics, Inc. (SPARK)
SRK-373Scholar Rock Holding Corp (SRRK)
srp-1005Sarepta Therapeutics, Inc. (SRPT)
Standard Lymphodepletion regimenArcellx, Inc. (ACLX)
tocilizumabJuno Therapeutics, Inc. (JUNO)
tp-271TETRAPHASE PHARMACEUTICALS INC (TTPH)
trivalent vaccine candidateSanofi (SNY)
ub-312Vaxxinity, Inc. (VAXX)
velinotamigCullinan Therapeutics, Inc. (CGEM)
venglustatSanofi (SNY)
VERVE-102Travere Therapeutics, Inc. (TVTX)
vg-3927Vigil Neuroscience, Inc. (VIGL)
vib7734Viela Bio, Inc. (VIE)
virus specific t cellsGH Research PLC (GHRS)
vonsetamigREGENERON PHARMACEUTICALS, INC. (REGN)
wtx-921Werewolf Therapeutics, Inc. (HOWL)
XmAb7195Xencor Inc (XNCR)
zb001Zenas BioPharma, Inc. (ZBIO)
Preclinical(205)
DrugCompany
4D-7254D Molecular Therapeutics, Inc. (FDMT)
a2342ALBIREO PHARMA, INC. (ALBO)
a2a agonistsREBUS HOLDINGS, INC. (NSPX)
a3907ALBIREO PHARMA, INC. (ALBO)
aav-gadMeiraGTx Holdings plc (MGTX)
ABO-504ABEONA THERAPEUTICS INC. (ABEO)
ABS-101Absci Corporation (ABSI)
ach-5548ACHILLION PHARMACEUTICALS INC (ACHN)
acu-6151KUBOTA PHARMACEUTICAL HOLDINGS CO LTD (ACUC)
adi-100Aditxt, Inc. (ADTX)
ADP037-ABCAlector, Inc. (ALEC)
ADP050-ABCAlector, Inc. (ALEC)
ADP056Alector, Inc. (ALEC)
ADP062-ABCAlector, Inc. (ALEC)
ADP063-ABCAlector, Inc. (ALEC)
ADP064-ABCAlector, Inc. (ALEC)
ADX-743Aldeyra Therapeutics, Inc. (ALDX)
aeol 11114bAEOLUS PHARMACEUTICALS, INC. (AOLS)
aeol 11207AEOLUS PHARMACEUTICALS, INC. (AOLS)
aevi-005AEVI GENOMIC MEDICINE, INC. (GNMX)
AGTX-2003 (RTI-1092769)Agentix Corp. (AGTX)
AL037Alector, Inc. (ALEC)
AL064Alector, Inc. (ALEC)
AL137Alector, Inc. (ALEC)
aln1003Alaunos Therapeutics, Inc. (TCRT)
ALPHA-0702Alpha Cognition Inc. (ACOG)
ALPHA-0802Alpha Cognition Inc. (ACOG)
ALPHA-1062 in combination with memantineAlpha Cognition Inc. (ACOG)
ALPHA-1062 sublingual formulationAlpha Cognition Inc. (ACOG)
alzheimer'sHEALTHY EXTRACTS INC. (HYEX)
Anti-TSHR candidateViridian Therapeutics, Inc.\DE (VRDN)
ar-14034 srAERIE PHARMACEUTICALS INC (AERI)
ATI-9494Aclaris Therapeutics, Inc. (ACRS)
atx-04AVENUE THERAPEUTICS, INC. (ATXI)
ATYR0101aTYR PHARMA INC (ATYR)
ATYR0750aTYR PHARMA INC (ATYR)
Base editing therapies (C3 and complement targets)Apellis Pharmaceuticals, Inc. (APLS)
cannabis-derived compoundsWEED, INC. (BUDZ)
caris assureCaris Life Sciences Inc. (CAI)
cb101CANTABIO PHARMACEUTICALS INC. (CTBO)
cb102CANTABIO PHARMACEUTICALS INC. (CTBO)
cb201CANTABIO PHARMACEUTICALS INC. (CTBO)
cb301CANTABIO PHARMACEUTICALS INC. (CTBO)
cb401CANTABIO PHARMACEUTICALS INC. (CTBO)
cb5138-3COHBAR, INC. (COBU)
cdx-301CARDAX, INC. (CDXI)
chronic wasting disease vaccineGENETHERA INC (GTHR)
cnm-agzn17Clene Inc. (CLNN)
cnm-znagClene Inc. (CLNN)
companion diagnostic tests for asthmabioAffinity Technologies Inc. (BIAF)
CPI-182Corvus Pharmaceuticals, Inc. (CRVS)
cpt60621COEPTIS THERAPEUTICS INC. (NDYN)
crebankitugZura Bio Ltd (ZURA)
cts-2090Histogen Inc. (HSTO)
cts-2096Histogen Inc. (HSTO)
dolcanatideSYNERGY PHARMACEUTICALS LLC (SGYP)
dtx701Dimension Therapeutics, Inc. (DMTX)
eb07Edesa Biotech, Inc. (EDSA)
ebd therapyAcumen Pharmaceuticals, Inc. (ABOS)
electroceuticals therapeutic devicesENDONOVO THERAPEUTICS, INC. (ENDV)
ent-576ENTEST GROUP, INC. (ETNI)
EPS-3903ENANTA PHARMACEUTICALS INC (ENTA)
eq302Equillium, Inc. (EQ)
eq504Equillium, Inc. (EQ)
ergod2ENTIA BIOSCIENCES, INC. (ERGO)
ergod2 neuroENTIA BIOSCIENCES, INC. (ERGO)
et-700Eton Pharmaceuticals, Inc. (ETON)
f528GYRE THERAPEUTICS, INC. (GYRE)
fin-524Finch Therapeutics Group, Inc. (FNCH)
fin-525Finch Therapeutics Group, Inc. (FNCH)
fmd vaccineGENVEC INC (GNVC)
frtx-10Fresh Tracks Therapeutics, Inc. (FRTX)
fusr1EVOLUTIONARY GENOMICS, INC. (FNAM)
gba1 gene replacementVoyager Therapeutics, Inc. (VYGR)
gba1 gene therapyVoyager Therapeutics, Inc. (VYGR)
gsd1b programPrime Medicine, Inc. (PRME)
herdsafeGENETHERA INC (GTHR)
hpp3033vTv Therapeutics Inc. (VTVT)
ht-003Hoth Therapeutics, Inc. (HOTH)
ht-alzHoth Therapeutics, Inc. (HOTH)
ht-vaHoth Therapeutics, Inc. (HOTH)
ic-500IVERIC bio, Inc. (ISEE)
idrx-73Blueprint Medicines Corp (BPMC)
igc-1cIGC Pharma, Inc. (IGC)
igc-m3IGC Pharma, Inc. (IGC)
imx-120Immix Biopharma, Inc. (IMMX)
In vivo HSC gene editing program for SCD and TDTEditas Medicine, Inc. (EDIT)
inb-600IN8BIO, INC. (INAB)
inb-619IN8BIO, INC. (INAB)
infectious disease vaccinesTranslate Bio, Inc. (TBIO)
inm-901InMed Pharmaceuticals Inc. (INM)
IRF5 programALUMIS INC. (ALMS)
jkb-122Biostax Corp. (BTAX)
kb-7898Kronos Bio, Inc. (KRON)
kind-509Kindred Biosciences, Inc. (KIN)
kros 102Kairos Pharma, LTD. (KAPA)
KT-294Kymera Therapeutics, Inc. (KYMR)
KT-295Kymera Therapeutics, Inc. (KYMR)
KYV-201Intellia Therapeutics, Inc. (NTLA)
labp-66Landos Biopharma, Inc. (LABP)
labp-73Landos Biopharma, Inc. (LABP)
lb-1ProPhase Labs, Inc. (PRPH)
lb-2ProPhase Labs, Inc. (PRPH)
Licensed siRNA targeting TMPRSS6AGIOS PHARMACEUTICALS, INC. (AGIO)
lmpIGC Pharma, Inc. (IGC)
lnc-001REBUS HOLDINGS, INC. (NSPX)
man-11Q BioMed Inc. (QBIO)
man-19Q BioMed Inc. (QBIO)
man-dexNAVIDEA BIOPHARMACEUTICALS, INC. (NAVB)
map vaccineGENETHERA INC (GTHR)
matloc 1MARIZYME, INC. (MRZM)
matloc 2MARIZYME, INC. (MRZM)
mirokidneyMiromatrix Medical Inc. (MIRO)
mitral heart valve disease treatmentPHIBRO ANIMAL HEALTH CORP (PAHC)
mosaiqQuotient Ltd (QTNT)
mupadolimabCorvus Pharmaceuticals, Inc. (CRVS)
NAV-4694Lantheus Holdings, Inc. (LNTH)
nc181NextCure, Inc. (NXTC)
nexi-004NexImmune, Inc. (NEXI)
next-generation ITK inhibitor preclinical candidatesCorvus Pharmaceuticals, Inc. (CRVS)
niagenNiagen Bioscience, Inc. (NAGE)
nm-0039 METERS BIOPHARMA, INC. (NMTR)
nmra-ck1δNeumora Therapeutics, Inc. (NMRA)
nmra-gcaseNeumora Therapeutics, Inc. (NMRA)
nmra-nmdaNeumora Therapeutics, Inc. (NMRA)
non-complement cardiovascular target candidateRA PHARMACEUTICALS, INC. (RARX)
novartis hd programVoyager Therapeutics, Inc. (VYGR)
novartis hd program productVoyager Therapeutics, Inc. (VYGR)
novel cannabinoid therapeuticGreater Cannabis Company, Inc. (GCAN)
Np-01CNBX Pharmaceuticals Inc. (CNBX)
NP-02CNBX Pharmaceuticals Inc. (CNBX)
nsr-abca4Nightstar Therapeutics plc (NITE)
nsr-best1Nightstar Therapeutics plc (NITE)
nurownBRAINSTORM CELL THERAPEUTICS INC. (BCLI)
oc-101Oyster Point Pharma, Inc. (OYST)
optejet ufdHYPERION DEFI, INC. (HYPD)
Oral complement inhibitorApellis Pharmaceuticals, Inc. (APLS)
oral factor d inhibitorsACHILLION PHARMACEUTICALS INC (ACHN)
oral small molecule c5 inhibitorRA PHARMACEUTICALS, INC. (RARX)
Pan-mutant BRAF degrader program (proprietary)Nurix Therapeutics, Inc. (NRIX)
Pan-mutant BRAF program (mutant BRAF degraders)Nurix Therapeutics, Inc. (NRIX)
patrol platformNeuBase Therapeutics, Inc. (NBSE)
pcs499Processa Pharmaceuticals, Inc. (PCSA)
phoenix autoPhoenix Life Sciences International Limited. (PLSI)
pl7737PALATIN TECHNOLOGIES INC (PTN)
pm577Prime Medicine, Inc. (PRME)
Pompe program candidateDyne Therapeutics, Inc. (DYN)
potential treatment for mitral valve disease in dogsPHIBRO ANIMAL HEALTH CORP (PAHC)
prime edited scipPrime Medicine, Inc. (PRME)
proflowSCICLONE PHARMACEUTICALS INC (SCLN)
prx-119Protalix BioTherapeutics, Inc. (PLX)
PRX012PROTHENA CORP PUBLIC LTD CO (PRTA)
PRX123PROTHENA CORP PUBLIC LTD CO (PRTA)
pt001Pandion Therapeutics, Inc. (PAND)
pt627Pandion Therapeutics, Inc. (PAND)
pulsevet shock wave therapyZomedica Corp. (ZOMDF)
RDX020ARDELYX, INC. (ARDX)
react/genPROKIDNEY CORP. (PROK)
react/universalPROKIDNEY CORP. (PROK)
repurposed drug for cns cancerCosmos Health Inc. (COSM)
rlyb332Rallybio Corp (RLYB)
ropinirole tdsCorium International, Inc. (CORI)
SavaDxFilana Therapeutics Inc. (FLNA)
sc379Sana Biotechnology, Inc. (SANA)
sequential-dialysis techniquePREMIER BIOMEDICAL INC (BIEI)
ser 252Serina Therapeutics, Inc. (SER)
ser-603Seres Therapeutics, Inc. (MCRB)
sg293Sana Biotechnology, Inc. (SANA)
sg299Sana Biotechnology, Inc. (SANA)
sgx943SOLIGENIX, INC. (SNGX)
sickle cell disease productGreenLight Biosciences Holdings, PBC (GRNA)
sig-007Sigilon Therapeutics, Inc. (SGTX)
siRNA targeting Beta2-spectrinBullfrog AI Holdings Inc. (BFRG)
sl65-based candidatesLogicBio Therapeutics, Inc. (LOGC)
sln548Silence Therapeutics Plc (SLN)
sls-004SEELOS THERAPEUTICS, INC. (SEEL)
sls-007SEELOS THERAPEUTICS, INC. (SEEL)
SPC-14Silo Pharma, Inc. (SILO)
spk-gaaSpark Therapeutics, Inc. (SPARK)
spk-tpp1Spark Therapeutics, Inc. (SPARK)
stat-201COEPTIS THERAPEUTICS INC. (NDYN)
szn-413Surrozen Inc. (SRZN)
tac-celiacSQZ Biotechnologies Co (SQZB)
tau silencing gene therapyVoyager Therapeutics, Inc. (VYGR)
testing services for clinical trialsINTERLEUKIN GENETICS INC (ILIU)
tgr-63IGC Pharma, Inc. (IGC)
tmb-003TREX WIND-DOWN, INC. (TMBR)
torudokimabZura Bio Ltd (ZURA)
tp-271LA JOLLA PHARMACEUTICAL CO (LJPC)
TSHR Antagonist ProgramCrinetics Pharmaceuticals, Inc. (CRNX)
undisclosed cardiometabolic program 1Korro Bio, Inc. (KRRO)
undisclosed cardiometabolic program 2Korro Bio, Inc. (KRRO)
unspecifiedPassage BIO, Inc. (PASG)
vadc45Vor Biopharma Inc. (VOR)
vax-xlVaxcyte, Inc. (PCVX)
vectorized anti-amyloid antibodyVoyager Therapeutics, Inc. (VYGR)
vib1116Viela Bio, Inc. (VIE)
vitaguardBioNexus Gene Lab Corp (BGLC)
vxx-301Vaxxinity, Inc. (VAXX)
vy-tau01Voyager Therapeutics, Inc. (VYGR)
vy1706Voyager Therapeutics, Inc. (VYGR)
wilson's disease programPrime Medicine, Inc. (PRME)
zegocractin (oral, preclinical administration)CalciMedica, Inc. (CALC)
zofinZeo ScientifiX, Inc. (ZEOX)
zw1528Zymeworks Inc. (ZYME)
Unknown(53)
DrugCompany
15-0 h20National Research Corporation Common Stock (Delaware) (NRC)
15-0 h20GH Research PLC (GHRS)
15-0 H20Valneva SE (VALN)
acg-801Aceragen, Inc. (ACGN)
al-101Oncotelic Therapeutics, Inc. (OTLC)
alglucosidase alfa gz419829Sanofi (SNY)
alirocumabSanofi (SNYNF)
ALZN002Alzamend Neuro, Inc. (ALZN)
anti tnf therapy including infliximabIO Biotech, Inc. (IOBT)
Any other SSRI/SNRI not already specifiedENANTA PHARMACEUTICALS INC (ENTA)
BCX10013BIOCRYST PHARMACEUTICALS INC (BCRX)
BinaxNOW® and Panbio® rapid testing platformsABBOTT LABORATORIES (ABT)
Cannabis Genomic Study (Sangre AT, LLC)WEED, INC. (BUDZ)
CLN1 program (out-licensed to Taysha)ABEONA THERAPEUTICS INC. (ABEO)
CLS-001Comera Life Sciences Holdings, Inc. (CMRA)
CPT60621Coeptis Therapeutics Holdings Inc. (COEP)
crexontAmneal Pharmaceuticals, Inc. (AMRX)
diphenhydramineMesoblast Limited (MESO)
Epi+Gen CHD™Cardio Diagnostics Holdings Inc. (CDIO)
filingAldeyra Therapeutics, Inc. (ALDX)
GBA1 discovery programCamp4 Therapeutics Corp (CAMP)
guselkumabInnovation Pharmaceuticals Inc. (IPIX)
HeartRisk™Cardio Diagnostics Holdings Inc. (CDIO)
Heptral™ABBOTT LABORATORIES (ABT)
inclisiranSanofi (SNYNF)
inclisiranSanofi (SNY)
infectimunePDS Biotechnology Corp (PDSB)
InFoods® platform (other disease targets)BIOMERICA INC (BMRA)
legalonMylan II B.V. (MYL)
Medical formulations portfolioCannabis Bioscience International Holdings, Inc. (CBIH)
Methylation detection kitTwist Bioscience Corp (TWST)
natural matrix protein fibersHCW Biologics Inc. (HCWB)
Next generation bispecific antibody platformCelldex Therapeutics, Inc. (CLDX)
NGS ToolsTwist Bioscience Corp (TWST)
no biologicsIO Biotech, Inc. (IOBT)
noninterventionalREGENERON PHARMACEUTICALS, INC. (REGN)
optimal medical therapyUtah Medical Products Inc. (UTMD)
Oral C2 InhibitorBIOCRYST PHARMACEUTICALS INC (BCRX)
Oral C5 InhibitorBIOCRYST PHARMACEUTICALS INC (BCRX)
PluriPain®BIOADAPTIVES, INC. (BDPT)
Precise MRD (minimum residual disease)MYRIAD GENETICS INC (MYGN)
PrecisionCHD™Cardio Diagnostics Holdings Inc. (CDIO)
ProLectin-RxBIOXYTRAN, INC (BIXT)
RemicadeMerck & Co., Inc. (MRK)
RisankizumabENANTA PHARMACEUTICALS INC (ENTA)
Samyr™ABBOTT LABORATORIES (ABT)
Serc™ABBOTT LABORATORIES (ABT)
SimponiMerck & Co., Inc. (MRK)
ST-400SANGAMO THERAPEUTICS, INC (SGMO)
Transmetil™ABBOTT LABORATORIES (ABT)
VaxneuvanceMerck & Co., Inc. (MRK)
vonicog alfaTAKEDA PHARMACEUTICAL CO LTD (TKPHF)
Xpro1595/INB03Xencor Inc (XNCR)
Phase 1/Phase 2(65)
DrugCompany
10 GE XenokidneyUNITED THERAPEUTICS Corp (UTHR)
80-ppm noGH Research PLC (GHRS)
aav9-glb1National Research Corporation Common Stock (Delaware) (NRC)
abbv-1758AbbVie Inc. (ABBV)
aln-pnpREGENERON PHARMACEUTICALS, INC. (REGN)
amg 732AMGEN INC (AMGN)
amt-191uniQure N.V. (QURE)
anti-cd19 car t-cellsGH Research PLC (GHRS)
ARO-MAPT-SCARROWHEAD PHARMACEUTICALS, INC. (ARWR)
axo-aav-gm2Sio Gene Therapies Inc. (SIOX)
BEAM-101Beam Therapeutics Inc. (BEAM)
chlamydia mrna vaccineSanofi (SNY)
CTX321CRISPR Therapeutics AG (CRSP)
eq001Equillium, Inc. (EQ)
ev71 inactivated enterovirus vaccine )(for ages 6-71 months)SINOVAC BIOTECH LTD (SVA)
gene therapyCalidi Biotherapeutics Inc. (CLDI)
gene therapyNORTHWEST BIOTHERAPEUTICS INC (NWBO)
GGTA1 KO ThymokidneyUNITED THERAPEUTICS Corp (UTHR)
high-dose tetravalent inactivated enterovirus vaccine )SINOVAC BIOTECH LTD (SVA)
inca034176Incyte Corp. (INCY)
intra-striatal raav5-mihttuniQure N.V. (QURE)
ion717IONIS PHARMACEUTICALS INC (IONS)
isaralgagene civaparvovecSANGAMO THERAPEUTICS, INC (SGMO)
Isaralgagene civaparvovec (ST-920)SANGAMO THERAPEUTICS, INC (SGMO)
itu512NOVARTIS AG (NVSEF)
itu512Novartis AG (NVS)
lonigutamabACELYRIN, Inc. (SLRN)
lonigutamabALUMIS INC. (ALMS)
low-dose of tetravalent inactivated enterovirus vaccineSINOVAC BIOTECH LTD (SVA)
lx1001Lexeo Therapeutics, Inc. (LXEO)
ly-m003IO Biotech, Inc. (IOBT)
ly3884961Prevail Therapeutics Inc. (PRVL)
medium-dose tetravalent inactivated enterovirus vaccineSINOVAC BIOTECH LTD (SVA)
mesenchymal stem cellsGH Research PLC (GHRS)
miransertibARQULE INC (ARQL)
mRNA-1975Moderna, Inc. (MRNA)
mRNA-1982Moderna, Inc. (MRNA)
multivalent pneumococcal vaccine - formulation 1PFIZER INC (PFE)
multivalent pneumococcal vaccine - formulation 2PFIZER INC (PFE)
multivalent pneumococcal vaccine - formulation 3PFIZER INC (PFE)
multivalent pneumococcal vaccine - formulation 4PFIZER INC (PFE)
optogenetic product candidateAPPLIED GENETIC TECHNOLOGIES CORP (AGTC)
pm359Prime Medicine, Inc. (PRME)
pr001Prevail Therapeutics Inc. (PRVL)
quadrivalent influenza standard dose vaccineSanofi (SNY)
rapcabtagene autoleucelNovartis AG (NVS)
rapcabtagene autoleucelNovartis AG (NVS)
Ristoglogene autogetemcel (risto-cel)Beam Therapeutics Inc. (BEAM)
rsv/hmpv vaccine candidate dose aSanofi (SNY)
rsv/hmpv vaccine candidate dose bSanofi (SNY)
rsv/hmpv vaccine candidate dose lSanofi (SNY)
snk01NKGen Biotech, Inc. (NKGN)
st-506SANGAMO THERAPEUTICS, INC (SGMO)
ST-920SANGAMO THERAPEUTICS, INC (SGMO)
syn-020Theriva Biologics, Inc. (TOVX)
tb-500IO Biotech, Inc. (IOBT)
tiv mrna-ha vaccine 2Sanofi (SNY)
trivalent messenger ribonucleic acid hemagglutinin vaccine 1Sanofi (SNY)
UX701Ultragenyx Pharmaceutical Inc. (RARE)
vca-894aVanda Pharmaceuticals Inc. (VNDA)
vinblastineTAKEDA PHARMACEUTICAL CO LTD (TKPHF)
vy7523Voyager Therapeutics, Inc. (VYGR)
WVE-003Wave Life Sciences Ltd. (WVE)
WVE-008Wave Life Sciences Ltd. (WVE)
XmAb564Xencor Inc (XNCR)
Phase 4(78)
DrugCompany
AcetaminophenStructure Therapeutics Inc. (GPCR)
adalimumabTakeda Pharmaceutical Company Limited American Depositary Shares (each representing 1/2 of a share of Common Stock) (TAK)
adalimumabTAKEDA PHARMACEUTICAL CO LTD (TKPHF)
Akkermansia muciniphila + InfliximabCrinetics Pharmaceuticals, Inc. (CRNX)
Akkermansia muciniphila + InfliximabENANTA PHARMACEUTICALS INC (ENTA)
alirocumabSanofi (SNY)
Atozet 10/40 mg or 10/80 mgOrganon & Co. (OGN)
AvacopanAMGEN INC (AMGN)
avalglucosidase alfaSanofi (SNY)
avalglucosidase alfa-ngptSanofi (SNY)
avalglucosidase alfa-ngpt ivSanofi (SNY)
Baxdrostat and dapagliflozinASTRAZENECA PLC (AZN)
Baxdrostat/dapagliflozinASTRAZENECA PLC (AZN)
Belumosudil mesylateSanofi (SNY)
BGF- BUDESONIDE/GLYCOPYRRONIUM/FORMOTEROLASTRAZENECA PLC (AZN)
budesonide/glycopyrrolate/formoterolASTRAZENECA PLC (AZN)
budesonide/glycopyrronium/formoterolASTRAZENECA PLC (AZN)
Cannabidiol Oral Solution [Epidiolex]Jazz Pharmaceuticals plc (JAZZ)
cetirizineSanofi (SNY)
CHM intervention groupValneva SE (VALN)
crexont erImpax Laboratories, LLC (IPXL)
Dapagliflozin 10mg TabASTRAZENECA PLC (AZN)
DexmedetomidineCOGNITION THERAPEUTICS INC (CGTX)
Dexmedetomidine infusionCOGNITION THERAPEUTICS INC (CGTX)
Efgartigimod PH20 SCARGENX SE (ARGX)
EmicizumabENANTA PHARMACEUTICALS INC (ENTA)
empagliflozinENANTA PHARMACEUTICALS INC (ENTA)
enalaprilNovartis AG (NVS)
Epidiolex 100 mg/mL Oral SolutionJazz Pharmaceuticals plc (JAZZ)
Fexofenadine HCL and pseudoephedrine HCLSanofi (SNY)
Glucose IVENANTA PHARMACEUTICALS INC (ENTA)
High dose potent statinCYTOKINETICS INC (CYTK)
High dose potent statinUNITED THERAPEUTICS Corp (UTHR)
ibrutinibIncyte Corp. (INCY)
immune globulinTakeda Pharmaceutical Company Limited American Depositary Shares (each representing 1/2 of a share of Common Stock) (TAK)
inclisiran sodium 300 mg inNovartis AG (NVS)
InfliximabCrinetics Pharmaceuticals, Inc. (CRNX)
InfliximabENANTA PHARMACEUTICALS INC (ENTA)
Intervention groupValneva SE (VALN)
KarXTBRISTOL MYERS SQUIBB CO (BMY)
LIVMARLI (maralixibat)Mirum Pharmaceuticals, Inc. (MIRM)
MemantineSUPERNUS PHARMACEUTICALS, INC. (SUPN)
Memantine Oral TabletSUPERNUS PHARMACEUTICALS, INC. (SUPN)
N-acetylcysteineENANTA PHARMACEUTICALS INC (ENTA)
Nebulized TyvasoUNITED THERAPEUTICS Corp (UTHR)
Olimel N12ENANTA PHARMACEUTICALS INC (ENTA)
OmalizumabENANTA PHARMACEUTICALS INC (ENTA)
Palmitoleic Acid + InfliximabENANTA PHARMACEUTICALS INC (ENTA)
PCV15UNITED THERAPEUTICS Corp (UTHR)
PimavanserinACADIA PHARMACEUTICALS INC (ACAD)
Pimavanserin 34 milligrams [Nuplazid]ACADIA PHARMACEUTICALS INC (ACAD)
Pimavanserin tartrateACADIA PHARMACEUTICALS INC (ACAD)
Pimavanserin Tartrate 34 Mg ORAL CAPSULE [NUPLAZID]ACADIA PHARMACEUTICALS INC (ACAD)
plasma-derived fviii/vwf concentrateGrifols S.A. (GRFS)
prasugrel or ticagrelorCidara Therapeutics, Inc. (CDTX)
replagalSHIRE PLC (SHPGF)
rozanolixizumabPOINT Biopharma Global Inc. (PNT)
sacubitril/valsartanNovartis AG (NVS)
Simufilam 100 mg oral tabletFilana Therapeutics Inc. (FLNA)
Streptococcus pneumoniae serotype 3UNITED THERAPEUTICS Corp (UTHR)
telitaciceptGH Research PLC (GHRS)
tocilizumabGH Research PLC (GHRS)
TP-05Tarsus Pharmaceuticals, Inc. (TARS)
treatment aASTRAZENECA PLC (AZN)
treatment bASTRAZENECA PLC (AZN)
treatment cASTRAZENECA PLC (AZN)
ustekinumabGH Research PLC (GHRS)
ustekinumabTakeda Pharmaceutical Company Limited American Depositary Shares (each representing 1/2 of a share of Common Stock) (TAK)
ustekinumabTAKEDA PHARMACEUTICAL CO LTD (TKPHF)
vedolizumabTAKEDA PHARMACEUTICAL CO LTD (TKPHF)
VedolizumabENANTA PHARMACEUTICALS INC (ENTA)
vedolizumab ivTakeda Pharmaceutical Company Limited American Depositary Shares (each representing 1/2 of a share of Common Stock) (TAK)
vinblastineTakeda Pharmaceutical Company Limited American Depositary Shares (each representing 1/2 of a share of Common Stock) (TAK)
xanomeline entericBRISTOL MYERS SQUIBB CO (BMY)
xanomeline/trospiumBRISTOL MYERS SQUIBB CO (BMY)
Zibotentan/DapagliflozinASTRAZENECA PLC (AZN)
zunveylAlpha Cognition Inc. (ACOG)
zunveyl + memantineAlpha Cognition Inc. (ACOG)

Compare drugs

Frequently asked questions

How many drugs are in development for Disease?

BioSniper tracks 1401 drugs in development for Disease across 452 companies.

How many clinical trials target Disease?

There are 2 clinical trials targeting Disease tracked by BioSniper.

What is the prevalence of Disease?

The estimated prevalence of Disease is approximately 0.7 per 100,000 population.

Deep-dive into Disease

Full trial data, competitive analysis, and AI-powered pipeline tracking.

Start Free Analysis
    Disease — Drugs in Development & Clinical Trials | BioSniper