olipudase alfa
olipudase alfa: 2 clinical trials tracked.
olipudase alfa evidence translation
What we can confirm
2 tracked trials
What it means
What to watch
Prepared research question
What is verified about olipudase alfa, and what remains unknown?
Traceable citations · Unknowns marked
See linked entities and source evidence0 indications · 1 study sponsors
Related indications
No linked indication is available.
Study sponsors
Clinical Trial Registry Records (2)
A Prospective Observational Study to Assess the Long-term Safety and Immunogenicity of Olipudase Alfa Therapy During Routine Clinical Care in Pediatric Patients Less Than 2 Years of Age With Acid Sphingomyelinase Deficiency
Primary endpoint: Number of cases in the exposed population with AEs, SAEs, and AESIs (including moderate/severe or recurrent hypersensitivity reactions and infusion-associated reactions)
A Long-Term Follow-up Study to Evaluate Safety and Tolerability of Olipudase Alfa in Patients Who Completed the DFI12712 or the LTS13632 Study in France
Primary endpoint: Number of Participants With Adverse Events (AEs) and Serious Adverse Events (SAEs)