alglucosidase alfa
alglucosidase alfa: 2 clinical trials tracked.
alglucosidase alfa evidence translation
What we can confirm
2 tracked trials
What it means
What to watch
Prepared research question
What is verified about alglucosidase alfa, and what remains unknown?
Traceable citations · Unknowns marked
See linked entities and source evidence0 indications · 2 study sponsors
Related indications
No linked indication is available.
Clinical Trials (2)
A Phase 3 Double-blind Randomized Study to Assess the Efficacy and Safety of Intravenous ATB200 Co-administered With Oral AT2221 in Adult Subjects With Late-onset Pompe Disease Compared With Alglucosidase Alfa/Placebo
Primary endpoint: Change From Baseline to Week 52 in 6 Minute Walk Distance (6MWD)
An Open-label Ascending Dose Cohort Study to Assess the Safety, Pharmacokinetics, and Preliminary Efficacy of Avalglucosidase Alfa (NeoGAA, GZ402666) in Patients With Infantile-onset Pompe Disease Treated With Alglucosidase Alfa Who Demonstrate Clinical Decline or Sub-optimal Clinical Response
Primary endpoint: PAP: Number of Participants With Treatment-emergent Adverse Events (TEAEs), Serious Treatment-emergent Adverse Events, and Adverse Event of Special Interest (AESI)