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zilganersen

zilganersen: developed by 1 company · 2 clinical trials tracked.

zilganersen evidence translation

What we can confirm

What it means

Source-backed records connect zilganersen to IONS; that link alone does not prove the drug works.

What to watch

Watch trial status, endpoints, and the next source-backed update.
BioSniper AIPage evidence connected

Prepared research question

How could zilganersen → IONS affect its developer, and what evidence supports the link?

Run cited research

Traceable citations · Unknowns marked

See linked entities and source evidence1 indications · 0 study sponsors

Related indications

Alexander Disease

Study sponsors

No additional listed-company sponsor is linked.

Development Pipeline (1)
CompanyPhase
IONIS PHARMACEUTICALS INC (IONS)
Alexander Disease
Phase 3
Clinical Trials (2)

Zilganersen Expanded Access Program for Individuals With Alexander Disease

Available
Expanded AccessIonis Pharmaceuticals, Inc.

A Phase 1-3, Double-Blind, Randomized, Placebo-Controlled Study to Evaluate the Efficacy, Safety, Pharmacokinetics and Pharmacodynamics of Intrathecally Administered ION373 in Patients With Alexander Disease

NCT04849741·Phase 3·IONS
Active, not recruiting

Primary endpoint: Percent Change from Baseline in the 10-Meter Walk Test (10MWT)

InterventionalRandomizeddouble54 enrolledStarted 2021-06Completion 2034-0713 sites · Australia, Canada, Israel, Italy…Ionis Pharmaceuticals, Inc.

Frequently asked questions

Who is developing zilganersen?

zilganersen is being developed by IONIS PHARMACEUTICALS INC.

How many clinical trials involve zilganersen?

BioSniper tracks 2 clinical trials involving zilganersen.