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zilganersen

zilganersen: 2 clinical trials tracked.

zilganersen evidence translation

What we can confirm

2 tracked trials

No verified listed company relationship

What it means

AI will separate confirmed drug evidence from unknown company context.

What to watch

Watch trial status, endpoints, and the next source-backed update.
BioSniper AIPage evidence connected

Prepared research question

What is verified about zilganersen, and what remains unknown?

Run cited research

Traceable citations · Unknowns marked

See linked entities and source evidence0 indications · 1 study sponsors

Related indications

No linked indication is available.

Clinical Trial Registry Records (2)

Zilganersen Expanded Access Program for Individuals With Alexander Disease

NCT07487389Registry updated 2026-09-29·IONS
Approved for marketing
Expanded AccessIonis Pharmaceuticals, Inc.

A Phase 1-3, Double-Blind, Randomized, Placebo-Controlled Study to Evaluate the Efficacy, Safety, Pharmacokinetics and Pharmacodynamics of Intrathecally Administered ION373 in Patients With Alexander Disease

NCT04849741Registry updated 2026-08-21·Phase 3·IONS
Active, not recruiting

Primary endpoint: Percent Change from Baseline in the 10-Meter Walk Test (10MWT)

InterventionalRandomizeddouble54 enrolledStarted 2021-06Completion 2034-0713 sites · Australia, Canada, Israel, Italy…Ionis Pharmaceuticals, Inc.