SMA

Rare Disease·MeSH: Spinal Muscular Atrophies of Childhood

Prevalence

75.0 / 100K

Incidence

47.0 / 100K/yr

738 drugs in development·186 companies·4 clinical trials

Drug Pipeline by Phase

Approved(62)

Drug	Company
acam2000	Emergent BioSolutions Inc. (EBS)
Alimta®	ELI LILLY & Co (LLY)
AMVUTTRA	ALNYLAM PHARMACEUTICALS, INC. (ALNY)
aPROMISE (commercialized as PYLARIFY AI in the U.S.)	Lantheus Holdings, Inc. (LNTH)
asmanex hfa	Organon & Co. (OGN)
Aspaveli	Apellis Pharmaceuticals, Inc. (APLS)
Aybintio (SB8)	Organon & Co. (OGN)
brightening antioxidant serum pigment correcting formula	REGENEREX PHARMA, INC. (RGPX)
chenodiol	Optec International, Inc. (GM)
clarithromycin	SUNSET ISLAND GROUP (SUN)
Clarithromycin Granules and Capsules	CHINA PHARMA HOLDINGS, INC. (CPHI)
cosela	G1 Therapeutics, Inc. (GTHX)
Cyramza	ELI LILLY & Co (LLY)
diphenhydramine	ACHIEVE LIFE SCIENCES, INC. (ACHV)
diphenhydramine	Miromatrix Medical Inc. (MIRO)
docetaxel	PFIZER INC (PFE)
docetaxel	Amneal Pharmaceuticals, Inc. (AMRX)
Dr. Xiao Brand Huangjingdanggui Tablet	China Health Industries Holdings, Inc. (CHHE)
Dr. Xiao Huangjingdanggui Tablet	China Health Industries Holdings, Inc. (CHHE)
elzonris	STEMLINE THERAPEUTICS INC (STML)
empaveli	KORU Medical Systems Inc. Common Stock (DE) (KRMD)
EMPAVELI	Apellis Pharmaceuticals, Inc. (APLS)
emrelis	AbbVie Inc. (ABBV)
Evrysdi	PTC THERAPEUTICS, INC. (PTCT)
fluconazole	ANI PHARMACEUTICALS INC (ANIP)
gavreto	RIGEL PHARMACEUTICALS INC (RIGL)
GIVLAARI	ALNYLAM PHARMACEUTICALS, INC. (ALNY)
ibtrozi	Nuvation Bio Inc. (NUVB)
Imdelltra	Royalty Pharma plc (RPRX)
iv tpoxx	SIGA TECHNOLOGIES INC (SIGA)
Jaypirca	ELI LILLY & Co (LLY)
Jaypirca®	ELI LILLY & Co (LLY)
Jemperli	ANAPTYSBIO, INC (ANAB)
krazati	BRISTOL MYERS SQUIBB CO (BMY)
LB Brand Xinpin Capsule	China Health Industries Holdings, Inc. (CHHE)
LB Xinpin Capsule	China Health Industries Holdings, Inc. (CHHE)
lisdexamfetamine di	Mylan II B.V. (MYL)
lorbrena	PFIZER INC (PFE)
minocycline	NEXUS BIOPHARMA INC (NEXS)
multaq	Sanofi (SNY)
ONPATTRO	ALNYLAM PHARMACEUTICALS, INC. (ALNY)
opdivo qvantig	BRISTOL MYERS SQUIBB CO (BMY)
OXLUMO	ALNYLAM PHARMACEUTICALS, INC. (ALNY)
paclitaxel	Mylan II B.V. (MYL)
pemetrexed	DR REDDYS LABORATORIES LTD (RDY)
pemfexy	EAGLE PHARMACEUTICALS, INC. (EGRX)
portrazza	ELI LILLY & Co (LLY)
propafenone	Mylan II B.V. (MYL)
pylarify	PROGENICS PHARMACEUTICALS INC (PGNX)
PYLARIFY	Lantheus Holdings, Inc. (LNTH)
rivfloza	Novo Nordisk A/S (NVO)
Roxithromycin Dispersible Tablets	CHINA PHARMA HOLDINGS, INC. (CPHI)
tembexa	Emergent BioSolutions Inc. (EBS)
tpoxx	SIGA TECHNOLOGIES INC (SIGA)
Triamcinolone Acetonide and Neomycin Paste	China Health Industries Holdings, Inc. (CHHE)
Ultomiris	Xencor Inc (XNCR)
venetoclax	DR REDDYS LABORATORIES LTD (RDY)
vigiv cnj-016	Emergent BioSolutions Inc. (EBS)
vizimpro	PFIZER INC (PFE)
voraxaze	CAMBELL INTERNATIONAL HOLDING CORP. (BITMIS)
Zenocutuzumab (Zeno) / BIZENGRI® (zenocutuzumab-zbco)	Merus N.V. (MRUS)
Zepzelca	Jazz Pharmaceuticals plc (JAZZ)

Phase 3(229)

Drug	Company
(osimertinib cohort	ASTRAZENECA PLC (AZN)
[177Lu]Lu-DOTA-TATE	Novartis AG (NVS)
177lu-psma-617	ENDOCYTE INC (ECYT)
abp 234	AMGEN INC (AMGN)
acasunlimab	Genmab A/S (GMAB)
Adagrasib	ENANTA PHARMACEUTICALS INC (ENTA)
aglatimagene besadenovec	Candel Therapeutics, Inc. (CADL)
ak112	Summit Therapeutics Inc. (SMMT)
AK112 Injection	Summit Therapeutics Inc. (SMMT)
Alectinib	Nuvalent, Inc. (NUVL)
amivantamab	GH Research PLC (GHRS)
amivantamab	GH Research PLC (GHRS)
Amivantamab	Merus N.V. (MRUS)
amivantamab sc	GH Research PLC (GHRS)
Amrubicin	Merus N.V. (MRUS)
Amrubicin	Merck & Co., Inc. (MRK)
apitegromab	Scholar Rock Holding Corp (SRRK)
APL-3007, pegcetacoplan	Apellis Pharmaceuticals, Inc. (APLS)
aumolertinib	EQRx, Inc. (EQRX)
autologous	ASTRAZENECA PLC (AZN)
avutometinib	Verastem, Inc. (VSTM)
azacytidine	Merus N.V. (MRUS)
azd0171	ASTRAZENECA PLC (AZN)
azd0240	ASTRAZENECA PLC (AZN)
AZD2936	ASTRAZENECA PLC (AZN)
AZD8205 and AZD5305 and AZD2936	ASTRAZENECA PLC (AZN)
azd9291	ASTRAZENECA PLC (AZN)
azd9291 80 mg/40 mg	ASTRAZENECA PLC (AZN)
belumosudil	Sanofi (SNY)
Belumosudil	Sanofi (SNY)
Bendamustine	ENANTA PHARMACEUTICALS INC (ENTA)
bgb-15025	BeOne Medicines Ltd. (ONC)
BGB-15025	BeOne Medicines Ltd. (ONC)
BGB-16673	ENANTA PHARMACEUTICALS INC (ENTA)
BGB-16673	Merus N.V. (MRUS)
bgb-a445	BeOne Medicines Ltd. (ONC)
BGB-A445	BeOne Medicines Ltd. (ONC)
BNT116	BioNTech SE (BNTX)
BNT316	BioNTech SE (BNTX)
BNT326	BioNTech SE (BNTX)
BNT327	BioNTech SE (BNTX)
Bortezomib	Sanofi (SNY)
Calderasib	Merck & Co., Inc. (MRK)
CAN-2409	Candel Therapeutics, Inc. (CADL)
canakinumab	Novartis AG (NVS)
capmatinib	GH Research PLC (GHRS)
cardamyst	Milestone Pharmaceuticals Inc. (MIST)
carfilzomib	Sanofi (SNY)
cemdisiran	REGENERON PHARMACEUTICALS, INC. (REGN)
Cemiplimab	ENANTA PHARMACEUTICALS INC (ENTA)
Ceralasertib	ENANTA PHARMACEUTICALS INC (ENTA)
Ceralasertib	ASTRAZENECA PLC (AZN)
Ceralasertib	Crinetics Pharmaceuticals, Inc. (CRNX)
Cetuximab	ENANTA PHARMACEUTICALS INC (ENTA)
Cetuximab Sarotalocan Sodium	FATE THERAPEUTICS INC (FATE)
clobetasol	GH Research PLC (GHRS)
cobolimab	ANAPTYSBIO, INC (ANAB)
Crizotinib	BRISTOL MYERS SQUIBB CO (BMY)
Crizotinib	Nuvation Bio Inc. (NUVB)
custirsen	ACHIEVE LIFE SCIENCES, INC. (ACHV)
daratumumab sc	GH Research PLC (GHRS)
Dato-DXd	ASTRAZENECA PLC (AZN)
datopotamab deruxtecan	ASTRAZENECA PLC (AZN)
Datopotamab Deruxtecan	Merus N.V. (MRUS)
disitamab vedotin	PFIZER INC (PFE)
Divarasib	ENANTA PHARMACEUTICALS INC (ENTA)
Docetetaxel	Merck & Co., Inc. (MRK)
domvanalimab	GILEAD SCIENCES, INC. (GILD)
Domvanalimab	ASTRAZENECA PLC (AZN)
Dostarlimab	ANAPTYSBIO, INC (ANAB)
Dostarlimab and TSR-022	ANAPTYSBIO, INC (ANAB)
drug	ImmunityBio, Inc. (IBRX)
eftilagimod alfa	Immutep Limited (IMMP)
eftilagimod alfa	IMMUTEP Ltd (PRRUF)
Eftilagimod Alfa	Immutep Limited (IMMP)
egfr-tki inhibitor based on investigator's choice	ArriVent BioPharma, Inc. (AVBP)
elotuzumab	GH Research PLC (GHRS)
Ensartinib	Merus N.V. (MRUS)
Ensartinib	ENANTA PHARMACEUTICALS INC (ENTA)
Entrectinib	Merus N.V. (MRUS)
Erlotinib	Merus N.V. (MRUS)
Erlotinib	Amneal Pharmaceuticals, Inc. (AMRX)
Erlotinib	ENANTA PHARMACEUTICALS INC (ENTA)
erlotinib 150/100 mg	ASTRAZENECA PLC (AZN)
Erlotinib Hydrochloride	Amneal Pharmaceuticals, Inc. (AMRX)
etoposide	Black Diamond Therapeutics, Inc. (BDTX)
Etoposide	ADMA BIOLOGICS, INC. (ADMA)
Etoposide	BioNTech SE (BNTX)
ETOPOSIDE - Study	Design Therapeutics, Inc. (DSGN)
ETOPOSIDE - Usual	Design Therapeutics, Inc. (DSGN)
Etoposide Injection	ASTRAZENECA PLC (AZN)
Etoposide phosphate	Black Diamond Therapeutics, Inc. (BDTX)
firmonertinib	ArriVent BioPharma, Inc. (AVBP)
Firmonertinib	Merus N.V. (MRUS)
Firmonertinib	Relay Therapeutics, Inc. (RLAY)
Firmonertinib	ADMA BIOLOGICS, INC. (ADMA)
FOLFIRI	IGM Biosciences, Inc. (IGMS)
FOLFIRI-HD	IGM Biosciences, Inc. (IGMS)
FOLFIRI+cetuximab	IGM Biosciences, Inc. (IGMS)
FOLFOX6/FOLFOX7	IGM Biosciences, Inc. (IGMS)
Four week alternating FOLFOX and FOLFIRI	IGM Biosciences, Inc. (IGMS)
furmonertinib	ArriVent BioPharma, Inc. (AVBP)
geo-mva	GeoVax Labs, Inc. (GOVX)
gotistobart	Onconetix, Inc. (ONCO)
Gotistobart	BioNTech SE (BNTX)
HER3-DXd	Merck & Co., Inc. (MRK)
HRS-4357 injection	KYNTRA BIO INC. (KYNB)
I-DXd	Merck & Co., Inc. (MRK)
Idelalisib	ENANTA PHARMACEUTICALS INC (ENTA)
Immune Checkpoint Inhibitor	Merus N.V. (MRUS)
Immune induction therapy	Merus N.V. (MRUS)
Inavolisib	ENANTA PHARMACEUTICALS INC (ENTA)
Intismeran autogene	Merus N.V. (MRUS)
Intismeran autogene	Merck & Co., Inc. (MRK)
isatuximab iv	Sanofi (SNY)
isatuximab sc	Sanofi (SNY)
ivonescimab	Summit Therapeutics Inc. (SMMT)
ivonescimab + ligufalimab	Summit Therapeutics Inc. (SMMT)
Ivonescimab Injection	Summit Therapeutics Inc. (SMMT)
JDQ443	Novartis AG (NVS)
l-leucovorin	Merus N.V. (MRUS)
Lazertinib	Merus N.V. (MRUS)
lbl-007	BeOne Medicines Ltd. (ONC)
LBL-007	BeOne Medicines Ltd. (ONC)
Lenvatinib	Merck & Co., Inc. (MRK)
lnp023	Novartis AG (NVS)
lnp023	Novartis AG (NVS)
Lurbinectedin	Crinetics Pharmaceuticals, Inc. (CRNX)
Lurbinectedin	Merus N.V. (MRUS)
Lurbinectedin	Merck & Co., Inc. (MRK)
MEDI4736+Tremelimumab	ASTRAZENECA PLC (AZN)
MEDI5752	ASTRAZENECA PLC (AZN)
minocycline	GH Research PLC (GHRS)
MK-0482	Merck & Co., Inc. (MRK)
MK-3475	Merck & Co., Inc. (MRK)
MK-4830	Merck & Co., Inc. (MRK)
N-803 + Avelumab	ImmunityBio, Inc. (IBRX)
N-803 + Avelumab + PD-L1 t-haNK	ImmunityBio, Inc. (IBRX)
Nelistotug	iTeos Therapeutics, Inc. (ITOS)
nomacopan	Akari Therapeutics Plc (AKTX)
norditropin	Novo Nordisk A/S (NVO)
nPulse Cardiac Catheter System	Pulse Biosciences Inc Common Stock (DE) (PLSE)
nvl-655	Nuvalent, Inc. (NUVL)
Obinutuzumab	ASTRAZENECA PLC (AZN)
ociperlimab	BeOne Medicines Ltd. (ONC)
ociperlimab	BeOne Medicines Ltd. (ONC)
olafertinib	Checkpoint Therapeutics, Inc. (CKPT)
Oleclumab	ASTRAZENECA PLC (AZN)
open-label azd9291 80 mg/40 mg	ASTRAZENECA PLC (AZN)
osimertinib	GH Research PLC (GHRS)
Osimertinib	Amneal Pharmaceuticals, Inc. (AMRX)
Osimertinib	Merus N.V. (MRUS)
Osimertinib + Savolitinib	ASTRAZENECA PLC (AZN)
osimertinib 80 mg/40 mg	ASTRAZENECA PLC (AZN)
Panitumumab	IGM Biosciences, Inc. (IGMS)
part a - azd9291 in combination with continuous selumetinib	ASTRAZENECA PLC (AZN)
part a - azd9291 in combination with medi4736	ASTRAZENECA PLC (AZN)
part b - azd9291 in combination with medi4736	ASTRAZENECA PLC (AZN)
part b - azd9291 in combination with selumetinib	ASTRAZENECA PLC (AZN)
Pegcetacoplan	Apellis Pharmaceuticals, Inc. (APLS)
pemetrexed	GILEAD SCIENCES, INC. (GILD)
pemetrexed	BeOne Medicines Ltd. (ONC)
pemetrexed	Incyte Corp. (INCY)
Pemetrexed	ELI LILLY & Co (LLY)
Pemetrexed	BRISTOL MYERS SQUIBB CO (BMY)
Pemetrexed	Merck & Co., Inc. (MRK)
Pemetrexed	ENANTA PHARMACEUTICALS INC (ENTA)
Pemetrexed Disodium	ENANTA PHARMACEUTICALS INC (ENTA)
Pemetrexed Disodium	Merus N.V. (MRUS)
Pemetrexed Disodium	ADMA BIOLOGICS, INC. (ADMA)
platinum chemotherapy	BridgeBio Oncology Therapeutics, Inc. (BBOT)
platinum-based chemotherapy	ArriVent BioPharma, Inc. (AVBP)
Plinabulin	BeyondSpring Inc. (BYSI)
Pralsetinib	Merus N.V. (MRUS)
ramucirumab	GH Research PLC (GHRS)
Ramucirumab	ASTRAZENECA PLC (AZN)
ravulizumab	REGENERON PHARMACEUTICALS, INC. (REGN)
regn2810/chemo/ipi	REGENERON PHARMACEUTICALS, INC. (REGN)
Repotrectinib	BRISTOL MYERS SQUIBB CO (BMY)
Rescue Medication	Merck & Co., Inc. (MRK)
Rescue Medications	Merck & Co., Inc. (MRK)
Rilvegostomig	ASTRAZENECA PLC (AZN)
Rucaparib	Merck & Co., Inc. (MRK)
Sacituzumab tirumotecan	Merus N.V. (MRUS)
Sacituzumab tirumotecan	Merck & Co., Inc. (MRK)
savolitinib	HUTCHMED (China) Limited (HCM)
savolitinib + osimertinib	HUTCHMED (China) Limited (HCM)
Selpercatinib	ELI LILLY & Co (LLY)
Sonrotoclax	ENANTA PHARMACEUTICALS INC (ENTA)
sotorasib	REVOLUTION MEDICINES, INC. (RVMD)
Supportive care measures	Merck & Co., Inc. (MRK)
Surovatamig	ASTRAZENECA PLC (AZN)
t-dxd	ASTRAZENECA PLC (AZN)
tak-676	Takeda Pharmaceutical Company Limited American Depositary Shares (each representing 1/2 of a share of Common Stock) (TAK)
tak-788	Takeda Pharmaceutical Company Limited American Depositary Shares (each representing 1/2 of a share of Common Stock) (TAK)
tak-788	TAKEDA PHARMACEUTICAL CO LTD (TKPHF)
Taletrectinib	Nuvation Bio Inc. (NUVB)
Telisotuzumab Adizutecan	AbbVie Inc. (ABBV)
Telisotuzumab vedotin	AbbVie Inc. (ABBV)
tepotinib	GH Research PLC (GHRS)
Tocilizumab	ENANTA PHARMACEUTICALS INC (ENTA)
Topotecan	Merus N.V. (MRUS)
Topotecan	Crinetics Pharmaceuticals, Inc. (CRNX)
Topotecan	Merck & Co., Inc. (MRK)
trametinib	Deciphera Pharmaceuticals, Inc. (DCPH)
tremelimumab	GH Research PLC (GHRS)
Tremelimumab	ASTRAZENECA PLC (AZN)
trilaciclib	G1 Therapeutics, Inc. (GTHX)
tsr-042	TESARO, Inc. (TSRO)
Tyrosine kinase Inhibitors	ENANTA PHARMACEUTICALS INC (ENTA)
uft	ASTRAZENECA PLC (AZN)
V940	Merck & Co., Inc. (MRK)
valacyclovir	Candel Therapeutics, Inc. (CADL)
Venetoclax	ENANTA PHARMACEUTICALS INC (ENTA)
Venetoclax	ASTRAZENECA PLC (AZN)
venetoclax 10 mg oral tablet [venclexta]	GH Research PLC (GHRS)
venetoclax 100 mg oral tablet [venclexta]	GH Research PLC (GHRS)
venetoclax 50 mg oral tablet [venclexta]	GH Research PLC (GHRS)
Vibostolimab	Merck & Co., Inc. (MRK)
vinorelbine	ASTRAZENECA PLC (AZN)
vinorelbine	BRISTOL MYERS SQUIBB CO (BMY)
vinorelbine	MAIA Biotechnology, Inc. (MAIA)
Vinorelbine Tartrate	ENANTA PHARMACEUTICALS INC (ENTA)
virtue sab	Orchestra BioMed Holdings Inc. (OBIO)
Volrustomig	ASTRAZENECA PLC (AZN)
zimberelimab	GILEAD SCIENCES, INC. (GILD)
Zipalertinib (CLN-081/TAS6417)	Cullinan Therapeutics, Inc. (CGEM)
ZL-1310	Merus N.V. (MRUS)
Zongertinib	ENANTA PHARMACEUTICALS INC (ENTA)

Phase 2(167)

Drug	Company
6-thio-2'-deoxyguanosine	MAIA Biotechnology, Inc. (MAIA)
AB-106	Nuvation Bio Inc. (NUVB)
ABBV-706	AbbVie Inc. (ABBV)
ABT-869	AbbVie Inc. (ABBV)
ABT-869 .25 mg/kg	AbbVie Inc. (ABBV)
ABT-869 0.10 mg/kg	AbbVie Inc. (ABBV)
ach-4471	ACHILLION PHARMACEUTICALS INC (ACHN)
Alectinib	Merus N.V. (MRUS)
alisertib	PUMA BIOTECHNOLOGY, INC. (PBYI)
alk202	SAB BIOTHERAPEUTICS, INC. (SABS)
ALLO-501A	Allogene Therapeutics, Inc. (ALLO)
ALLO-647	Allogene Therapeutics, Inc. (ALLO)
am0010	ARMO BIOSCIENCES, INC. (ARMO)
amivantamab	ASTRAZENECA PLC (AZN)
Amivantamab	Structure Therapeutics Inc. (GPCR)
Amivantamab and Recombinant Human Hyaluronidase	Structure Therapeutics Inc. (GPCR)
Amivantamab IV	Bausch Health Companies Inc. (BHC)
Amivantamab IV	Structure Therapeutics Inc. (GPCR)
Amivantamab SC	Structure Therapeutics Inc. (GPCR)
Amivantamab SC	Bausch Health Companies Inc. (BHC)
anti-cd20 car-t	CELLULAR BIOMEDICINE GROUP, INC. (CMBG)
anti-pd-1/l1	HUTCHMED (China) Limited (HCM)
argx-119 iv	ARGENX SE (ARGX)
azd2811	ASTRAZENECA PLC (AZN)
BDTX-1535	Black Diamond Therapeutics, Inc. (BDTX)
bnt116	REGENERON PHARMACEUTICALS, INC. (REGN)
BNT327 Dose Level 1	BioNTech SE (BNTX)
BNT327 Dose Level 2	BioNTech SE (BNTX)
Boserolimab	Merus N.V. (MRUS)
Boserolimab	Merck & Co., Inc. (MRK)
bruton's tyrosine kinase inhibitor	GH Research PLC (GHRS)
canakinumab	Novartis AG (NVS)
capmatinib	Novartis AG (NVS)
capmatinib	Novartis AG (NVS)
CAR BCMA-CD70-T cells	Merus N.V. (MRUS)
CAR BCMA-CD70-T cells	Filana Therapeutics Inc. (FLNA)
Cediranib	ASTRAZENECA PLC (AZN)
cemiplimab	MAIA Biotechnology, Inc. (MAIA)
cemiplimab	Sanofi (SNY)
Cemiplimab	BioNTech SE (BNTX)
Cemiplimab	Assertio Holdings, Inc. (ASRT)
Cemiplimab	Merus N.V. (MRUS)
Cemiplimab	FATE THERAPEUTICS INC (FATE)
Cemiplimab 350 mg IV	Merus N.V. (MRUS)
ceralasertib	GH Research PLC (GHRS)
chlorhexidine	GH Research PLC (GHRS)
clindamycin	GH Research PLC (GHRS)
Clobetasol	Bausch Health Companies Inc. (BHC)
Cobimetinib	Merus N.V. (MRUS)
concurrent chemo/radiation therapy	Innovation Pharmaceuticals Inc. (IPIX)
concurrent chemo/radiation therapy	JOHNSON & JOHNSON (JNJ)
Crizotinib	Amneal Pharmaceuticals, Inc. (AMRX)
ct053ptsa	SUNSHINE BIOPHARMA INC. (SBFM)
cylembio	IO Biotech, Inc. (IOBT)
Diclofenac Potassium	ENANTA PHARMACEUTICALS INC (ENTA)
diphenhydramine	Sanofi (SNYNF)
direct oral anticoagulant	GH Research PLC (GHRS)
Divarasib	Merus N.V. (MRUS)
Doxycycline	Bausch Health Companies Inc. (BHC)
dzd8586	NYMOX PHARMACEUTICAL CORP (NYMXF)
Ensartinib	ADMA BIOLOGICS, INC. (ADMA)
env 105	Kairos Pharma, LTD. (KAPA)
EOS-448	iTeos Therapeutics, Inc. (ITOS)
erlotinib	CG Oncology, Inc. (CGON)
Etoposide	AbbVie Inc. (ABBV)
Etoposide	Merck & Co., Inc. (MRK)
etripamil ns	Milestone Pharmaceuticals Inc. (MIST)
etrumadenant	Arcus Biosciences, Inc. (RCUS)
Etrumadenant	Arcus Biosciences, Inc. (RCUS)
fianlimab	REGENERON PHARMACEUTICALS, INC. (REGN)
FOLFOX	ENANTA PHARMACEUTICALS INC (ENTA)
fs118	F-star Therapeutics, Inc. (FSTX)
HER3-DXd	Merus N.V. (MRUS)
Ibrutinib	Crinetics Pharmaceuticals, Inc. (CRNX)
Ibrutinib	ENANTA PHARMACEUTICALS INC (ENTA)
Ifinatamab Deruxtecan	Merus N.V. (MRUS)
ifosfamide	Black Diamond Therapeutics, Inc. (BDTX)
IGM-2644	IGM Biosciences, Inc. (IGMS)
Immune Checkpoint Inhibitors	ENANTA PHARMACEUTICALS INC (ENTA)
inupadenant	iTeos Therapeutics, Inc. (ITOS)
inupadenant (EOS-850)	iTeos Therapeutics, Inc. (ITOS)
isatuximab	Sanofi (SNY)
Isatuximab	Sanofi (SNY)
isatuximab sc-obds	Sanofi (SNY)
ivonescimab	GH Research PLC (GHRS)
jdq443	Novartis AG (NVS)
JNJ-90301900	Merus N.V. (MRUS)
Lazertinib	Bausch Health Companies Inc. (BHC)
Lazertinib	Structure Therapeutics Inc. (GPCR)
Livmoniplimab	AbbVie Inc. (ABBV)
ln-145	IOVANCE BIOTHERAPEUTICS, INC. (IOVA)
Lorigerlimab	MACROGENICS INC (MGNX)
Lurbinectedin	Jazz Pharmaceuticals plc (JAZZ)
Lurbinectedin	AbbVie Inc. (ABBV)
MCLA-129	Merus N.V. (MRUS)
mfolfirinox	BridgeBio Oncology Therapeutics, Inc. (BBOT)
mFOLFOX6	BridgeBio Oncology Therapeutics, Inc. (BBOT)
MGC018	MACROGENICS INC (MGNX)
montelukast	GH Research PLC (GHRS)
montelukast	Sanofi (SNY)
Montelukast	Sanofi (SNY)
N-803	CG Oncology, Inc. (CGON)
NALIRIFOX	Merus N.V. (MRUS)
nv-387	NANOVIRICIDES, INC. (NNVC)
Olaparib	Merus N.V. (MRUS)
olvimulogene nanivacirepvec	GENELUX Corp (GNLX)
oms906	OMEROS CORP (OMER)
OMS906	Xencor Inc (XNCR)
part a - azd9291 in combination with azd6094	ASTRAZENECA PLC (AZN)
part b - azd9291 in combination with azd6094	ASTRAZENECA PLC (AZN)
part c - azd9291 in combination with azd6094	ASTRAZENECA PLC (AZN)
part d - azd9291 in combination with azd6094	ASTRAZENECA PLC (AZN)
Patritumab Deruxtecan	Merus N.V. (MRUS)
Pemetrexed	Amneal Pharmaceuticals, Inc. (AMRX)
Pemetrexed	Merus N.V. (MRUS)
Pemetrexed	Arcus Biosciences, Inc. (RCUS)
Pemetrexed	iTeos Therapeutics, Inc. (ITOS)
Pemetrexed Disodium for Injection	Merus N.V. (MRUS)
pivekimab sunirine	ImmunoGen, Inc. (IMGN)
platinum compound	GH Research PLC (GHRS)
platinum doublet	REGENERON PHARMACEUTICALS, INC. (REGN)
platinum-based doublet	GILEAD SCIENCES, INC. (GILD)
poziotinib	Assertio Holdings, Inc. (ASRT)
propranolol	GH Research PLC (GHRS)
Propranolol	Bausch Health Companies Inc. (BHC)
quemliclustat	GILEAD SCIENCES, INC. (GILD)
Raludotatug Deruxtecan	Merck & Co., Inc. (MRK)
Ramucirumab	ELI LILLY & Co (LLY)
REC-4539	RECURSION PHARMACEUTICALS, INC. (RXRX)
regn7075	REGENERON PHARMACEUTICALS, INC. (REGN)
reqorsa	Genprex, Inc. (GNPX)
rmc-4630	REVOLUTION MEDICINES, INC. (RVMD)
RP1	ENANTA PHARMACEUTICALS INC (ENTA)
rtx-224	Rubius Therapeutics, Inc. (RUBY)
rucosopasem manganese	Galera Therapeutics, Inc. (GRTX)
Sapanisertib (CB-228, formerly TAK-228)	Calithera Biosciences, Inc. (CALA)
sar446523	Sanofi (SNYNF)
sarilumab	REGENERON PHARMACEUTICALS, INC. (REGN)
saruparib	GH Research PLC (GHRS)
SBRT	Merus N.V. (MRUS)
Serplulimab	Merus N.V. (MRUS)
smallpox	SIGA TECHNOLOGIES INC (SIGA)
stenoparib	Allarity Therapeutics, Inc. (ALLR)
Tagraxofusp	AbbVie Inc. (ABBV)
Tecovirimat	UNITED THERAPEUTICS Corp (UTHR)
temsirolimus	Black Diamond Therapeutics, Inc. (BDTX)
timolol	GH Research PLC (GHRS)
Timolol	Bausch Health Companies Inc. (BHC)
tislelizumab	Novartis AG (NVS)
tislelizumab	Novartis AG (NVS)
Topotecan	BioNTech SE (BNTX)
Tremelimumab	ADMA BIOLOGICS, INC. (ADMA)
tusamitamab ravtansine	Sanofi (SNY)
ubamatamab	REGENERON PHARMACEUTICALS, INC. (REGN)
V940	Merus N.V. (MRUS)
Vemurafenib	Merus N.V. (MRUS)
Vinorelbine	ELI LILLY & Co (LLY)
Vinorelbine	ENANTA PHARMACEUTICALS INC (ENTA)
vintafolide	ENDOCYTE INC (ECYT)
vs-7375	Verastem, Inc. (VSTM)
xh-s003	INFINITY PHARMACEUTICALS, INC. (INFI)
xh-s003	RA PHARMACEUTICALS, INC. (RARX)
zaltenibart	OMEROS CORP (OMER)
Zaltenibart (OMS906)	Xencor Inc (XNCR)
Zelenectide pevedotin	Merus N.V. (MRUS)
zelenectide pevedotin (formerly BT8009)	BICYCLE THERAPEUTICS PLC (BCYC)
zinc gluconate	GH Research PLC (GHRS)

Phase 1(146)

Drug	Company
[177lu]lu-dota-tate	Novartis AG (NVS)
[68Ga]Ga DOTA-5G and [177Lu]Lu DOTA-ABM-5G.	UNITED THERAPEUTICS Corp (UTHR)
[68ga]ga-dota-tate	Novartis AG (NVS)
111in-etn029	Novartis AG (NVS)
111in-etn029	NOVARTIS AG (NVSEF)
225ac-etn029	NOVARTIS AG (NVSEF)
225ac-etn029	Novartis AG (NVS)
AB248	AMGEN INC (AMGN)
ABT-263	AbbVie Inc. (ABBV)
ADCT-601	ADC Therapeutics SA (ADCT)
alk-inhibitor or ret-inhibitor	BioNTech SE (BNTX)
ALT-803	ENANTA PHARMACEUTICALS INC (ENTA)
ALX2004	ALX ONCOLOGY HOLDINGS INC (ALXO)
amg 436	AMGEN INC (AMGN)
amivantamab	GH Research PLC (GHRS)
amivantamab	GH Research PLC (GHRS)
anti-B7-H3 antibody conjugated to topoisomerase I inhibitor	BioNTech SE (BNTX)
anti-HER3 antibody conjugated to topoisomerase I inhibitor	BioNTech SE (BNTX)
anvumetostat	AMGEN INC (AMGN)
apg-1252	ASCENTAGE PHARMA GROUP INTERNATIONAL (AAPG)
AUTO6NG	Autolus Therapeutics plc (AUTL)
autologous genetically modified t cells	Adaptimmune Therapeutics PLC (ADAP)
avxs-101	AveXis, Inc. (AVXS)
azacytidine	ENANTA PHARMACEUTICALS INC (ENTA)
AZD2936	Merus N.V. (MRUS)
azirkitug	AbbVie Inc. (ABBV)
BBO-10203	BridgeBio Oncology Therapeutics, Inc. (BBOT)
bbo-11818	BridgeBio Oncology Therapeutics, Inc. (BBOT)
BBO-11818	Merus N.V. (MRUS)
BBO-11818	ENANTA PHARMACEUTICALS INC (ENTA)
BBO-11818	BridgeBio Pharma, Inc. (BBIO)
BBO-8520	BridgeBio Oncology Therapeutics, Inc. (BBOT)
bg-60366	BeOne Medicines Ltd. (BEIGF)
bg-60366	BeOne Medicines Ltd. (ONC)
BI 764532	Merus N.V. (MRUS)
bispecific antibody for pd-l1	BioNTech SE (BNTX)
Bispecific antibody for PD-L1 and VEGF-A	BioNTech SE (BNTX)
Budigalimab	AbbVie Inc. (ABBV)
C-TIL051	NEKTAR THERAPEUTICS (NKTR)
Capmatinib	Structure Therapeutics Inc. (GPCR)
cc8464	Pelthos Therapeutics Inc. (PTHS)
Cemiplimab	Merck & Co., Inc. (MRK)
cetrelimab	Innovation Pharmaceuticals Inc. (IPIX)
cetrelimab	JOHNSON & JOHNSON (JNJ)
cetuximab	REVOLUTION MEDICINES, INC. (RVMD)
cetuximab	BridgeBio Oncology Therapeutics, Inc. (BBOT)
Cetuximab	BridgeBio Pharma, Inc. (BBIO)
CFT8919	C4 Therapeutics, Inc. (CCCC)
Crizotinib	ENANTA PHARMACEUTICALS INC (ENTA)
CTX-8371	Compass Therapeutics, Inc. (CMPX)
Danvatirsen	Merus N.V. (MRUS)
Danvatirsen	ASTRAZENECA PLC (AZN)
daratumumab	GH Research PLC (GHRS)
daraxonrasib	REVOLUTION MEDICINES, INC. (RVMD)
deltacel	Kiromic Biopharma, Inc. (KRBP)
Digoxin	Merck & Co., Inc. (MRK)
EB-SELECT Single-Target CAR-NK Cells	Merus N.V. (MRUS)
ec1456	ENDOCYTE INC (ECYT)
elvn-002	Enliven Therapeutics, Inc. (ELVN)
enozertinib	Oric Pharmaceuticals, Inc. (ORIC)
Entinostat	Syndax Pharmaceuticals Inc (SNDX)
fhd-909	Foghorn Therapeutics Inc. (FHTX)
FOLFOX	BridgeBio Pharma, Inc. (BBIO)
FT836	FATE THERAPEUTICS INC (FATE)
GDC-1971	ENANTA PHARMACEUTICALS INC (ENTA)
GDC-6036	ENANTA PHARMACEUTICALS INC (ENTA)
gen-011	GENOCEA BIOSCIENCES, INC. (GNCA)
Gocatamig	Merus N.V. (MRUS)
H1299 Cell Lysates	CG Oncology, Inc. (CGON)
hdp-101	NYMOX PHARMACEUTICAL CORP (NYMXF)
hdp-101	Takeda Pharmaceutical Company Limited American Depositary Shares (each representing 1/2 of a share of Common Stock) (TAK)
honokiol	GH Research PLC (GHRS)
Iadademstat	ENANTA PHARMACEUTICALS INC (ENTA)
ide849	IDEAYA Biosciences, Inc. (IDYA)
IDE849 (SHR-4849)	IDEAYA Biosciences, Inc. (IDYA)
imgc936	ImmunoGen, Inc. (IMGN)
incb086550	Incyte Corp. (INCY)
investigator's treatment of choice	Genprex, Inc. (GNPX)
JANX008	Janux Therapeutics, Inc. (JANX)
jnj-86974680	Innovation Pharmaceuticals Inc. (IPIX)
jnj-86974680	JOHNSON & JOHNSON (JNJ)
JNJ-86974680	Janux Therapeutics, Inc. (JANX)
jnj-90301900	Innovation Pharmaceuticals Inc. (IPIX)
jnj-90301900	JOHNSON & JOHNSON (JNJ)
ko-2806	Kura Oncology, Inc. (KURA)
lazertinib	GH Research PLC (GHRS)
LB2102	Legend Biotech Corp (LEGN)
LN-145	IOVANCE BIOTHERAPEUTICS, INC. (IOVA)
LY4175408	ELI LILLY & Co (LLY)
MEDI5752	Merus N.V. (MRUS)
Midazolam	Merck & Co., Inc. (MRK)
MK-0482	Merus N.V. (MRUS)
MK-4830	Merus N.V. (MRUS)
mobocertinib	TAKEDA PHARMACEUTICAL CO LTD (TKPHF)
mobocertinib	Takeda Pharmaceutical Company Limited American Depositary Shares (each representing 1/2 of a share of Common Stock) (TAK)
nalirifox	BridgeBio Oncology Therapeutics, Inc. (BBOT)
NALIRIFOX	BridgeBio Pharma, Inc. (BBIO)
NALIRIFOX	ENANTA PHARMACEUTICALS INC (ENTA)
neo-pv-01	Neon Therapeutics, Inc. (NTGN)
nt-112	ASTRAZENECA PLC (AZN)
NVL-520	Nuvalent, Inc. (NUVL)
nxp900	Nuvectis Pharma, Inc. (NVCT)
Oleclumab	Merus N.V. (MRUS)
Olomorasib	ELI LILLY & Co (LLY)
osimertinib	BioNTech SE (BNTX)
osimertinib	Nuvectis Pharma, Inc. (NVCT)
Osimertinib	Jazz Pharmaceuticals plc (JAZZ)
part c - azd6094 monotherapy	ASTRAZENECA PLC (AZN)
Pemetrexed	ADMA BIOLOGICS, INC. (ADMA)
Pemetrexed	BridgeBio Pharma, Inc. (BBIO)
pf-08046054	PFIZER INC (PFE)
pf-08052666	PFIZER INC (PFE)
Platinum chemotherapy	BridgeBio Pharma, Inc. (BBIO)
plogosertib (plogo)	Bio Green Med Solution, Inc. (BGMSP)
ponsegromab	PFIZER INC (PFE)
Pozelimab	REGENERON PHARMACEUTICALS, INC. (REGN)
Pumitamig	Merus N.V. (MRUS)
QEQ278	Novartis AG (NVS)
quaratusugene ozeplasmid	Genprex, Inc. (GNPX)
ramucirumab	Genprex, Inc. (GNPX)
retifanlimab	Incyte Corp. (INCY)
rmc-5127	REVOLUTION MEDICINES, INC. (RVMD)
rmc-6236	REVOLUTION MEDICINES, INC. (RVMD)
rmc-6291	REVOLUTION MEDICINES, INC. (RVMD)
rmc-9805	REVOLUTION MEDICINES, INC. (RVMD)
Rucaparib	ENANTA PHARMACEUTICALS INC (ENTA)
S241656	IGM Biosciences, Inc. (IGMS)
sar408701	Sanofi (SNY)
sar439459	Sanofi (SNY)
sar442085	Sanofi (SNY)
sar446523	Sanofi (SNY)
sigvotatug vedotin	PFIZER INC (PFE)
tak-676	TAKEDA PHARMACEUTICAL CO LTD (TKPHF)
Tarlatamab	AMGEN INC (AMGN)
tas3351	CG Oncology, Inc. (CGON)
TNG260	Tango Therapeutics, Inc. (TNGX)
tno155	Novartis AG (NVS)
tno155 in combination with egf816	Novartis AG (NVS)
Tocilizumab	ADMA BIOLOGICS, INC. (ADMA)
Venetoclax	ADMA BIOLOGICS, INC. (ADMA)
Vibostolimab	Merus N.V. (MRUS)
xmt-2056	Mersana Therapeutics, Inc. (MRSN)
yl201	AMGEN INC (AMGN)
Zidesamtinib	Nuvalent, Inc. (NUVL)
zl-1310	AMGEN INC (AMGN)
zl-1310	Zai Lab Ltd (ZLAB)

Preclinical(26)

Drug	Company
225ac-psma-62	POINT Biopharma Global Inc. (PNT)
adxs-503	OS Therapies Inc (OSTX)
adxs-503	OLD AYALA, INC (AYLA)
ALPHA-0702	Alpha Cognition Inc. (ACOG)
ALPHA-0802	Alpha Cognition Inc. (ACOG)
ast-vac2	ASTERIAS BIOTHERAPEUTICS, INC. (AST)
ATNM-400	Actinium Pharmaceuticals, Inc. (ATNM)
BP1003	BIO-PATH HOLDINGS, INC. (BPTH)
chi3l1 bsabs	Ocean Biomedical, Inc. (OCEA)
chi3l1 mab	Ocean Biomedical, Inc. (OCEA)
CPI-935	Corvus Pharmaceuticals, Inc. (CRVS)
EO-1022	Elevation Oncology, Inc. (ELEV)
Fourth-Generation EGFR Inhibitor	Theseus Pharmaceuticals, Inc. (THRX)
fyarro + adagrasib	Whitehawk Therapeutics, Inc. (WHWK)
KRAS program	Cogent Biosciences, Inc. (COGT)
mink-215	MiNK Therapeutics, Inc. (INKT)
oncr-021	Oncorus, Inc. (ONCR)
oncr-788	Oncorus, Inc. (ONCR)
oral factor d inhibitors	ACHILLION PHARMACEUTICALS INC (ACHN)
Pan-mutant BRAF degrader program (proprietary)	Nurix Therapeutics, Inc. (NRIX)
Pan-mutant BRAF program (mutant BRAF degraders)	Nurix Therapeutics, Inc. (NRIX)
pnt2001	POINT Biopharma Global Inc. (PNT)
precision adcs	Prelude Therapeutics Inc (PRLD)
THE-349	Theseus Pharmaceuticals, Inc. (THRX)
til	CELLULAR BIOMEDICINE GROUP, INC. (CMBG)
ttx-sipdl1	Transcode Therapeutics, Inc. (RNAZ)

Unknown(9)

Drug	Company
ADXS-503	Ayala Pharmaceuticals, Inc. (ADXS)
bengay heat therapy	JOHNSON & JOHNSON (JNJ)
FitYourOutfit® (FYO) Body Composition System	BIOADAPTIVES, INC. (BDPT)
innovative production yield enhancement process	ADMA BIOLOGICS, INC. (ADMA)
Milkyway	AIBOTICS, INC. (AIBT)
NeuCovix-HT	AXIM BIOTECHNOLOGIES, INC. (AXIM)
neutrogena light therapy aging mask+	JOHNSON & JOHNSON (JNJ)
non-SGLT2 inhibitors	ENANTA PHARMACEUTICALS INC (ENTA)
vigiv	Emergent BioSolutions Inc. (EBS)

BLA Filed(2)

Drug	Company
gtx-104	Grace Therapeutics, Inc. (GRCE)
sl-401	STEMLINE THERAPEUTICS INC (STML)

Early Phase 1(1)

Drug	Company
VTP-600	Barinthus Biotherapeutics plc. (BRNS)

N/A(7)

Drug	Company
Crizotinib	Crinetics Pharmaceuticals, Inc. (CRNX)
Erlotinib	Crinetics Pharmaceuticals, Inc. (CRNX)
First-line antihypertensive single-pill combination	Merus N.V. (MRUS)
Pemetrexed Disodium	Amneal Pharmaceuticals, Inc. (AMRX)
Pemetrexed Disodium	Crinetics Pharmaceuticals, Inc. (CRNX)
Yishen Qutong Granules	Merus N.V. (MRUS)
Yishen Qutong Simulant Granules	Merus N.V. (MRUS)

Phase 1/Phase 2(51)

Drug	Company
[68Ga]Ga-DOTA-TATE	Novartis AG (NVS)
ABV-1519	ABVC BIOPHARMA, INC. (ABVC)
aln-cfb	REGENERON PHARMACEUTICALS, INC. (REGN)
amo959	Novartis AG (NVS)
AMO959	Novartis AG (NVS)
belantamab mafodotin	Sanofi (SNYNF)
belantamab mafodotin	Sanofi (SNY)
Cemiplimab	Sanofi (SNY)
cetuximab	Novartis AG (NVS)
cetuximab	Novartis AG (NVS)
Cetuximab	ELI LILLY & Co (LLY)
chemotherapy	Krystal Biotech, Inc. (KRYS)
cln-081	Cullinan Therapeutics, Inc. (CGEM)
diphenhydramine or equivalent	Sanofi (SNY)
dji136	NOVARTIS AG (NVSEF)
dji136	Novartis AG (NVS)
dzd6008	Takeda Pharmaceutical Company Limited American Depositary Shares (each representing 1/2 of a share of Common Stock) (TAK)
elironrasib	REVOLUTION MEDICINES, INC. (RVMD)
evorpacept	Sanofi (SNYNF)
evorpacept	Sanofi (SNY)
Gocatamig	Merck & Co., Inc. (MRK)
hpn328	Harpoon Therapeutics, Inc. (HARP)
ide397	AMGEN INC (AMGN)
ifinatamab deruxtecan	Merck & Co., Inc. (MRK)
inlexisertib	Deciphera Pharmaceuticals, Inc. (DCPH)
isatuximab sar650984	Sanofi (SNY)
isatuximab SAR650984	Sanofi (SNY)
kb707	Krystal Biotech, Inc. (KRYS)
loxo-292	ELI LILLY & Co (LLY)
LY3537982	ELI LILLY & Co (LLY)
m1774	GH Research PLC (GHRS)
montelukast or equivalent	Sanofi (SNY)
mRNA-1769	Moderna, Inc. (MRNA)
Neladalkib	Nuvalent, Inc. (NUVL)
opnurasib	Novartis AG (NVS)
opnurasib	NOVARTIS AG (NVSEF)
osimertinib	Takeda Pharmaceutical Company Limited American Depositary Shares (each representing 1/2 of a share of Common Stock) (TAK)
osimertinib	SUNSHINE BIOPHARMA INC. (SBFM)
osimertinib	Genprex, Inc. (GNPX)
pegenzileukin	Sanofi (SNY)
pegenzileukin	Sanofi (SNYNF)
pemetrexed	REVOLUTION MEDICINES, INC. (RVMD)
platinum-based chemotherapy	REGENERON PHARMACEUTICALS, INC. (REGN)
platinum-based chemotherapy	Genprex, Inc. (GNPX)
platinum-based doublet chemotherapy	REGENERON PHARMACEUTICALS, INC. (REGN)
REC-617	RECURSION PHARMACEUTICALS, INC. (RXRX)
sar439459	Sanofi (SNYNF)
tcr-t library	Alaunos Therapeutics, Inc. (TCRT)
TNG456	Tango Therapeutics, Inc. (TNGX)
tno155	Novartis AG (NVS)
wsd0922-fu	SUNSHINE BIOPHARMA INC. (SBFM)

Phase 2/Phase 3(11)

Drug	Company
CA-170	CURIS INC (CRIS)
eik1001	Eikon Therapeutics Inc. (EIKN)
IDE161	IDEAYA Biosciences, Inc. (IDYA)
iza-bren	BRISTOL MYERS SQUIBB CO (BMY)
nogapendekin alfa	GH Research PLC (GHRS)
osimertinib	AbbVie Inc. (ABBV)
Pemetrexed	AbbVie Inc. (ABBV)
Pemetrexed	BioNTech SE (BNTX)
screening platform	GH Research PLC (GHRS)
sitravatinib	Mirati Therapeutics, Inc. (MRTX)
surufatinib	HUTCHMED (China) Limited (HCM)

Phase 4(27)

Drug	Company
5-FU	Merus N.V. (MRUS)
Belumosudil mesylate	Sanofi (SNY)
bms-986012	BRISTOL MYERS SQUIBB CO (BMY)
bms-986489	BRISTOL MYERS SQUIBB CO (BMY)
BMS-986504	BRISTOL MYERS SQUIBB CO (BMY)
BMS-986525	BRISTOL MYERS SQUIBB CO (BMY)
Cetuximab	IGM Biosciences, Inc. (IGMS)
Chemotherapy	Merus N.V. (MRUS)
Diclofenac Potassium	Assertio Holdings, Inc. (ASRT)
eculizumab	ALEXION PHARMACEUTICALS, INC. (ALXN)
eculizumab	REGENERON PHARMACEUTICALS, INC. (REGN)
Enzalutamide；Abiraterone	KYNTRA BIO INC. (KYNB)
IBI363 + Chemotherapy	Merus N.V. (MRUS)
monalizumab	GH Research PLC (GHRS)
Monalizumab	ASTRAZENECA PLC (AZN)
Montelukast	Structure Therapeutics Inc. (GPCR)
Neoadjuvant olaparib	ASTRAZENECA PLC (AZN)
Olaparib	ASTRAZENECA PLC (AZN)
osimertinib	ASTRAZENECA PLC (AZN)
Osimertinib 80mg/40mg	ASTRAZENECA PLC (AZN)
Pemetrexed	ASTRAZENECA PLC (AZN)
Ravulizumab	ASTRAZENECA PLC (AZN)
Relatlimab	BRISTOL MYERS SQUIBB CO (BMY)
Single agent chemotherapy	Merus N.V. (MRUS)
SKB571 for injection	Merus N.V. (MRUS)
trametinib	Novartis AG (NVS)
Trametinib	Novartis AG (NVS)

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Frequently asked questions

How many drugs are in development for SMA?

BioSniper tracks 738 drugs in development for SMA across 186 companies.

How many clinical trials target SMA?

There are 4 clinical trials targeting SMA tracked by BioSniper.

What is the prevalence of SMA?

The estimated prevalence of SMA is approximately 75.0 per 100,000 population.

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