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pegcetacoplan

Generic: PEGCETACOPLAN·Brand: EMPAVELI, Empaveli, SYFOVRE, Syfovre

pegcetacoplan: developed by 1 company · 12 clinical trials tracked.

pegcetacoplan evidence translation

What we can confirm

What it means

Source-backed records connect pegcetacoplan to APLS; that link alone does not prove the drug works.

What to watch

Watch trial status, endpoints, and the next source-backed update.
BioSniper AIPage evidence connected

Prepared research question

How could pegcetacoplan → APLS affect its developer, and what evidence supports the link?

Run cited research

Traceable citations · Unknowns marked

See linked entities and source evidence8 indications · 1 study sponsors
Development Pipeline (4)
Clinical Trials (12)showing 10 most recent

US Early Access Program for the Treatment of Patients With C3 Glomerulopathy or Primary Immune-Complex Membranoproliferative Glomerulonephritis With Pegcetacoplan

Approved for marketing
Expanded AccessApellis Pharmaceuticals, Inc.

A Phase 3, Randomized, Placebo-Controlled, Double-Blinded, Multicenter Study to Evaluate the Efficacy and Safety of Pegcetacoplan in Adults at High Risk of Delayed Graft Function (DGF) Following Kidney Allograft Transplantation

NCT07020832·Phase 3·APLS
Suspended

Primary endpoint: Time to freedom from dialysis through Day 90

InterventionalRandomizedtriple320 targetStarted 2026-05Completion 2030-071 site · BrazilApellis Pharmaceuticals, Inc.

Safety, Tolerability, Pharmacokinetics, and Exploratory Efficacy of ABBV-6628 in Subjects With Geographic Atrophy Secondary to Age-Related Macular Degeneration

NCT07160179·Phase 1/Phase 2·ABBV
Recruiting

Primary endpoint: Number of Participants Experiencing Adverse Events

InterventionalRandomizedquadruple66 targetStarted 2025-08Completion 2029-105 sites · United StatesAbbVie

A Prospective, Multicenter, Open-Label, Observational Phase 4 Study to Evaluate Real-World Safety, Tolerability, and Treatment Patterns of Pegcetacoplan (Syfovre) in Patients With Geographic Atrophy Secondary to Age-Related Macular Degeneration

Active, not recruiting

Primary endpoint: Incidence of ocular AEs in treated eyes overall and according to physician-directed treatment interval based on US prescribing information

Observational300 targetStarted 2023-09Completion 2027-0634 sites · United StatesApellis Pharmaceuticals, Inc.

An Open-Label, Nonrandomized, Multicenter Extension Study to Evaluate the Long-term Safety and Efficacy of Pegcetacoplan in Patients With C3 Glomerulopathy or Immune-Complex Membranoproliferative Glomerulonephritis

NCT05809531·Phase 3·APLS
Active, not recruiting

Primary endpoint: Proportion of participants with a reduction in urine protein-to-creatinine ratio (uPCR) of at least 50% from the pretreatment value over time.

Interventionalopen100 targetStarted 2023-05Completion 2027-0747 sites · Argentina, Australia, Belgium, Brazil…Apellis Pharmaceuticals, Inc.

An Open-label, Single-arm, Multicenter Pilot Study to Evaluate the Pharmacokinetics, Pharmacodynamics, Efficacy and Safety of Pegcetacoplan in Patients With Transplant-associated Thrombotic Microangiopathy (TA-TMA) After Hematopoietic Stem Cell Transplantation (HSCT)

NCT05148299·Phase 2
Completed

Primary endpoint: Pegcetacoplan Pharmacokinetic (PK) Parameter Area Under the Curve Limited to the End of Dosing Interval (AUC0-tau)

Interventionalopen12 enrolledStarted 2022-02Completion 2024-1214 sites · France, Greece, Italy, Spain…Swedish Orphan Biovitrum

A Phase 3, Randomized, Placebo-Controlled, Double-Blinded, Multicenter Study to Evaluate the Efficacy and Safety of Pegcetacoplan in Patients With C3 Glomerulopathy or Immune-Complex Membranoproliferative Glomerulonephritis

NCT05067127·Phase 3·APLS
Completed

Primary endpoint: Randomized Controlled Period: Change From Baseline in Log-Transformed Urine Protein-to-Creatinine Ratio (uPCR) at Week 26

InterventionalRandomizedtriple124 enrolledStarted 2021-11Completion 2025-0150 sites · Argentina, Australia, Austria, Belgium…Apellis Pharmaceuticals, Inc.

An Open-Label, Randomized, Controlled, Phase 2 Study to Evaluate the Safety and Efficacy of Pegcetacoplan in the Treatment of Post-Transplant Recurrence of C3G or IC-MPGN

NCT04572854·Phase 2·APLS
Completed

Primary endpoint: Percentage of Subjects With Reduction in C3c Staining on Renal Biopsy at Week 12

InterventionalRandomizedopen13 enrolledStarted 2021-09Completion 2026-0125 sites · Argentina, Australia, Austria, Brazil…Apellis Pharmaceuticals, Inc.

A Phase 3, Open-Label, Multicenter, Extension Study to Evaluate the Long-Term Safety and Efficacy of Pegcetacoplan in Subjects With Geographic Atrophy Secondary to Age-Related Macular Degeneration

NCT04770545·Phase 3·APLS
Completed

Primary endpoint: Incidence and severity of ocular and systemic adverse events

Interventionalopen792 enrolledStarted 2021-03Completion 2025-0950 sites · United StatesApellis Pharmaceuticals, Inc.

An Open Label, Single-Arm, Phase 2 Study to Evaluate the Safety, Pharmacokinetics, and Biologic Activity of Pegcetacoplan in Pediatric Patients With Paroxysmal Nocturnal Hemoglobinuria

NCT04901936·Phase 2·APLS
Recruiting

Primary endpoint: Pegcetacoplan serum concentrations over the course of the 16-week treatment period

Interventionalopen12 targetStarted 2021-02Completion 2028-1212 sites · Czechia, France, Malaysia, Netherlands…Apellis Pharmaceuticals, Inc.

Frequently asked questions

Who is developing pegcetacoplan?

pegcetacoplan is being developed by Apellis Pharmaceuticals, Inc..

How many clinical trials involve pegcetacoplan?

BioSniper tracks 12 clinical trials involving pegcetacoplan.