DSGNNasdaq

Design Therapeutics, Inc.

Healthcare·Oncology·Commercial·Carlsbad, CA, United States
OncologyRare DiseaseNeurologyOphthalmologyInfectious DiseaseMetabolicRespiratoryDermatologyPsychiatry

Design Therapeutics, Inc. (DSGN): 17 pipeline candidates · 5 upcoming catalysts · ~39 mo cash runway · 14 clinical trials. Updated within the last hour.

10.0/10

BioSniper Score

5-factor signal · derived from public data

Cash Runway10.0

39.0 months

Financial Health9.9

D/E 0.06 · 0% dilution

Pipeline Maturity10.0

Lead: Approved

Pipeline Breadth10.0

17 candidates

Catalyst Momentum10.0

5 upcoming, next in ~132d

Insider SignalN/A

N/A

A transparent, data-derived signal for Design Therapeutics, Inc.across cash runway, pipeline maturity & breadth, catalyst momentum and clinical/regulatory footprint. Each factor traces to tracked public filings — not an investment recommendation.

Key Financials

Market Cap

$685.2M

Cash

$12.8M

Quarterly Burn

$16.4M

Runway

39.0 mo

Revenue

$0

Cash Runway vs Catalysts

Tracked catalysts land within the current projected cash runway.

Cash ends ~Sep 2029
Today~43 mo out
Catalyst within runway

Pipeline (17 candidates)

Showing 10 of 17 candidates. Sign up for full pipeline.

Upcoming Catalysts (5)

Institutional Holdings

Source: SEC Form 13F · as of Mar 2026

Institutional holders

120

Total value held

$267.2M

HolderSharesValue
ra capital management, l.p.2,972,973$31.6M
vanguard capital management llc2,699,700$28.7M
baker bros. advisors lp2,585,978$27.5M
blackrock, inc.2,133,764$22.7M
woodline partners lp1,923,002$20.5M
driehaus capital management llc1,744,987$18.6M
trails edge capital partners, lp852,013$9.1M
fmr llc798,411$8.5M
kynam capital management, lp784,606$8.3M
geode capital management, llc692,518$7.4M

Showing top 10 of 120 institutional holders of Design Therapeutics, Inc.. Sign up for the full 13F holder list and quarter-by-quarter ownership history.

14 clinical trials·CEO: Mr. Pratik Shah Ph.D.

Frequently asked questions

How many drug candidates are in Design Therapeutics, Inc.'s pipeline?

Design Therapeutics, Inc. (DSGN) has 17 pipeline candidates tracked by BioSniper across SEC filings and clinical trial registrations.

What is Design Therapeutics, Inc.'s lead drug candidate?

Design Therapeutics, Inc.'s most advanced tracked candidate is 9vHPV Vaccine plus BCG Vaccine Mix for percutaneous use (Phase 1) for HIV Infections.

What is Design Therapeutics, Inc.'s next catalyst?

Design Therapeutics, Inc.'s next tracked catalyst is a Phase3_Topline event — "Phase 3 Topline: Explore the Relationship Between Single Nucleotide Polymorphisms and Topotecan Response and Toxicity" — expected October 28, 2026.

What is Design Therapeutics, Inc.'s cash runway?

Based on its most recent reported cash balance and quarterly burn rate, Design Therapeutics, Inc. has approximately 39.0 months of cash runway.

What is Design Therapeutics, Inc.'s market capitalization?

Design Therapeutics, Inc.'s market capitalization is approximately $685.2M.

Get the full picture on Design Therapeutics, Inc.

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