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alpelisib

Generic: ALPELISIB·Brand: PIQRAY, Piqray, VIJOICE, Vijoice

alpelisib: developed by 1 company · 29 clinical trials tracked · 3 FDA decisions.

alpelisib evidence translation

What we can confirm

3 FDA records · 29 tracked trials

What it means

Source-backed records connect alpelisib to NVS; that link alone does not prove the drug works.

What to watch

Watch active trials and any change in FDA or trial status.
BioSniper AIPage evidence connected

Prepared research question

How could alpelisib → NVS affect its developer, and what evidence supports the link?

Run cited research

Traceable citations · Unknowns marked

See linked entities and source evidence8 indications · 7 study sponsors
Development Pipeline (2)
CompanyPhase
Novartis AG (NVS)
Advanced HER2+Breast Cancer; PIK3CA-Related Overgrowth Spect…
Phase 4
Novartis AG (NVS)Approved
Clinical Trials (29)showing 10 most recent

Managed Access Programs for BYL719, Alpelisib

Available
Expanded AccessNovartis Pharmaceuticals

An Open Label, Multi-center Alpelisib Roll-over Study to Assess Long-term Safety in Participants Who Have Completed a Novartis Sponsored Alpelisib (BYL719) Study and Are Judged by the Investigator to Benefit From Continued Treatment With Alpelisib.

NCT07679269·Phase 2·NVS
Not yet recruiting

Primary endpoint: Number of participants with Adverse Events (AEs) and Serious Adverse Events (SAEs)

Interventionalopen51 targetStarted 2027-01Completion 2031-07Novartis Pharmaceuticals

Study Assessing the Efficacy, Safety and Pharmacokinetics of Alpelisib in Pediatric and Adult Patients With PIK3CA-related Overgrowth Spectrum (PROS)

NCT06997588·Phase 2·NVS
Recruiting

Primary endpoint: Proportion of participants with a confirmed objective response by BIRC

Interventionalopen104 targetStarted 2025-10Completion 2030-0937 sites · Australia, Austria, Belgium, France…Novartis Pharmaceuticals

VATCH (Vascular Anomaly Analysis for Therapy Choice): Phase II Study of Alpelisib Treatment in Subjects With TIE2/PIK3CA Pathway Driven Vascular Anomalies

NCT07543822·Phase 2
Active, not recruiting

Primary endpoint: Percentage of subjects with a Substantial Response or Intermediate Response to Alpelisib using an Individualized Response Criteria

Interventionalopen61 targetStarted 2025-08Completion 2030-081 site · United StatesChildren's Hospital of Philadelphia

A Modular Open Label, Signal Seeking, Phase II Trial of Targeted Therapies for Patients With Slow-Flow or Fast-Flow Vascular Malformations (TARGET-VM)

NCT05983159·Phase 2
Recruiting

Primary endpoint: The number of participants who achieve or exceed a predetermined threshold of improvement in their most significant symptom at 48 weeks based on the Vascular Malformation Patient Specific Outcome Measure (VM-PSOM).

Interventionalopen50 targetStarted 2024-09Completion 2026-122 sites · AustraliaMurdoch Childrens Research Institute

A Two-stage Double-blind, Randomized, Placebo-controlled Study to Assess the Efficacy, Safety and Pharmacokinetics of Alpelisib in Pediatric and Adult Patients With Lymphatic Malformations Associated With a PIK3CA Mutation.

NCT05948943·Phase 2/Phase 3·NVS
Recruiting

Primary endpoint: Stage 2:Radiological response rate at Week 24 of Stage 2 (adult and pediatric (6 - 17 years of age) participants)

InterventionalRandomizedquadruple232 targetStarted 2023-11Completion 2033-0550 sites · Argentina, Australia, Belgium, Czechia…Novartis Pharmaceuticals

Molecular Analysis for Combination Therapy Choice (ComboMATCH)

NCT05564377·Phase 2·RLAY
Recruiting

Primary endpoint: Accrual of patients to ComboMATCH treatment trials

InterventionalRandomizedopen2,900 targetStarted 2023-04Completion 2030-0750 sites · United StatesNational Cancer Institute (NCI)

An Umbrella, Randomized, Controlled, Pre Operative Trial Testing Integrative Subtype Targeted Therapeutics in Estrogen Receptor Positive, HER2-Negative Breast Cancer

NCT05101564·Phase 2
Completed

Primary endpoint: Percentage Change in Ki67

InterventionalRandomizedopen19 enrolledStarted 2023-03Completion 2024-061 site · United StatesJennifer Lee Caswell-Jin

A Phase 1b/2, Open-Label Umbrella Study To Evaluate Safety And Efficacy Of Elacestrant In Various Combination In Patients With Metastatic Breast Cancer

NCT05563220·Phase 1/Phase 2·STML
Active, not recruiting

Primary endpoint: Number of Participants with DLTs Observed During the First Cycle

Interventionalopen435 targetStarted 2023-01Completion 2028-1250 sites · Argentina, Australia, Belgium, Brazil…Stemline Therapeutics, Inc.

Phase 3, Open-Label, Randomized, Study Comparing Gedatolisib Combined With Fulvestrant & With or Without Palbociclib to Standard-of-Care Therapies in Patients With HR-Positive, HER2-Negative Advanced Breast Cancer Previously Treated With a CDK4/6 Inhibitor in Combination w/Non-Steroidal Aromatase Inhibitor Therapy

NCT05501886·Phase 3·RLAY
Active, not recruiting

Primary endpoint: Progression Free Survival (PFS) in Patients with PIK3CA WT and PIK3CA MT Breast Cancer

InterventionalRandomizedopen701 targetStarted 2022-12Completion 2026-1250 sites · United StatesCelcuity Inc
FDA Decisions3 records
Approval(NVS)FDA ↗
NDA218466Type 3 - New Dosage FormOrphan DrugStandardOralGranule
Approval(NVS)FDA ↗
NDA215039Type 10 - New Indication Submitted as Distinct NDA - Not ConsolidatedOrphan DrugPriorityOralTablet
Approval(NVS)FDA ↗
NDA212526Type 1 - New Molecular EntityPriorityOralTablet

Frequently asked questions

Who is developing alpelisib?

alpelisib is being developed by Novartis AG.

How many clinical trials involve alpelisib?

BioSniper tracks 29 clinical trials involving alpelisib.

What is alpelisib's latest FDA decision?

The most recent tracked FDA decision for alpelisib is Approval, dated April 24, 2024.