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hydroxyurea

Generic: HYDROXYUREA·Brand: DROXIA, Droxia, HYDREA, HYDROXYUREA, Hydrea, SIKLOS, Siklos, XROMI, Xromi

hydroxyurea: 12 clinical trials tracked.

hydroxyurea evidence translation

What we can confirm

12 tracked trials

No verified listed developer

What it means

AI will separate confirmed drug evidence from unknown company context.

What to watch

Watch trial status, endpoints, and the next source-backed update.
BioSniper AIPage evidence connected

Prepared research question

What is verified about hydroxyurea, and what remains unknown?

Run cited research

Traceable citations · Unknowns marked

See linked entities and source evidence5 indications · 4 study sponsors
Clinical Trials (12)showing 10 most recent

Frontline Ziftomenib in NPM1-Mutated or KMT2A-Rearranged Acute Myeloid Leukemia in Patients Not Eligible for Intensive Induction or Other Therapy

NCT06930352·Phase 2
Recruiting

Primary endpoint: Complete remission (CR) plus CR/response with hematologic improvement

Interventionalopen70 targetStarted 2026-10Completion 2027-121 site · United StatesUma Borate

Haploidentical Donor Hematopoietic Cell Transplant for Sickle Cell Disease

NCT07616154·Phase 2·GHRS
Recruiting

Primary endpoint: GVHD-free and rejection free survival (GRFS)

Interventionalopen45 targetStarted 2026-09Completion 2035-091 site · United StatesSt. Jude Children's Research Hospital

CD83 CAR T in Relapsed or Refractory Acute Myeloid Leukemia (AML): A Phase I Trial

NCT06871410·Phase 1
Recruiting

Primary endpoint: Incidence of dose-limiting toxicity (DLT)

Interventionalopen26 targetStarted 2026-02Completion 2028-041 site · United StatesRoswell Park Cancer Institute

A Phase 3, Randomized, Double-blind, Active-Comparator-Controlled Clinical Study to Evaluate the Efficacy and Safety of Bomedemstat (MK-3543) Versus Hydroxyurea in Cytoreductive Therapy Naïve Essential Thrombocythemia Participants

NCT06456346·Phase 3
Active, not recruiting

Primary endpoint: Durable Clinicohematologic Response (DCHR) Rate

InterventionalRandomizeddouble300 targetStarted 2024-07Completion 2028-0350 sites · Argentina, Australia, Austria, Canada…Merck Sharp & Dohme LLC

BrUOG 419 - Promoting Utilization and Safety of Hydroxyurea Using Precision in Africa (PUSHUP)

NCT05285917·Phase 3
Recruiting

Primary endpoint: Rate of clinical, sickle cell adverse events (grade ≥ 3) as assessed by CTCAE v5.0

InterventionalRandomizedopen400 targetStarted 2023-11Completion 2027-091 site · AngolaBrown University

HU-F-AIM - A Prospective, Interventional Study to Evaluate HU-resistance in Polycythemia Vera Patients Who Meet Predictive Parameters Identified in the Machine Learning Project PV-AIM

NCT05853458·Phase 4·NVS
Terminated

Primary endpoint: Proportion of PV patients with HU-resistance/intolerance within 6-9 months after start of de novo HU- treatment in presence of the PV-AIM HU-resistance predictors at the start of HU treatment.

Interventionalopen76 enrolledStarted 2023-07Completion 2026-0221 sites · GermanyNovartis Pharmaceuticals

A Phase 2 Open-label Study to Evaluate the Activity of Etavopivat on Transcranial Doppler Velocities in Pediatric Patients With Sickle Cell Disease Who Are at Increased Risk for Primary Stroke

NCT05953584·Phase 2
Recruiting

Primary endpoint: Change in the highest TAMMV in any of the L/R internal carotid artery [ICA] and L/R middle cerebral artery [MCA], whichever is highest, as measured by TCD

Interventionalopen27 targetStarted 2023-06Completion 2027-099 sites · India, Nigeria, OmanForma Therapeutics, Inc.

Alternative Dosing And Prevention of Transfusions (ADAPT): A Prospective Study to Reduce Transfusion Requirements for Children With Sickle Cell Anemia Using Pharmacokinetics-based Hydroxyurea Dosing

NCT05662098·Early Phase 1
Active, not recruiting

Primary endpoint: To compare the rates of blood transfusions overall and by specific indications in children with sickle cell anaemia (SCA), prior to and during hydroxyurea treatment

Interventionalopen100 targetStarted 2022-06Completion 2027-121 site · UgandaChildren's Hospital Medical Center, Cincinnati

Hydroxyurea Therapy for Neurological and Cognitive Protection in Pediatric Sickle Cell Anemia in Uganda: A Single Arm Open Label Trial, "BRAIN SAFE II"

NCT04750707·Phase 3
Completed

Primary endpoint: The frequency, age specific prevalence and severity of Sickle Cell Vasculopathy manifested by New stroke as assessed by the Pediatric NIH Stroke Scale (PedNIHSS) over the 3-year study while on hydroxyurea treatment, compared to baseline assessments.

Interventionalopen270 enrolledStarted 2021-03Completion 2025-031 site · UgandaGlobal Health Uganda LTD

Open-label, Single-arm Trial to Evaluate Antitumor Activity, Safety, and Pharmacokinetics of Isatuximab Used in Combination With Chemotherapy in Pediatric Patients From 28 Days to Less Than 18 Years of Age With Relapsed/Refractory B or T Acute Lymphoblastic Leukemia or Acute Myeloid Leukemia in First or Second Relapse

NCT03860844·Phase 2·SNY
Terminated

Primary endpoint: Percentage of Participants With Complete Response (CR) Rate

Interventionalopen67 targetStarted 2019-08Completion 2023-0541 sites · Argentina, Brazil, Denmark, France…Sanofi