| INSMINSMED Inc | 1,500,000 | $245.3M |
| RVMDREVOLUTION MEDICINES, INC. | 1,500,000 | $145.9M |
| CYTKCYTOKINETICS INC | 1,600,000 | $105.5M |
| REGNREGENERON PHARMACEUTICALS, INC. | 85,000 | $65.7M |
| ROIVRoivant Sciences Ltd. | 2,000,000 | $55.4M |
| RYTMRHYTHM PHARMACEUTICALS, INC. | 600,000 | $52.2M |
| SRRKScholar Rock Holding Corp | 500,000 | $24.6M |
| BBIOBridgeBio Pharma, Inc. | 275,000 | $20.4M |
| ARWRARROWHEAD PHARMACEUTICALS, INC. | 300,000 | $18.8M |
| ORICOric Pharmaceuticals, Inc. | 1,400,000 | $17.7M |
| ALMSALUMIS INC. | 800,000 | $17.6M |
| QUREuniQure N.V. | 900,000 | $14.7M |
| GILDGILEAD SCIENCES, INC. | 100,000 | $13.9M |
| COGTCogent Biosciences, Inc. | 350,000 | $13.5M |
| DNTHDianthus Therapeutics, Inc. /DE/ | 150,000 | $12.6M |
| RGNXREGENXBIO Inc. | 1,500,000 | $12.6M |
| SLNOSOLENO THERAPEUTICS INC | 325,000 | $10.9M |
| IRONDisc Medicine, Inc. | 170,000 | $10.9M |
| NRIXNurix Therapeutics, Inc. | 700,000 | $10.8M |
| TNGXTango Therapeutics, Inc. | 450,000 | $9.4M |
| IONSIONIS PHARMACEUTICALS INC | 125,000 | $9.4M |
| SANASana Biotechnology, Inc. | 3,200,000 | $9.2M |
| BHVNBiohaven Ltd. | 1,000,000 | $8.5M |
| VKTXViking Therapeutics, Inc. | 250,000 | $8.1M |
| DFTXDefinium Therapeutics Inc. | 400,000 | $7.6M |
| BEAMBeam Therapeutics Inc. | 300,000 | $7.1M |
| RZLTRezolute, Inc. | 2,000,000 | $6.1M |
| CAPRCAPRICOR THERAPEUTICS, INC. | 200,000 | $6.1M |
| AXSMAxsome Therapeutics, Inc. | 35,000 | $5.9M |
| PTGXProtagonist Therapeutics, Inc | 50,000 | $5.3M |
| FBRXForte Biosciences, Inc. | 150,000 | $3.9M |
| LBRXLB PHARMACEUTICALS INC | 150,000 | $3.7M |
| SVRASavara Inc | 600,000 | $3.3M |
| RLMDRELMADA THERAPEUTICS, INC. | 450,000 | $3.1M |
| IMCRImmunocore Holdings plc | 100,000 | $3.0M |
| MAZEMaze Therapeutics, Inc. | 100,000 | $3.0M |
| TENXTENAX THERAPEUTICS, INC. | 167,000 | $2.7M |
| OLMAOlema Pharmaceuticals, Inc. | 150,000 | $2.2M |
| IVAInventiva S.A. | 400,000 | $2.2M |
| SIONSionna Therapeutics, Inc. | 50,000 | $2.0M |