PNH

Hematology·MeSH: Anemia

18 drugs in development·10 companies·3 clinical trials

Drug Pipeline by Phase

Approved(2)

Drug	Company
empaveli	KORU Medical Systems Inc. Common Stock (DE) (KRMD)
Ultomiris	Xencor Inc (XNCR)

Phase 3(8)

Drug	Company
alxn2040	ALEXION PHARMACEUTICALS, INC. (ALXN)
alxn2050	ALEXION PHARMACEUTICALS, INC. (ALXN)
APL-3007, pegcetacoplan	Apellis Pharmaceuticals, Inc. (APLS)
lnp023	Novartis AG (NVS)
nomacopan	Akari Therapeutics Plc (AKTX)
Pegcetacoplan	Apellis Pharmaceuticals, Inc. (APLS)
Pegcetacoplan (systemic)	Apellis Pharmaceuticals, Inc. (APLS)
Systemic pegcetacoplan	Apellis Pharmaceuticals, Inc. (APLS)

Phase 2(5)

Drug	Company
ach-4471	ACHILLION PHARMACEUTICALS INC (ACHN)
ach-5228	ALEXION PHARMACEUTICALS, INC. (ALXN)
OMS906	Xencor Inc (XNCR)
zaltenibart	OMEROS CORP (OMER)
Zaltenibart (OMS906)	Xencor Inc (XNCR)

Phase 1(1)

Drug	Company
xh-s003	RA PHARMACEUTICALS, INC. (RARX)

Preclinical(1)

Drug	Company
oral factor d inhibitors	ACHILLION PHARMACEUTICALS INC (ACHN)

Phase 1/Phase 2(1)

Drug	Company
aln-cfb	REGENERON PHARMACEUTICALS, INC. (REGN)

BioSniper tracks 18 drugs in development for PNH across 10 companies.

There are 3 clinical trials targeting PNH tracked by BioSniper.

Full trial data, competitive analysis, and AI-powered pipeline tracking.