Muscular Dystrophy

·MeSH: Muscular Dystrophies

Prevalence

0.5 / 100K

65 drugs in development·27 companies·3 clinical trials

Drug Pipeline by Phase

Phase 3(20)
DrugCompany
aoc 1044Avidity Biosciences, Inc. (RNAM)
aoc-1020Avidity Biosciences, Inc. (RNAM)
apitegromabScholar Rock Holding Corp (SRRK)
AtalurenPTC THERAPEUTICS, INC. (PTCT)
BBP-418BridgeBio Pharma, Inc. (BBIO)
casimersenSarepta Therapeutics, Inc. (SRPT)
duchenne muscular dystrophy"CAPRICOR THERAPEUTICS, INC. (CAPR)
edspQuince Therapeutics, Inc. (QNCX)
eteplirsenSarepta Therapeutics, Inc. (SRPT)
golodirsenSarepta Therapeutics, Inc. (SRPT)
losmapimodFulcrum Therapeutics, Inc. (FULC)
RGX-202REGENXBIO Inc. (RGNX)
srp-1001Sarepta Therapeutics, Inc. (SRPT)
srp-4045Sarepta Therapeutics, Inc. (SRPT)
srp-4053Sarepta Therapeutics, Inc. (SRPT)
srp-5051Sarepta Therapeutics, Inc. (SRPT)
SRP-9003 (LGMD2E/R4/bidridistrogene xeboparvovec)Sarepta Therapeutics, Inc. (SRPT)
zeleciment basivarsen (z-basivarsen)Dyne Therapeutics, Inc. (DYN)
zeleciment rostudirsenDyne Therapeutics, Inc. (DYN)
zeleciment rostudirsen (z-rostudirsen)Dyne Therapeutics, Inc. (DYN)
Preclinical(1)
DrugCompany
ck-089CYTOKINETICS INC (CYTK)
Early Phase 1(1)
DrugCompany
sat-3247Satellos Bioscience Inc. (MSLE)

Compare drugs

agamree vs AGAMREE®agamree vs amondys 45agamree vs deflazacort

Frequently asked questions

How many drugs are in development for Muscular Dystrophy?

BioSniper tracks 65 drugs in development for Muscular Dystrophy across 27 companies.

How many clinical trials target Muscular Dystrophy?

There are 3 clinical trials targeting Muscular Dystrophy tracked by BioSniper.

What is the prevalence of Muscular Dystrophy?

The estimated prevalence of Muscular Dystrophy is approximately 0.5 per 100,000 population.

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