Respiratory
5 drugs are in development for Cystic Fibrosis.
- Companies
- 4
- Clinical trials
- 39
BioSniper AIPage evidence connected
Prepared research question
Which programs lead the Cystic Fibrosis pipeline—and what evidence could change the picture?
Run cited research
Traceable citations · Unknowns marked
Drug Pipeline by Phase
Phase 2(5)
| Drug | Company |
|---|---|
| ARCT-032 | Arcturus Therapeutics Holdings Inc. (ARCT) |
| galicaftor | Sionna Therapeutics, Inc. (SION) |
| lti-05 | Rein Therapeutics, Inc. (RNTX) |
| mrt5005 | Translate Bio, Inc. (TBIO) |
| navocaftor | Sionna Therapeutics, Inc. (SION) |
About this indication
Cystic Fibrosis context
Respiratory·MeSH: Cystic Fibrosis (D003550)
Also known as: Mucoviscidosis
Incidence
3.5 / 100K/yr
Frequently asked questions
How many drugs are in development for Cystic Fibrosis?
BioSniper tracks 5 drugs in development for Cystic Fibrosis across 4 companies.
How many clinical trials target Cystic Fibrosis?
There are 39 clinical trials targeting Cystic Fibrosis tracked by BioSniper.