Acid Sphingomyelinase Deficiency

·MeSH: Niemann-Pick Diseases

Prevalence

0.5 / 100K

2 drugs in development·1 company·3 clinical trials

Drug Pipeline by Phase

Frequently asked questions

How many drugs are in development for Acid Sphingomyelinase Deficiency?

BioSniper tracks 2 drugs in development for Acid Sphingomyelinase Deficiency across 1 company.

How many clinical trials target Acid Sphingomyelinase Deficiency?

There are 3 clinical trials targeting Acid Sphingomyelinase Deficiency tracked by BioSniper.

What is the prevalence of Acid Sphingomyelinase Deficiency?

The estimated prevalence of Acid Sphingomyelinase Deficiency is approximately 0.5 per 100,000 population.

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    Acid Sphingomyelinase Deficiency — Drugs in Development & Clinical Trials | BioSniper