sepiapterin
Generic: SEPIAPTERIN·Brand: SEPHIENCE, Sephience
sepiapterin: developed by 1 company · 1 clinical trial tracked.
sepiapterin evidence translation
What we can confirm
1 tracked trial
What it means
Source-backed records connect sepiapterin to PTCT; that link alone does not prove the drug works.
What to watch
Watch trial status, endpoints, and the next source-backed update.
BioSniper AIPage evidence connected
Prepared research question
How could sepiapterin → PTCT affect its developer, and what evidence supports the link?
Run cited research
Traceable citations · Unknowns marked
See linked entities and source evidence2 indications · 0 study sponsors
Related indications
PhenylketonuriaPhenylketonuria (PKU)
Study sponsors
No additional listed-company sponsor is linked.
Development Pipeline (2)
| Company | Phase |
|---|---|
| PTC THERAPEUTICS, INC. (PTCT) | Phase 3 |
| PTC THERAPEUTICS, INC. (PTCT) Phenylketonuria (PKU) | Approved |
Clinical Trials (1)
A Phase 3b Open-Label Study of Long-Term Neurocognitive Outcomes in Children With Phenylketonuria Treated With Sepiapterin
Primary endpoint: Mean Change From Baseline in Full-scale Intelligence Quotient (FSIQ) Wechsler Preschool and Primary Scale of Intelligence - Fourth Edition (WPPSI-IV) Score
Interventionalopen56 targetStarted 2024-03Completion 2031-0210 sites · Australia, France, Ireland, Poland…PTC Therapeutics
Frequently asked questions
Who is developing sepiapterin?
sepiapterin is being developed by PTC THERAPEUTICS, INC..
How many clinical trials involve sepiapterin?
BioSniper tracks 1 clinical trial involving sepiapterin.