Neurology
1 drug is in development for Phenylketonuria.
- Companies
- 1
- Clinical trials
- 8
BioSniper AIPage evidence connected
Prepared research question
Which programs lead the Phenylketonuria pipeline—and what evidence could change the picture?
Run cited research
Traceable citations · Unknowns marked
Drug Pipeline by Phase
Phase 3(1)
| Drug | Company |
|---|---|
| Sepiapterin | PTC THERAPEUTICS, INC. (PTCT) |
About this indication
Phenylketonuria context
Neurology·MeSH: Phenylketonurias (D010661)
Also known as: Phenylketonurias
Incidence
1.2 / 100K/yr
Frequently asked questions
How many drugs are in development for Phenylketonuria?
BioSniper tracks 1 drug in development for Phenylketonuria across 1 company.
How many clinical trials target Phenylketonuria?
There are 8 clinical trials targeting Phenylketonuria tracked by BioSniper.