Phenylketonuria
Rare Disease·MeSH: Phenylketonurias
Prevalence
6.0 / 100K
Incidence
1.2 / 100K/yr
12 drugs in development·9 companies·8 clinical trials
Drug Pipeline by Phase
Approved(2)
Phase 3(5)
Phase 2(1)
| Drug | Company |
|---|---|
| mze782 | Maze Therapeutics, Inc. (MAZE) |
Phase 1(1)
| Drug | Company |
|---|---|
| AG-181 | AGIOS PHARMACEUTICALS, INC. (AGIO) |
Early Phase 1(1)
| Drug | Company |
|---|---|
| CBT102-A capsule | Valneva SE (VALN) |
Phase 1/Phase 2(1)
| Drug | Company |
|---|---|
| sar444836 | Sanofi (SNY) |
Phase 4(1)
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Frequently asked questions
How many drugs are in development for Phenylketonuria?
BioSniper tracks 12 drugs in development for Phenylketonuria across 9 companies.
How many clinical trials target Phenylketonuria?
There are 8 clinical trials targeting Phenylketonuria tracked by BioSniper.
What is the prevalence of Phenylketonuria?
The estimated prevalence of Phenylketonuria is approximately 6.0 per 100,000 population.
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