Skip to main content

omaveloxolone

Generic: OMAVELOXOLONE·Brand: SKYCLARYS, Skyclarys

omaveloxolone: developed by 1 company · 5 clinical trials tracked · 1 FDA decision.

omaveloxolone evidence translation

What we can confirm

1 FDA record · 5 tracked trials

What it means

Source-backed records connect omaveloxolone to BIIB; that link alone does not prove the drug works.

What to watch

Watch active trials and any change in FDA or trial status.
BioSniper AIPage evidence connected

Prepared research question

How could omaveloxolone → BIIB affect its developer, and what evidence supports the link?

Run cited research

Traceable citations · Unknowns marked

See linked entities and source evidence4 indications · 0 study sponsors

Related indications

Friedreich's ataxiaHealthy Adult Subjects; Friedreich Ataxia; Healthy VolunteerFriedreich AtaxiaHealthy Volunteer

Study sponsors

No additional listed-company sponsor is linked.

Development Pipeline (2)
CompanyPhase
BIOGEN INC. (BIIB)
Friedreich's ataxia
Approved
BIOGEN INC. (BIIB)
Healthy Adult Subjects; Friedreich Ataxia; Healthy Volunteer
Phase 3
Clinical Trials (5)

A Post-marketing, Observational, Descriptive Study to Assess the Risk Associated With Pregnancy, the Maternal Complications, and Adverse Effects on the Developing Fetus, Neonate, and Infant Among Individuals Exposed to Omaveloxolone During Pregnancy and/or Lactation

Recruiting

Primary endpoint: Number of Major Congenital Malformations (MCMs)

Observational10 targetStarted 2026-10Completion 2035-041 site · United StatesBiogen

A Phase 1, Randomized, Open-Label, Single-Dose, Crossover, Bioequivalence Study of Omaveloxolone Tablets for Oral Suspension Versus Capsules in Healthy Adult Participants

NCT07297199·Phase 1·BIIB
Completed

Primary endpoint: Maximum Observed Plasma Concentration (Cmax) of Omaveloxolone

InterventionalRandomizedopen70 enrolledStarted 2025-12Completion 2026-051 site · United StatesBiogen

A Phase 3 Study to Evaluate the Efficacy, Safety, Pharmacokinetics, and Pharmacodynamics of Omaveloxolone (BIIB141) in Participants With Friedreich's Ataxia Aged 2 to < 16 Years

NCT06953583·Phase 3·BIIB
Recruiting

Primary endpoint: Part 1: Change From Baseline in Upright Stability Score (USS) Subscale E of Modified Friedreich's Ataxia Rating Scale (mFARS) at Week 52

InterventionalRandomizedquadruple255 targetStarted 2025-06Completion 2029-1134 sites · Australia, Austria, Brazil, Canada…Biogen

An Observational, Multinational, Post-Marketing Registry of Omaveloxolone-Treated Patients With Friedreich's Ataxia

Recruiting

Primary endpoint: Omaveloxolone Naive Cohort: Number of Participants With Treatment-Emergent Serious Adverse Events (TESAEs)

Observational300 targetStarted 2024-12Completion 2029-1014 sites · Austria, Belgium, Czechia, Germany…Biogen

A Single Sequence, 2-Period, Open-label Crossover Study in Healthy Subjects to Determine the Effect of a Moderate CYP3A4 Inducer on the Pharmacokinetics of Omaveloxolone

NCT05909644·Phase 1·BIIB
Completed

Primary endpoint: Maximum concentration (Cmax) of omaveloxolone

Interventionalopen20 enrolledStarted 2023-07Completion 2023-081 site · United StatesBiogen
FDA Decisions1 records
Approval1 INDICATIONS AND USAGE SKYCLARYS is indicated for the treatment of Friedreich's ataxia in adults and adolescents aged 16 years and older. SKYCLARYS is indicated for the treatment of Friedreich's ataxia in adults and adolescents aged 16 years and older. ( 1 )(BIIB)FDA ↗
NDA216718Type 1 - New Molecular EntityOrphan DrugPriorityOralCapsule

Frequently asked questions

Who is developing omaveloxolone?

omaveloxolone is being developed by BIOGEN INC..

How many clinical trials involve omaveloxolone?

BioSniper tracks 5 clinical trials involving omaveloxolone.

What is omaveloxolone's latest FDA decision?

The most recent tracked FDA decision for omaveloxolone is Approval for 1 INDICATIONS AND USAGE SKYCLARYS is indicated for the treatment of Friedreich's ataxia in adults and adolescents aged 16 years and older. SKYCLARYS is indicated for the treatment of Friedreich's ataxia in adults and adolescents aged 16 years and older. ( 1 ), dated February 28, 2023.