Neurology
3 drugs are in development for Friedreich Ataxia.
- Companies
- 3
- Clinical trials
- 14
Prepared research question
Which programs lead the Friedreich Ataxia pipeline—and what evidence could change the picture?
Traceable citations · Unknowns marked
Drug Pipeline by Phase
| Drug | Company |
|---|---|
| Vatiquinone | PTC THERAPEUTICS, INC. (PTCT) |
| Drug | Company |
|---|---|
| lx2006 | Lexeo Therapeutics, Inc. (LXEO) |
| Drug | Company |
|---|---|
| nomlabofusp | Larimar Therapeutics, Inc. (LRMR) |
About this indication
Friedreich Ataxia context
Also known as: Ataxia, Friedreich Familial, Ataxia, Friedreich Hereditary, Ataxia, Friedreich Spinocerebellar, Ataxia, Friedreich's, Ataxia, Friedreich's Familial, Ataxia, Friedreich's Hereditary, Ataxias, Friedreich, Ataxias, Friedreich's Hereditary, Disease, Friedreich, Disease, Friedreich's, Friedreich Hereditary Spinal Ataxia, Friedreich's Hereditary Spinal Ataxia, Hereditary Spinal Scleroses, Spinal Sclerosis, Hereditary
Frequently asked questions
How many drugs are in development for Friedreich Ataxia?
BioSniper tracks 3 drugs in development for Friedreich Ataxia across 3 companies.
How many clinical trials target Friedreich Ataxia?
There are 14 clinical trials targeting Friedreich Ataxia tracked by BioSniper.