Skip to main content

asciminib

Generic: ASCIMINIB HYDROCHLORIDE·Brand: SCEMBLIX, Scemblix

asciminib: developed by 1 company · 12 clinical trials tracked · 1 FDA decision.

asciminib evidence translation

What we can confirm

1 FDA record · 12 tracked trials

What it means

Source-backed records connect asciminib to NVS; that link alone does not prove the drug works.

What to watch

Watch active trials and any change in FDA or trial status.
BioSniper AIPage evidence connected

Prepared research question

How could asciminib → NVS affect its developer, and what evidence supports the link?

Run cited research

Traceable citations · Unknowns marked

See linked entities and source evidence2 indications · 0 study sponsors

Study sponsors

No additional listed-company sponsor is linked.

Development Pipeline (1)
CompanyPhase
Novartis AG (NVS)Approved
Clinical Trials (12)showing 10 most recent

Phase 1 Study of Asciminib Maintenance Therapy Following Allogeneic Stem Cell Transplant or Chimeric Antigen Receptor T Cell Therapy (CAR T) to Prevent Relapse in Adults With Philadelphia Chromosome-Positive Acute Lymphoblastic Leukemia

NCT07250087·Phase 1
Recruiting

Primary endpoint: Recommended Phase 2 Dose

Interventionalopen36 targetStarted 2026-01Completion 2029-111 site · United StatesH. Lee Moffitt Cancer Center and Research Institute

Phase II Study of Asciminib for Second-line Treatment of Chronic Phase Chronic Myeloid Leukemia

NCT06629584·Phase 2
Recruiting

Primary endpoint: Major molecular response (MMR) rate by 12 months

Interventionalopen40 targetStarted 2025-02Completion 2028-121 site · United StatesM.D. Anderson Cancer Center

A Prospective, Multicenter, Single-arm, Open-label, Phase IV, Post-authorization Interventional Study to Assess the Safety and Efficacy of Asciminib in Indian Patients With Ph+ CML-CP (Without T315I Mutation), Previously Treated With Two or More Tyrosine Kinase Inhibitors and Ph+ CML-CP With T315I Mutation

NCT06427811·Phase 4·NVS
Completed

Primary endpoint: Frequency and severity of adverse events(AEs)/serious AEs (SAEs) in participants with Ph+ CML-CP without T315I mutation

Interventionalopen85 enrolledStarted 2024-11Completion 2026-0310 sites · IndiaNovartis Pharmaceuticals

Phase I/II Study of the Combination of Blinatumomab and Asciminib in Patients With Philadelphia Chromosome-Positive Acute Lymphoblastic Leukemia

NCT06308588·Phase 1/Phase 2
Recruiting

Primary endpoint: Safety and adverse events (AEs)

Interventionalopen40 targetStarted 2024-08Completion 2029-052 sites · United StatesM.D. Anderson Cancer Center

Phase II Study Assessing Efficacy and Safety of Asciminib in Patients With Newly Diagnosed Chronic Myeloid Leukemia in Chronic Phase.

NCT06236724·Phase 2
Recruiting

Primary endpoint: Safety and adverse events (AEs)

Interventionalopen50 targetStarted 2024-01Completion 2035-071 site · United StatesM.D. Anderson Cancer Center

A Phase 3, Multicenter, Randomized, Open-Label, Trial Evaluating the Efficacy and Safety of Asciminib Used in Consolidation With Imatinib v. Imatinib to Achieve Treatment-free Remission in Chronic Phase-Chronic Myelogenous Leukemia Patients

NCT05413915·Phase 3
Terminated

Primary endpoint: Event-free survival rate

InterventionalRandomizedopen8 targetStarted 2023-11Completion 2025-074 sites · CanadaSarit Assouline

A Phase IIIb, Multi-center, Open-label, Randomized Study of Tolerability and Efficacy of Oral Asciminib Versus Nilotinib in Patients With Newly Diagnosed Philadelphia Chromosome Positive Chronic Myelogenous Leukemia in Chronic Phase.

NCT05456191·Phase 3·NVS
Active, not recruiting

Primary endpoint: Time to Discontinuation of Study Treatment Due to Adverse Event (TTDAE) (From Interim Analysis)

InterventionalRandomizedopen568 enrolledStarted 2022-11Completion 2031-0750 sites · Argentina, Bulgaria, Canada, Czechia…Novartis Pharmaceuticals

Protocol Number: HJKC3-0003. Treatment Free Remission After Asciminib Based Therapy in Chronic Phase Chronic Myeloid Leukemia (CP-CML) Patients Who Relapsed After a Prior Attempt at TKI Discontinuation

NCT04838041·Phase 2
Recruiting

Primary endpoint: One-year "second" treatment-free remission.

Interventionalopen51 targetStarted 2021-11Completion 2029-075 sites · United StatesMedical College of Wisconsin

A Phase III, Multi-center, Open-label, Randomized Study of Oral Asciminib Versus Investigator Selected TKI in Patients With Newly Diagnosed Philadelphia Chromosome Positive Chronic Myelogenous Leukemia in Chronic Phase

NCT04971226·Phase 3·NVS
Active, not recruiting

Primary endpoint: Percentage of Participants With Major Molecular Response (MMR) at Week 48 - Ascimimib vs. Investigator Selected TKI

InterventionalRandomizedopen405 enrolledStarted 2021-10Completion 2031-0150 sites · Australia, Austria, Belgium, Bulgaria…Novartis Pharmaceuticals

Frontline Asciminib Combination in Chronic Phase CML

NCT03906292·Phase 2
Active, not recruiting

Primary endpoint: deep molecular response (Rate of MR4)

Interventionalopen125 enrolledStarted 2019-08Completion 2027-1221 sites · GermanyUniversity of Jena
FDA Decisions1 records
Approval(NVS)FDA ↗
NDA215358Type 1 - New Molecular EntityOrphan DrugPriorityOralTablet

Frequently asked questions

Who is developing asciminib?

asciminib is being developed by Novartis AG.

How many clinical trials involve asciminib?

BioSniper tracks 12 clinical trials involving asciminib.

What is asciminib's latest FDA decision?

The most recent tracked FDA decision for asciminib is Approval, dated October 29, 2021.