| ARWRARROWHEAD PHARMACEUTICALS, INC. | 366,936 | $23.0M |
| IONSIONIS PHARMACEUTICALS INC | 290,024 | $21.8M |
| AXSMAxsome Therapeutics, Inc. | 58,729 | $9.9M |
| ESPREsperion Therapeutics, Inc. | 3,299,441 | $9.0M |
| BIIBBIOGEN INC. | 43,800 | $8.0M |
| QUREuniQure N.V. | 486,520 | $8.0M |
| RAREUltragenyx Pharmaceutical Inc. | 364,802 | $7.6M |
| ARQTArcutis Biotherapeutics, Inc. | 320,972 | $7.6M |
| BMRNBIOMARIN PHARMACEUTICAL INC | 92,305 | $5.2M |
| VRTXVERTEX PHARMACEUTICALS INC / MA | 11,355 | $5.1M |
| DNLIDenali Therapeutics Inc. | 254,857 | $4.9M |
| URGNUroGen Pharma Ltd. | 238,122 | $4.3M |
| ALNYALNYLAM PHARMACEUTICALS, INC. | 12,222 | $4.0M |
| VRDNViridian Therapeutics, Inc.\DE | 173,516 | $3.4M |
| KRYSKrystal Biotech, Inc. | 11,170 | $2.9M |
| ZLABZai Lab Ltd | 132,189 | $2.5M |
| BNTXBioNTech SE | 27,000 | $2.4M |
| CRSPCRISPR Therapeutics AG | 42,874 | $2.0M |
| MGTXMeiraGTx Holdings plc | 212,112 | $1.8M |
| WVEWave Life Sciences Ltd. | 241,010 | $1.7M |
| STOKStoke Therapeutics, Inc. | 50,000 | $1.6M |
| FDMT4D Molecular Therapeutics, Inc. | 170,256 | $1.6M |
| BEAMBeam Therapeutics Inc. | 63,982 | $1.5M |
| MRNAModerna, Inc. | 29,994 | $1.5M |
| PFEPFIZER INC | 52,679 | $1.5M |
| RNACCartesian Therapeutics, Inc. | 179,114 | $1.1M |
| MOHMolina Healthcare Inc | 8,140 | $1.1M |
| SRPTSarepta Therapeutics, Inc. | 46,000 | $1.0M |
| RCKTRocket Pharmaceuticals Inc. | 242,146 | $867K |
| TSHATaysha Gene Therapies, Inc. | 181,900 | $813K |
| AUTLAutolus Therapeutics plc | 363,430 | $502K |
| FATEFATE THERAPEUTICS INC | 414,311 | $497K |
| VYGRVoyager Therapeutics, Inc. | 120,000 | $463K |