Wilson Disease

Rare Disease·MeSH: Disease

Prevalence

0.5 / 100K

6 drugs in development·6 companies·5 clinical trials

Drug Pipeline by Phase

Phase 3(2)

Drug	Company
alxn1840	ALEXION PHARMACEUTICALS, INC. (ALXN)
alxn1840	Monopar Therapeutics (MNPR)

Preclinical(3)

Drug	Company
dtx701	Dimension Therapeutics, Inc. (DMTX)
et-700	Eton Pharmaceuticals, Inc. (ETON)
pm577	Prime Medicine, Inc. (PRME)

Phase 1/Phase 2(1)

Drug	Company
UX701	Ultragenyx Pharmaceutical Inc. (RARE)

BioSniper tracks 6 drugs in development for Wilson Disease across 6 companies.

There are 5 clinical trials targeting Wilson Disease tracked by BioSniper.

The estimated prevalence of Wilson Disease is approximately 0.5 per 100,000 population.

Full trial data, competitive analysis, and AI-powered pipeline tracking.