Neurology
4 drugs are in development for Wilson Disease.
- Companies
- 4
- Clinical trials
- 6
Prepared research question
Which programs lead the Wilson Disease pipeline—and what evidence could change the picture?
Traceable citations · Unknowns marked
Drug Pipeline by Phase
| Drug | Company |
|---|---|
| alxn1840 | Monopar Therapeutics (MNPR) |
| Drug | Company |
|---|---|
| dtx701 | Dimension Therapeutics, Inc. (DMTX) |
| Drug | Company |
|---|---|
| pm577 | Prime Medicine, Inc. (PRME) |
| UX701 | Ultragenyx Pharmaceutical Inc. (RARE) |
About this indication
Wilson Disease context
Also known as: Cerebral Pseudoscleroses, Copper Storage Diseases, Degeneration Syndrome, Hepatolenticular, Degeneration Syndromes, Hepatolenticular, Degeneration, Hepatocerebral, Degeneration, Hepatolenticular, Degeneration, Neurohepatic, Degeneration, Progressive Lenticular, Degenerations, Hepatocerebral, Degenerations, Neurohepatic, Disease, Copper Storage, Diseases, Hepato-Neurologic Wilson, Diseases, Kinnier-Wilson, Hepato Neurologic Wilson Disease, Kinnier Wilson Disease, Pseudosclerosis, Pseudosclerosis, Cerebral, Westphal Strumpell Syndrome, Westphal-Strumpell Syndromes, Wilsons Disease
Frequently asked questions
How many drugs are in development for Wilson Disease?
BioSniper tracks 4 drugs in development for Wilson Disease across 4 companies.
How many clinical trials target Wilson Disease?
There are 6 clinical trials targeting Wilson Disease tracked by BioSniper.