Urea Cycle Disorder

Rare Disease·MeSH: Urea Cycle Disorders, Inborn

6 drugs in development·5 companies·1 clinical trial

Drug Pipeline by Phase

Approved(3)

Drug	Company
olpruva	Acer Therapeutics Inc. (ACER)
olpruva	ZEVRA THERAPEUTICS, INC. (ZVRA)
ravicti	Horizon Therapeutics Public Ltd Co (HZNP)

Phase 2(1)

Drug	Company
kb195	Kaleido Biosciences, Inc. (KLDO)

Phase 1(2)

Drug	Company
cmp-001	Camp4 Therapeutics Corp (CAMP)
CMP-CPS-001	Camp4 Therapeutics Corp (CAMP)

BioSniper tracks 6 drugs in development for Urea Cycle Disorder across 5 companies.

There are 1 clinical trial targeting Urea Cycle Disorder tracked by BioSniper.

Full trial data, competitive analysis, and AI-powered pipeline tracking.