Transthyretin Amyloidosis
Rare Disease·MeSH: Amyloidosis, Hereditary, Transthyretin-Related
6 drugs in development·4 companies·9 clinical trials
Drug Pipeline by Phase
Approved(1)
| Drug | Company |
|---|---|
| Tegsedi | PTC THERAPEUTICS, INC. (PTCT) |
Phase 3(3)
Phase 1(1)
| Drug | Company |
|---|---|
| NTLA-2001 | Intellia Therapeutics, Inc. (NTLA) |
Preclinical(1)
| Drug | Company |
|---|---|
| ag10 | ALEXION PHARMACEUTICALS, INC. (ALXN) |
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Frequently asked questions
How many drugs are in development for Transthyretin Amyloidosis?
BioSniper tracks 6 drugs in development for Transthyretin Amyloidosis across 4 companies.
How many clinical trials target Transthyretin Amyloidosis?
There are 9 clinical trials targeting Transthyretin Amyloidosis tracked by BioSniper.
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