Rare Diseases
Rare Disease·MeSH: Rare Diseases
2 drugs in development·2 companies·8 clinical trials
Drug Pipeline by Phase
Phase 2(1)
| Drug | Company |
|---|---|
| amx0318 | Amylyx Pharmaceuticals, Inc. (AMLX) |
Preclinical(1)
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Frequently asked questions
How many drugs are in development for Rare Diseases?
BioSniper tracks 2 drugs in development for Rare Diseases across 2 companies.
How many clinical trials target Rare Diseases?
There are 8 clinical trials targeting Rare Diseases tracked by BioSniper.
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