Pyruvate Kinase Deficiency
Hematology·MeSH: Pyruvate Kinase Deficiency of Red Cells
3 drugs in development·2 companies·7 clinical trials
Drug Pipeline by Phase
Phase 3(1)
| Drug | Company |
|---|---|
| AG-348 | AGIOS PHARMACEUTICALS, INC. (AGIO) |
Phase 1(1)
| Drug | Company |
|---|---|
| rp-l301 | Rocket Pharmaceuticals Inc. (RCKT) |
Phase 4(1)
| Drug | Company |
|---|---|
| Mitapivat | AGIOS PHARMACEUTICALS, INC. (AGIO) |
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Frequently asked questions
How many drugs are in development for Pyruvate Kinase Deficiency?
BioSniper tracks 3 drugs in development for Pyruvate Kinase Deficiency across 2 companies.
How many clinical trials target Pyruvate Kinase Deficiency?
There are 7 clinical trials targeting Pyruvate Kinase Deficiency tracked by BioSniper.
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