PKU

·MeSH: Phenylketonurias

5 drugs in development·5 companies·2 clinical trials

Drug Pipeline by Phase

Approved(2)

Drug	Company
sapropterin	DR REDDYS LABORATORIES LTD (RDY)
Sephience	PTC THERAPEUTICS, INC. (PTCT)

Phase 3(2)

Drug	Company
labafenogene marselecobac	SYNLOGIC, INC. (SYBX)
pegvaliase	BIOMARIN PHARMACEUTICAL INC (BMRN)

Phase 2(1)

Drug	Company
mze782	Maze Therapeutics, Inc. (MAZE)

BioSniper tracks 5 drugs in development for PKU across 5 companies.

There are 2 clinical trials targeting PKU tracked by BioSniper.

Full trial data, competitive analysis, and AI-powered pipeline tracking.