Pediatric Pyruvate Kinase Deficiency
Hematology·MeSH: Hematologic Diseases
1 drug in development·1 company·2 clinical trials
Drug Pipeline by Phase
Phase 4(1)
| Drug | Company |
|---|---|
| Mitapivat | AGIOS PHARMACEUTICALS, INC. (AGIO) |
Frequently asked questions
How many drugs are in development for Pediatric Pyruvate Kinase Deficiency?
BioSniper tracks 1 drug in development for Pediatric Pyruvate Kinase Deficiency across 1 company.
How many clinical trials target Pediatric Pyruvate Kinase Deficiency?
There are 2 clinical trials targeting Pediatric Pyruvate Kinase Deficiency tracked by BioSniper.
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