OTC Deficiency
Neurology·MeSH: Ornithine Carbamoyltransferase Deficiency Disease
4 drugs in development·2 companies·1 clinical trial
Drug Pipeline by Phase
Phase 3(3)
Preclinical(1)
| Drug | Company |
|---|---|
| dtx301 | Dimension Therapeutics, Inc. (DMTX) |
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Frequently asked questions
How many drugs are in development for OTC Deficiency?
BioSniper tracks 4 drugs in development for OTC Deficiency across 2 companies.
How many clinical trials target OTC Deficiency?
There are 1 clinical trial targeting OTC Deficiency tracked by BioSniper.
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