Niemann-Pick Disease Type A
Rare Disease
Prevalence
5.0 / 100K
1 drug in development·1 company·1 clinical trial
Drug Pipeline by Phase
Phase 3(1)
| Drug | Company |
|---|---|
| plx-300 | Polaryx Therapeutics Inc. (PLYX) |
Frequently asked questions
How many drugs are in development for Niemann-Pick Disease Type A?
BioSniper tracks 1 drug in development for Niemann-Pick Disease Type A across 1 company.
How many clinical trials target Niemann-Pick Disease Type A?
There are 1 clinical trial targeting Niemann-Pick Disease Type A tracked by BioSniper.
What is the prevalence of Niemann-Pick Disease Type A?
The estimated prevalence of Niemann-Pick Disease Type A is approximately 5.0 per 100,000 population.
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