Mucopolysaccharidosis IV A

Rare Disease·MeSH: Mucopolysaccharidosis IV

Prevalence

5.0 / 100K

0 drugs in development·0 companies·3 clinical trials

Frequently asked questions

How many clinical trials target Mucopolysaccharidosis IV A?

There are 3 clinical trials targeting Mucopolysaccharidosis IV A tracked by BioSniper.

What is the prevalence of Mucopolysaccharidosis IV A?

The estimated prevalence of Mucopolysaccharidosis IV A is approximately 5.0 per 100,000 population.

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    Mucopolysaccharidosis IV A — Drugs in Development & Clinical Trials | BioSniper