Long-chain Fatty Acid Oxidation Disorders (LC-FAOD)
·MeSH: Carnitine-Acylcarnitine Translocase Deficiency
2 drugs in development·1 company·2 clinical trials
Drug Pipeline by Phase
Approved(1)
| Drug | Company |
|---|---|
| Dojolvi | Ultragenyx Pharmaceutical Inc. (RARE) |
Phase 3(1)
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Frequently asked questions
How many drugs are in development for Long-chain Fatty Acid Oxidation Disorders (LC-FAOD)?
BioSniper tracks 2 drugs in development for Long-chain Fatty Acid Oxidation Disorders (LC-FAOD) across 1 company.
How many clinical trials target Long-chain Fatty Acid Oxidation Disorders (LC-FAOD)?
There are 2 clinical trials targeting Long-chain Fatty Acid Oxidation Disorders (LC-FAOD) tracked by BioSniper.
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