Hermansky-Pudlak Syndrome 4
Oncology·MeSH: N-acetyl glutamate synthetase deficiency
Prevalence
30.0 / 100K
0 drugs in development·0 companies·1 clinical trial
Frequently asked questions
How many clinical trials target Hermansky-Pudlak Syndrome 4?
There are 1 clinical trial targeting Hermansky-Pudlak Syndrome 4 tracked by BioSniper.
What is the prevalence of Hermansky-Pudlak Syndrome 4?
The estimated prevalence of Hermansky-Pudlak Syndrome 4 is approximately 30.0 per 100,000 population.
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