Hereditary Transthyretin-mediated Amyloidosis With Polyneropathy
Rare Disease·MeSH: Amyloidosis, Hereditary, Transthyretin-Related
1 drug in development·1 company·1 clinical trial
Drug Pipeline by Phase
Unknown(1)
| Drug | Company |
|---|---|
| inotersen | AKCEA THERAPEUTICS, INC. (AKCA) |
Frequently asked questions
How many drugs are in development for Hereditary Transthyretin-mediated Amyloidosis With Polyneropathy?
BioSniper tracks 1 drug in development for Hereditary Transthyretin-mediated Amyloidosis With Polyneropathy across 1 company.
How many clinical trials target Hereditary Transthyretin-mediated Amyloidosis With Polyneropathy?
There are 1 clinical trial targeting Hereditary Transthyretin-mediated Amyloidosis With Polyneropathy tracked by BioSniper.
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