Neurology
1 drug is in development for GM1 Gangliosidosis.
- Companies
- 1
- Clinical trials
- 5
BioSniper AIPage evidence connected
Prepared research question
Which programs lead the GM1 Gangliosidosis pipeline—and what evidence could change the picture?
Run cited research
Traceable citations · Unknowns marked
Drug Pipeline by Phase
Phase 1/Phase 2(1)
| Drug | Company |
|---|---|
| axo-aav-gm1 | Sio Gene Therapies Inc. (SIOX) |
About this indication
GM1 Gangliosidosis context
Neurology·MeSH: Gangliosidosis, GM1 (D016537)
Also known as: Beta Galactosidase 1 Deficiency Disease, Beta Galactosidosis, G(M1) Gangliosidosis, Gangliosidosis G(M1), Gangliosidosis GM1
Frequently asked questions
How many drugs are in development for GM1 Gangliosidosis?
BioSniper tracks 1 drug in development for GM1 Gangliosidosis across 1 company.
How many clinical trials target GM1 Gangliosidosis?
There are 5 clinical trials targeting GM1 Gangliosidosis tracked by BioSniper.