GM1 Gangliosidosis
Neurology·MeSH: Gangliosidosis, GM1
Prevalence
0.5 / 100K
2 drugs in development·2 companies·5 clinical trials
Drug Pipeline by Phase
Phase 1/Phase 2(2)
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Frequently asked questions
How many drugs are in development for GM1 Gangliosidosis?
BioSniper tracks 2 drugs in development for GM1 Gangliosidosis across 2 companies.
How many clinical trials target GM1 Gangliosidosis?
There are 5 clinical trials targeting GM1 Gangliosidosis tracked by BioSniper.
What is the prevalence of GM1 Gangliosidosis?
The estimated prevalence of GM1 Gangliosidosis is approximately 0.5 per 100,000 population.
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