Gangliosidosis
Prevalence
0.5 / 100K
4 drugs in development·3 companies·1 clinical trial
Drug Pipeline by Phase
Phase 3(1)
| Drug | Company |
|---|---|
| plx-300 | Polaryx Therapeutics Inc. (PLYX) |
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Frequently asked questions
How many drugs are in development for Gangliosidosis?
BioSniper tracks 4 drugs in development for Gangliosidosis across 3 companies.
How many clinical trials target Gangliosidosis?
There are 1 clinical trial targeting Gangliosidosis tracked by BioSniper.
What is the prevalence of Gangliosidosis?
The estimated prevalence of Gangliosidosis is approximately 0.5 per 100,000 population.
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