Friedreich's Ataxia
Rare Disease·MeSH: Friedreich Ataxia
7 drugs in development·5 companies·1 clinical trial
Drug Pipeline by Phase
Approved(1)
| Drug | Company |
|---|---|
| SKYCLARYS | BIOGEN INC. (BIIB) |
Phase 2(1)
| Drug | Company |
|---|---|
| jotrol | JUPITER NEUROSCIENCES, INC. (JUNS) |
Preclinical(4)
Phase 1/Phase 2(1)
| Drug | Company |
|---|---|
| SGT-212 | Solid Biosciences Inc. (SLDB) |
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Frequently asked questions
How many drugs are in development for Friedreich's Ataxia?
BioSniper tracks 7 drugs in development for Friedreich's Ataxia across 5 companies.
How many clinical trials target Friedreich's Ataxia?
There are 1 clinical trial targeting Friedreich's Ataxia tracked by BioSniper.
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