Neurology
9 drugs are in development for Duchenne Muscular Dystrophy.
- Companies
- 7
- Clinical trials
- 44
Prepared research question
Which programs lead the Duchenne Muscular Dystrophy pipeline—and what evidence could change the picture?
Traceable citations · Unknowns marked
Drug Pipeline by Phase
| Drug | Company |
|---|---|
| Deramiocel | CAPRICOR THERAPEUTICS, INC. (CAPR) |
| KER-065 | Keros Therapeutics, Inc. (KROS) |
| pgn-edo51 | PepGen Inc. (PEPG) |
| WVE-N531 | Wave Life Sciences Ltd. (WVE) |
| Drug | Company |
|---|---|
| SGT-003 | Solid Biosciences Inc. (SLDB) |
| Drug | Company |
|---|---|
| elevidys | Sarepta Therapeutics, Inc. (SRPT) |
About this indication
Duchenne Muscular Dystrophy context
Also known as: Cardiomyopathy, Dilated, 3B, Cardiomyopathy, Dilated, X-Linked, Childhood Muscular Dystrophy, Pseudohypertrophic, Childhood Pseudohypertrophic Muscular Dystrophy, Duchenne Type Progressive Muscular Dystrophy, Muscular Dystrophy, Childhood, Pseudohypertrophic, Muscular Dystrophy, Duchenne Type, Muscular Dystrophy, Pseudohypertrophic Progressive, Duchenne Type, Muscular Dystrophy, Pseudohypertrophic, Childhood, Pseudohypertrophic Muscular Dystrophy
Incidence
1.5 / 100K/yr
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Frequently asked questions
How many drugs are in development for Duchenne Muscular Dystrophy?
BioSniper tracks 9 drugs in development for Duchenne Muscular Dystrophy across 7 companies.
How many clinical trials target Duchenne Muscular Dystrophy?
There are 44 clinical trials targeting Duchenne Muscular Dystrophy tracked by BioSniper.