Confirmed Biallelic RPE65 Mutation-associated Retinal Dystrophy

Oncology·MeSH: Leber Congenital Amaurosis
1 drug in development·1 company·1 clinical trial

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How many drugs are in development for Confirmed Biallelic RPE65 Mutation-associated Retinal Dystrophy?

BioSniper tracks 1 drug in development for Confirmed Biallelic RPE65 Mutation-associated Retinal Dystrophy across 1 company.

How many clinical trials target Confirmed Biallelic RPE65 Mutation-associated Retinal Dystrophy?

There are 1 clinical trial targeting Confirmed Biallelic RPE65 Mutation-associated Retinal Dystrophy tracked by BioSniper.

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    Confirmed Biallelic RPE65 Mutation-associated Retinal Dystrophy — Drugs in Development & Clinical Trials | BioSniper