Neurology
2 drugs are in development for Angelman Syndrome.
- Companies
- 2
- Clinical trials
- 10
BioSniper AIPage evidence connected
Prepared research question
Which programs lead the Angelman Syndrome pipeline—and what evidence could change the picture?
Run cited research
Traceable citations · Unknowns marked
Drug Pipeline by Phase
Phase 3(2)
| Drug | Company |
|---|---|
| GTX-102 | Ultragenyx Pharmaceutical Inc. (RARE) |
| obudanersen | IONIS PHARMACEUTICALS INC (IONS) |
About this indication
Angelman Syndrome context
Neurology·MeSH: Angelman Syndrome (D017204)
Also known as: Children, Puppet, Syndrome, Happy Puppet
Frequently asked questions
How many drugs are in development for Angelman Syndrome?
BioSniper tracks 2 drugs in development for Angelman Syndrome across 2 companies.
How many clinical trials target Angelman Syndrome?
There are 10 clinical trials targeting Angelman Syndrome tracked by BioSniper.