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selumetinib

Generic: SELUMETINIB SULFATE·Brand: KOSELUGO, Koselugo

selumetinib: developed by 2 companies · 11 clinical trials tracked · 2 FDA decisions.

selumetinib evidence translation

What we can confirm

2 FDA records · 11 tracked trials

What it means

More than one developer is source-backed. Until you choose one, AI stays drug-only and does not guess ownership.

What to watch

Watch active trials and any change in FDA or trial status.
BioSniper AIPage evidence connected

Prepared research question

What is verified about selumetinib, and what remains unknown?

Run cited research

Traceable citations · Unknowns marked

See linked entities and source evidence7 indications · 0 study sponsors

Study sponsors

No additional listed-company sponsor is linked.

Development Pipeline (2)
CompanyPhase
ARRAY BIOPHARMA INC (ARRY)
cancer and NF1
Phase 3
ASTRAZENECA PLC (AZN)Approved
Clinical Trials (11)showing 10 most recent

A Single-Center, Single-Arm, Phase II Study to Explore the Efficacy and Safety of MEK1/2 Inhibitor (MEKi) Selumetinib in the Treatment of Patients With NF2-Related Schwannomatosis

NCT07707947·Phase 2
Not yet recruiting

Primary endpoint: Objective Response Rate (ORR)in NF2-related vestibular schwannoma assessed according to the REiNS criteria

Interventionalopen20 targetStarted 2026-07Completion 2028-121 site · ChinaBeijing Tiantan Hospital

A Phase 1/1b/2 Study of Cabozantinib in Combination With Selumetinib for Plexiform Neurofibroma in Adults and Adolescents With Neurofibromatosis Type 1

NCT06502171·Phase 1
Recruiting

Primary endpoint: The number of participants that experienced a dose limiting toxicity when taking cabozantinib and selumetinib together.

Interventionalopen30 targetStarted 2026-06Completion 2034-086 sites · United StatesGirish Dhall, MD

Early Phase Study to Evaluate the MEK Inhibitor Selumetinib With the MDM2 Inhibitor APG-115 in Patients With Neurofibromatosis Type 1 and Pre-malignant and Malignant Peripheral Nerve Sheath Tumors

NCT06735820·Phase 1/Phase 2
Recruiting

Primary endpoint: The number of treated patients with adverse events as determined by the common criteria for adverse version 5 (CTCAEv5).

Interventionalopen45 targetStarted 2026-06Completion 2028-102 sites · United StatesAeRang Kim

A Phase III, Multicentre, International Study With a Parallel, Randomised, Double-blind, Placebo-controlled, 2 Arm Design to Assess the Efficacy and Safety of Selumetinib in Adult Participants With NF1 Who Have Symptomatic, Inoperable Plexiform Neurofibromas (KOMET)

NCT04924608·Phase 3·AZN
Active, not recruiting

Primary endpoint: Confirmed Partial and Complete Response Rate (ORR) by End of Cycle 16 Using Volumetric MRI Analysis as Determined by ICR (Per REiNS Criteria) in Participants With NF1 Who Have Symptomatic, Inoperable PN.

InterventionalRandomizedquadruple145 targetStarted 2021-11Completion 2029-0234 sites · Australia, Brazil, Canada, China…AstraZeneca

A Phase I, Single-Arm, Sequential Study to Evaluate the Effect of Food on the Gastrointestinal Tolerability and Pharmacokinetics of Selumetinib After Multiple Doses in Adolescent Children With Neurofibromatosis Type 1 Related Plexiform Neurofibromas

NCT05101148·Phase 1·AZN
Active, not recruiting

Primary endpoint: Selumetinib area under the plasma concentration-time curve from zero to 12 hours post-dose (AUC0-12)

Interventionalopen24 enrolledStarted 2021-07Completion 2028-049 sites · Poland, Russia, Spain, United StatesAstraZeneca

A Phase 1 Open Label Study to Assess the Safety, Tolerability, Pharmacokinetics and Clinical Efficacy of Selumetinib, a Selective Mitogen Activated Protein Kinase Kinase (MEK) 1 Inhibitor, in Chinese Paediatric and Adult Subjects With Neurofibromatosis Type 1 (NF1) and Inoperable Plexiform Neurofibromas (PN)

NCT04590235·Phase 1·AZN
Active, not recruiting

Primary endpoint: Adverse events

Interventionalopen32 enrolledStarted 2020-12Completion 2026-082 sites · ChinaAstraZeneca

SARC031: A Phase 2 Trial of the MEK Inhibitor Selumetinib (AZD6244 Hydrogen Sulfate) in Combination With the mTOR Inhibitor Sirolimus for Patients With Unresectable or Metastatic Malignant Peripheral Nerve Sheath Tumors

NCT03433183·Phase 2
Completed

Primary endpoint: Clinical Benefit Rate of Selumetinib in Combination With Sirolimus in Patients With Unresectable or Metastatic NF1 Associated or Sporadic MPNST.

Interventionalopen21 enrolledStarted 2019-10Completion 2023-105 sites · United StatesSarcoma Alliance for Research through Collaboration

A Phase II, Open-Label, Study of Olaparib in Combination With Either Durvalumab (MEDI4736), Selumetinib or Capivasertib, or Ceralasertib Monotherapy in Patients With Metastatic Triple-Negative Breast Cancer

NCT03801369·Phase 2
Terminated

Primary endpoint: Objective Response Rate (ORR)

Interventionalopen24 targetStarted 2018-12Completion 2024-121 site · United StatesGordon Mills, MD, PhD

Evaluation of the Combination of Selumetinib and Olaparib in Endometrial, Ovarian and Other Solid Tumors With Ras Pathway Alterations, and Ovarian Tumors With PARP Resistance

NCT03162627·Phase 1
Active, not recruiting

Primary endpoint: Maximum Tolerated Dose (MTD) for Combination of Selumetinib and Olaparib in Participants with Advanced or Recurrent Solid Tumors

Interventionalopen90 targetStarted 2017-08Completion 2026-081 site · United StatesM.D. Anderson Cancer Center

National Lung Matrix Trial: Multi-drug, Genetic Marker-directed, Non-comparative, Multi-centre, Multi-arm Phase II Trial in Non-small Cell Lung Cancer

NCT02664935·Phase 2
Completed

Primary endpoint: Objective response (OR)

Interventionalopen423 enrolledStarted 2015-05Completion 2023-1125 sites · United KingdomUniversity of Birmingham
FDA Decisions2 records
Approval1 INDICATIONS AND USAGE KOSELUGO is indicated for the treatment of adult and pediatric patients 1 year of age and older with neurofibromatosis type 1 (NF1) who have symptomatic, inoperable plexiform neurofibromas (PN) [see Dosage and Administration (2) ]. KOSELUGO is a kinase inhibitor indicated for the treatment of adult and pediatric patients 1 year of age and older with neurofibromatosis type 1 (NF1) who have symptomatic, inoperable plexiform neurofibromas (PN). ( 1 )(AZN)FDA ↗
NDA219943Type 3 - New Dosage FormOrphan DrugPriorityOralGranule
Approval1 INDICATIONS AND USAGE KOSELUGO is indicated for the treatment of adult and pediatric patients 1 year of age and older with neurofibromatosis type 1 (NF1) who have symptomatic, inoperable plexiform neurofibromas (PN) [see Dosage and Administration (2) ]. KOSELUGO is a kinase inhibitor indicated for the treatment of adult and pediatric patients 1 year of age and older with neurofibromatosis type 1 (NF1) who have symptomatic, inoperable plexiform neurofibromas (PN). ( 1 )(AZN)FDA ↗
NDA213756Type 1 - New Molecular EntityOrphan DrugPriorityOralCapsule

Frequently asked questions

Who is developing selumetinib?

selumetinib is being developed by ARRAY BIOPHARMA INC, ASTRAZENECA PLC.

How many clinical trials involve selumetinib?

BioSniper tracks 11 clinical trials involving selumetinib.

What is selumetinib's latest FDA decision?

The most recent tracked FDA decision for selumetinib is Approval for 1 INDICATIONS AND USAGE KOSELUGO is indicated for the treatment of adult and pediatric patients 1 year of age and older with neurofibromatosis type 1 (NF1) who have symptomatic, inoperable plexiform neurofibromas (PN) [see Dosage and Administration (2) ]. KOSELUGO is a kinase inhibitor indicated for the treatment of adult and pediatric patients 1 year of age and older with neurofibromatosis type 1 (NF1) who have symptomatic, inoperable plexiform neurofibromas (PN). ( 1 ), dated September 10, 2025.