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pitolisant

Generic: pitolisant·Brand: WAKIX, Wakix

pitolisant: developed by 2 companies · 5 clinical trials tracked.

pitolisant evidence translation

What we can confirm

5 tracked trials

What it means

More than one developer is source-backed. Until you choose one, AI stays drug-only and does not guess ownership.

What to watch

Watch trial status, endpoints, and the next source-backed update.
BioSniper AIPage evidence connected

Prepared research question

What is verified about pitolisant, and what remains unknown?

Run cited research

Traceable citations · Unknowns marked

See linked entities and source evidence6 indications · 0 study sponsors

Related indications

Excessive daytime sleepiness (EDS) and cataplexy in patients with narcolepsy; adults and pediatric patients six years and olderIdiopathic Hypersomnia; Prader-Willi Syndrome; Pregnancy RelatedExcessive daytime sleepiness or cataplexy in adult patients with narcolepsy; excessive daytime sleepiness associated with obstructive sleep apnea syndromeIdiopathic HypersomniaNarcolepsyPrader-Willi Syndrome

Study sponsors

No additional listed-company sponsor is linked.

Development Pipeline (4)
CompanyPhase
Harmony Biosciences Holdings, Inc. (HRMY)
Excessive daytime sleepiness (EDS) and cataplexy in patients…
Approved
Harmony Biosciences Holdings, Inc. (HRMY)
Idiopathic Hypersomnia; Prader-Willi Syndrome; Pregnancy Rel…
Phase 3
Harmony Biosciences Holdings, Inc. (HRMY)
Idiopathic Hypersomnia; Prader-Willi Syndrome; Pregnancy Rel…
Phase 3
Viatris Inc (VTRS)
Excessive daytime sleepiness or cataplexy in adult patients …
Approved
Clinical Trials (5)

An Open-Label Study to Evaluate Safety of Pitolisant in Participants With Prader-Willi Syndrome

NCT07219485·Phase 3·HRMY
Enrolling by invitation

Primary endpoint: Percentage of participants reporting Treatment-Emergent Adverse Events (TEAEs)

Interventionalopen150 targetStarted 2025-08Completion 2030-081 site · United StatesHarmony Biosciences Management, Inc.

A Phase 3, Randomized, Double-Blind, Placebo-controlled, Efficacy and Safety Study of Pitolisant Followed by an Open-Label Extension in Patients With Prader-Willi Syndrome

NCT06366464·Phase 3·HRMY
Recruiting

Primary endpoint: Change in severity of EDS as measured by Patient-Reported Outcomes Measurement Information System Bank v1.0 - Sleep-Related Impairment (PROMIS-SRI) T-score

InterventionalRandomizedquadruple134 targetStarted 2024-05Completion 2028-0450 sites · Australia, Belgium, Canada, Denmark…Harmony Biosciences Management, Inc.

An Open-Label Study to Evaluate the Long-Term Safety and Effectiveness of Pitolisant in Adult Patients With Idiopathic Hypersomnia Who Completed Study HBS-101-CL-010

NCT05458128·Phase 3·HRMY
Completed

Primary endpoint: Safety and tolerability of pitolisant

Interventionalopen119 enrolledStarted 2022-08Completion 2025-1032 sites · United StatesHarmony Biosciences Management, Inc.

WAKIX® (Pitolisant) Pregnancy Registry: An Observational Study of the Safety of Pitolisant Exposure in Pregnant Women and Their Offspring

Recruiting

Primary endpoint: Major congenital malformation

Observational1,329 targetStarted 2021-08Completion 2030-061 site · United StatesHarmony Biosciences Management, Inc.

A Randomized, Double-Blind, Placebo-Controlled Phase 2 Study to Evaluate the Safety and Efficacy of Pitolisant in Patients With Prader-Willi Syndrome, Followed by an Open Label Extension

NCT04257929·Phase 2·HRMY
Completed

Primary endpoint: Excessive Daytime Sleepiness

InterventionalRandomizedtriple65 enrolledStarted 2020-12Completion 2026-0113 sites · United StatesHarmony Biosciences Management, Inc.

Frequently asked questions

Who is developing pitolisant?

pitolisant is being developed by Harmony Biosciences Holdings, Inc., Viatris Inc.

How many clinical trials involve pitolisant?

BioSniper tracks 5 clinical trials involving pitolisant.