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lumasiran

Generic: LUMASIRAN SODIUM·Brand: OXLUMO, Oxlumo

lumasiran: 1 clinical trial tracked.

lumasiran evidence translation

What we can confirm

1 tracked trial

No verified listed company relationship

What it means

AI will separate confirmed drug evidence from unknown company context.

What to watch

Watch trial status, endpoints, and the next source-backed update.
BioSniper AIPage evidence connected

Prepared research question

What is verified about lumasiran, and what remains unknown?

Run cited research

Traceable citations · Unknowns marked

See linked entities and source evidence0 indications · 1 study sponsors

Related indications

No linked indication is available.

Clinical Trial Registry Records (1)

ILLUMINATE-C: A Single Arm Study to Evaluate Efficacy, Safety, Pharmacokinetics, and Pharmacodynamics of Lumasiran in Patients With Advanced Primary Hyperoxaluria Type 1 (PH1)

NCT04152200Registry updated 2025-07-18·Phase 3·ALNY
Completed

Primary endpoint: Cohort A: Percent Change in Plasma Oxalate From Baseline to Month 6

Interventionalopen21 enrolledStarted 2020-01Completion 2025-0614 sites · Australia, Belgium, France, Israel…Alnylam Pharmaceuticals