eladocagene exuparvovec

Generic: eladocagene exuparvovec·Brand: Kebilidi

eladocagene exuparvovec: sourced relationships with 1 company · 1 clinical trial tracked.

What we can confirm

1 tracked trial

PTC THERAPEUTICS, INC. (PTCT)

What it means

Source-backed records connect eladocagene exuparvovec to PTCT; that link alone does not prove the drug works.

What to watch

Watch trial status, endpoints, and the next source-backed update.

BioSniper AIPage evidence connected

Prepared research question

How could eladocagene exuparvovec → PTCT affect its developer, and what evidence supports the link?

Run cited research

Traceable citations · Unknowns marked

See linked entities and source evidence1 indications · 0 study sponsors

Related indications

Aromatic L-Amino Decarboxylase (AADC) deficiency

Study sponsors

No additional listed-company sponsor is linked.

Dated Pipeline Records (1)

Company	Dated record stage	Indication
PTC THERAPEUTICS, INC. (PTCT) licensee · Reported 2024-02-29 · Current development: unknownSource Aromatic L-Amino Decarboxylase (AADC) deficiency	Approved	Aromatic L-Amino Decarboxylase (AADC) deficiency

Clinical Trial Registry Records (1)

An Open-Label Trial to Address the Safety of the SmartFlow MR-Compatible Ventricular Cannula for Administering Eladocagene Exuparvovec to Pediatric Subjects

NCT04903288Registry updated 2026-04-24·Phase 2·PTCT

Active, not recruiting

Primary endpoint: Change From Baseline in HVA Metabolite Level at the End of the Trial Phase

Interventionalopen13 targetStarted 2021-05Completion 2028-046 sites · Israel, Taiwan, United StatesPTC Therapeutics

Frequently asked questions

Which companies have sourced relationships with eladocagene exuparvovec?

eladocagene exuparvovec has dated SEC/FDA relationship records for PTC THERAPEUTICS, INC..

How many clinical trials involve eladocagene exuparvovec?

BioSniper tracks 1 clinical trial involving eladocagene exuparvovec.