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autologous base edited cd34+ hspcs beam-101

Generic: Autologous Base Edited CD34+ HSPCs BEAM-101

autologous base edited cd34+ hspcs beam-101: 1 clinical trial tracked.

autologous base edited cd34+ hspcs beam-101 evidence translation

What we can confirm

1 tracked trial

No verified listed company relationship

What it means

AI will separate confirmed drug evidence from unknown company context.

What to watch

Watch trial status, endpoints, and the next source-backed update.
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Prepared research question

What is verified about autologous base edited cd34+ hspcs beam-101, and what remains unknown?

Run cited research

Traceable citations · Unknowns marked

See linked entities and source evidence1 indications · 1 study sponsors
Clinical Trial Registry Records (1)

A Phase 1/2 Study Evaluating the Safety and Efficacy of a Single Dose of Autologous CD34+ Base Edited Hematopoietic Stem Cells (BEAM-101) in Patients With Sickle Cell Disease and Severe Vaso-Occlusive Crises (Beacon Trial)

NCT05456880Registry updated 2025-12-16·Phase 1/Phase 2·BEAM
Active, not recruiting

Primary endpoint: Change in annualized number of severe VOCs (Vascular-occlusive Crisis) relative to baseline

Interventionalopen15 targetStarted 2022-08Completion 2028-0219 sites · United StatesBeam Therapeutics Inc.